Works matching AU Haurigot, Virginia


Results: 12
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    Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs.

    Published in:
    Molecular Therapy, 2010, v. 18, n. 7, p. 1318, doi. 10.1038/mt.2010.73
    By:
    • Haurigot, Virginia;
    • Mingozzi, Federico;
    • Buchlis, George;
    • Hui, Daniel J.;
    • Chen, Yifeng;
    • Basner-Tschakarjan, Etiena;
    • Arruda, Valder R.;
    • Radu, Antoneta;
    • Franck, Helen G.;
    • Wright, J Fraser;
    • Zhou, Shangzhen;
    • Stedman, Hansell H;
    • Bellinger, Dwight A.;
    • Nichols, Timothy C;
    • High, Katherine A.
    Publication type:
    Article
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    Treatment of Diabetes and Long-Term Survival After Insulin and Glucokinase Gene Therapy.

    Published in:
    Diabetes, 2013, v. 62, n. 5, p. 1718, doi. 10.2337/db12-1113
    By:
    • Callejas, David;
    • Mann, Christopher J.;
    • Ayuso, Eduard;
    • Lage, Ricardo;
    • Grifoll, Iris;
    • Roca, Carles;
    • Andaluz, Anna;
    • Gopegui, Rafael Ruiz-de;
    • Montané, Joel;
    • Muñoz, Sergio;
    • Ferre, Tura;
    • Haurigot, Virginia;
    • Shangzhen Zhou;
    • Ruberte, Jesús;
    • Mingozzi, Federico;
    • High, Katherine A.;
    • Garcia, Felix;
    • Bosch, Fatima
    Publication type:
    Article
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    In vivo genome editing restores haemostasis in a mouse model of haemophilia.

    Published in:
    Nature, 2011, v. 475, n. 7355, p. 217, doi. 10.1038/nature10177
    By:
    • Hojun Li;
    • Haurigot, Virginia;
    • Doyon, Yannick;
    • Tianjian Li;
    • Wong, Sunnie Y.;
    • Bhagwat, Anand S.;
    • Malani, Nirav;
    • Anguela, Xavier M.;
    • Sharma, Rajiv;
    • Ivanciu, Lacramiora;
    • Murphy, Samuel L.;
    • Finn, Jonathan D.;
    • Khazi, Fayaz R.;
    • Shangzhen Zhou;
    • Paschon, David E.;
    • Rebar, Edward J.;
    • Bushman, Frederic D.;
    • Gregory, Philip D.;
    • Holmes, Michael C.;
    • High, Katherine A.
    Publication type:
    Article
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    Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy.

    Published in:
    Human Molecular Genetics, 2015, v. 24, n. 7, p. 2078, doi. 10.1093/hmg/ddu727
    By:
    • Ribera, Albert;
    • Haurigot, Virginia;
    • Garcia, Miguel;
    • Marcó, Sara;
    • Motas, Sandra;
    • Villacampa, Pilar;
    • Maggioni, Luca;
    • León, Xavier;
    • Molas, Maria;
    • Sánchez, Víctor;
    • Muñoz, Sergio;
    • Leborgne, Christian;
    • Moll, Xavier;
    • Pumarola, Martí;
    • Mingozzi, Federico;
    • Ruberte, Jesús;
    • Añor, Sònia;
    • Bosch, Fatima
    Publication type:
    Article