Works matching AU Pacanowski, Michael A.

Results: 40
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    Precision Medicine 2030.

    Published in:
    Clinical Pharmacology & Therapeutics, 2020, v. 107, n. 1, p. 62, doi. 10.1002/cpt.1675
    By:
    • Pacanowski, Michael;
    • Liu, Qi
    Publication type:
    Article
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    Identification of Stevens-Johnson syndrome and toxic epidermal necrolysis in electronic health record databases.

    Published in:
    Pharmacoepidemiology & Drug Safety, 2015, v. 24, n. 7, p. 684, doi. 10.1002/pds.3778
    By:
    • Davis, Robert L.;
    • Gallagher, Mia A.;
    • Asgari, Maryam M.;
    • Eide, Melody J.;
    • Margolis, David J.;
    • Macy, Eric;
    • Burmester, James K.;
    • Selvam, Nandini;
    • Boscarino, Joseph A.;
    • Cromwell, Lee F.;
    • Feigelson, Heather S.;
    • Kuntz, Jennifer L.;
    • Pawloski, Pamala A.;
    • Penfold, Robert B.;
    • Raebel, Marsha A.;
    • Sridhar, Gayathri;
    • Wu, Ann;
    • La Grenade, Lois A.;
    • Pacanowski, Michael A.;
    • Pinheiro, Simone P.
    Publication type:
    Article
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    Regulatory news: Olipudase alfa‐rpcp (Xenpozyme™) for treatment of non‐central nervous system manifestations of acid sphingomyelinase deficiency (ASMD) in adult and pediatric patients—FDA Approval summary.

    Published in:
    Journal of Inherited Metabolic Disease, 2024, v. 47, n. 4, p. 575, doi. 10.1002/jimd.12754
    By:
    • Hon, Yuen Yi;
    • Zaidi, Anita;
    • Giffin, Andrew;
    • Wang, Yan;
    • Lei, Nie;
    • Hossain, Md Nayeem;
    • Wang, Jie;
    • Li, Hongshan;
    • Liu, Guansheng;
    • Liu, Jiang;
    • Yang, Yuching;
    • Zhu, Hao;
    • Pacanowski, Michael;
    • McLeod‐Flynn, Laurie;
    • Summan, Mukesh;
    • Liu, Yongmin;
    • Sheikh, Faruk;
    • Dickensheets, Harold;
    • Kim, Jennifer;
    • McWilliams, Ian
    Publication type:
    Article
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    Regulatory news: Cipaglucosidase alfa‐atga (Pombiliti) coadministered with Miglustat (Opfolda) for adults with late‐onset Pompe disease.

    Published in:
    Journal of Inherited Metabolic Disease, 2024, v. 47, n. 4, p. 578, doi. 10.1002/jimd.12744
    By:
    • Luquetti, Daniela V.;
    • Jeng, Linda J. B.;
    • Donohue, Kathleen M.;
    • Maynard, Janet W.;
    • Morris, Emily;
    • Wang, Yan;
    • Nie, Lei;
    • Adeniyi, Oluseyi;
    • Ready, Travis;
    • Li, RuoJing;
    • Wang, Jie;
    • Liu, Jiang;
    • Pacanowski, Michael;
    • McNerney, Mary Ellen;
    • Akinshola, B. Emmanuel;
    • McLeod‐Flynn, Laurie;
    • Weis, Shawna;
    • Summan, Mukesh;
    • Namuswe, Frances;
    • Shafiei, Hamid
    Publication type:
    Article
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    Regulatory news: Nulibry (fosdenopterin) approved to reduce the risk of mortality in patients with molybdenum cofactor deficiency type A: FDA approval summary.

    Published in:
    Journal of Inherited Metabolic Disease, 2021, v. 44, n. 5, p. 1085, doi. 10.1002/jimd.12421
    By:
    • Farrell, Sheila;
    • Karp, Jacqueline;
    • Hager, Rebecca;
    • Wang, Yan;
    • Adeniyi, Oluseyi;
    • Wang, Jie;
    • Li, Liang;
    • Ma, Lian;
    • Peretz, Jackye;
    • Summan, Mukesh;
    • Kong, Nicolas;
    • White, Michael;
    • Pacanowski, Michael;
    • Price, Dionne;
    • Filie, Jane;
    • Donohue, Kathleen;
    • Joffe, Hylton
    Publication type:
    Article
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    Considerations for Developing Targeted Therapies in Low‐Frequency Molecular Subsets of a Disease.

    Published in:
    Clinical Pharmacology & Therapeutics, 2018, v. 104, n. 2, p. 282, doi. 10.1002/cpt.1041
    By:
    • Schuck, Robert N.;
    • Woodcock, Janet;
    • Zineh, Issam;
    • Stein, Peter;
    • Jarow, Jonathan;
    • Temple, Robert;
    • Permutt, Thomas;
    • LaVange, Lisa;
    • Beaver, Julia A.;
    • Charlab, Rosane;
    • Blumenthal, Gideon M.;
    • Dorff, Sarah E.;
    • Leptak, Christopher;
    • Lemery, Steven;
    • Rogers, Hobart;
    • Chowdhury, Badrul;
    • Litwack, E. David;
    • Pacanowski, Michael
    Publication type:
    Article
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    Research Directions in Genetic Predispositions to Stevens–Johnson Syndrome / Toxic Epidermal Necrolysis.

    Published in:
    Clinical Pharmacology & Therapeutics, 2018, v. 103, n. 3, p. 390, doi. 10.1002/cpt.890
    By:
    • Manolio, Teri A.;
    • Hutter, Carolyn M.;
    • Avigan, Mark;
    • Cibotti, Ricardo;
    • Davis, Robert L.;
    • Denny, Joshua C.;
    • Grenade, Lois La;
    • Wheatley, Lisa M.;
    • Carrington, Mary N.;
    • Chantratita, Wasun;
    • Chung, Wen‐hung;
    • Dalton, Andrea D.;
    • Hung, Shuen‐iu;
    • Lee, Ming Ta Michael;
    • Leeder, J. Steven;
    • Lertora, Juan J. L.;
    • Mahasirimongkol, Surakameth;
    • Mcleod, Howard L.;
    • Mockenhaupt, Maja;
    • Pacanowski, Michael
    Publication type:
    Article
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