Found: 12
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Modulation of CD8<sup>+</sup> T cell responses to AAV vectors with IgG-derived MHC class II epitopes.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1, doi. 10.1038/mt.2013.166
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- Publication type:
- Article
Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy.
- Published in:
- Human Molecular Genetics, 2015, v. 24, n. 7, p. 2078, doi. 10.1093/hmg/ddu727
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- Publication type:
- Article
Treatment of Diabetes and Long-Term Survival After Insulin and Glucokinase Gene Therapy.
- Published in:
- Diabetes, 2013, v. 62, n. 5, p. 1718, doi. 10.2337/db12-1113
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- Publication type:
- Article
Endocrine Pancreas Regeneration in Diabetic IGF-I Transgenic Mice Results from Replication of Pre-Existing β-Cells Rather than from Bone Marrow Cell Recruitment and Differentiation.
- Published in:
- Diabetes, 2007, v. 56, p. A424
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- Publication type:
- Article
Increased Intraocular IGF-I Induces Blood-Retinal Barrier Breakdown in a Transgenic Animal Model of Diabetic Retinopathy.
- Published in:
- Diabetes, 2007, v. 56, p. A26
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- Publication type:
- Article
In vivo genome editing restores haemostasis in a mouse model of haemophilia.
- Published in:
- Nature, 2011, v. 475, n. 7355, p. 217, doi. 10.1038/nature10177
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- Publication type:
- Article
Liver Production of Sulfamidase Reverses Peripheral and Ameliorates CNS Pathology in Mucopolysaccharidosis IIIA Mice.
- Published in:
- Molecular Therapy, 2012, v. 20, n. 2, p. 254, doi. 10.1038/mt.2011.220
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- Publication type:
- Article
Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 7, p. 1318, doi. 10.1038/mt.2010.73
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- Publication type:
- Article
236. Bone Marrow-Derived Cells Do Not Contribute to Endocrine Pancreas Regeneration in Diabetic RIP/IGF-I Transgenic Mice
- Published in:
- 2005
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- Publication type:
- Abstract
Long-Term Retinal PEDF Overexpression Prevents Neovascularization in a Murine Adult Model of Retinopathy.
- Published in:
- PLoS ONE, 2012, v. 7, n. 7, p. 1, doi. 10.1371/journal.pone.0041511
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- Publication type:
- Article
Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy.
- Published in:
- 2013
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- Publication type:
- journal article
Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.
- Published in:
- Human Molecular Genetics, 2017, v. 26, n. 8, p. 1535, doi. 10.1093/hmg/ddx058
- By:
- Publication type:
- Article