Works matching IS 2328-9503 AND VI 11 AND IP 1 AND DT 2024


Results: 21
    1

    Propensity matched comparison of omaveloxolone treatment to Friedreich ataxia natural history data.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 4, doi. 10.1002/acn3.51897
    By:
    • Lynch, David R.;
    • Goldsberry, Angie;
    • Rummey, Christian;
    • Farmer, Jennifer;
    • Boesch, Sylvia;
    • Delatycki, Martin B.;
    • Giunti, Paola;
    • Hoyle, J. Chad;
    • Mariotti, Caterina;
    • Mathews, Katherine D.;
    • Nachbauer, Wolfgang;
    • Perlman, Susan;
    • Subramony, S.H.;
    • Wilmot, George;
    • Zesiewicz, Theresa;
    • Weissfeld, Lisa;
    • Meyer, Colin
    Publication type:
    Article
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    Subcutaneous batoclimab in generalized myasthenia gravis: Results from a Phase 2a trial with an open‐label extension.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 194, doi. 10.1002/acn3.51946
    By:
    • Nowak, Richard J.;
    • Breiner, Ari;
    • Bril, Vera;
    • Allen, Jeffrey A.;
    • Khan, Shaida;
    • Levine, Todd;
    • Jacobs, Daniel H.;
    • Sahagian, Gregory;
    • Siddiqi, Zaeem A.;
    • Xu, Jing;
    • Macias, William L.;
    • Benatar, Michael;
    • Adams, Laurence;
    • Genge, Angela;
    • Habib, Ali;
    • Hinton, John L.;
    • Holmlund, Tomas H.;
    • Lange, Dale J.;
    • Nicolle, Michael W.;
    • Phan, Han C.
    Publication type:
    Article
    7

    Short‐chain fatty acid producers in the gut are associated with pediatric multiple sclerosis onset.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 169, doi. 10.1002/acn3.51944
    By:
    • Schoeps, Vinicius A.;
    • Zhou, Xiaoyuan;
    • Horton, Mary K.;
    • Zhu, Feng;
    • McCauley, Kathryn E.;
    • Nasr, Zahra;
    • Virupakshaiah, Akash;
    • Gorman, Mark P.;
    • Benson, Leslie A.;
    • Weinstock‐Guttman, Bianca;
    • Waldman, Amy;
    • Banwell, Brenda L.;
    • Bar‐Or, Amit;
    • Marrie, Ruth Ann;
    • van Domselaar, Gary;
    • O'Mahony, Julia;
    • Mirza, Ali I.;
    • Bernstein, Charles N.;
    • Yeh, E. Ann;
    • Casper, T. Charles
    Publication type:
    Article
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    12

    The role of the amygdala in ictal central apnea: insights from brain MRI morphometry.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 121, doi. 10.1002/acn3.51938
    By:
    • Micalizzi, Elisa;
    • Ballerini, Alice;
    • Giovannini, Giada;
    • Cioclu, Maria Cristina;
    • Scolastico, Simona;
    • Pugnaghi, Matteo;
    • Orlandi, Niccolò;
    • Malagoli, Marcella;
    • Genovese, Maurilio;
    • Todeschini, Alessandra;
    • Giunta, Leandra;
    • Villani, Flavio;
    • Meletti, Stefano;
    • Vaudano, Anna Elisabetta
    Publication type:
    Article
    13
    14

    Clinical variability associated with intronic FGF14 GAA repeat expansion in Japan.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 96, doi. 10.1002/acn3.51936
    By:
    • Ando, Masahiro;
    • Higuchi, Yujiro;
    • Yuan, Junhui;
    • Yoshimura, Akiko;
    • Kojima, Fumikazu;
    • Yamanishi, Yuki;
    • Aso, Yasuhiro;
    • Izumi, Kotaro;
    • Imada, Minako;
    • Maki, Yoshimitsu;
    • Nakagawa, Hiroto;
    • Hobara, Takahiro;
    • Noguchi, Yutaka;
    • Takei, Jun;
    • Hiramatsu, Yu;
    • Nozuma, Satoshi;
    • Sakiyama, Yusuke;
    • Hashiguchi, Akihiro;
    • Matsuura, Eiji;
    • Okamoto, Yuji
    Publication type:
    Article
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    Clinical importance of changes in magnetic resonance biomarkers for Duchenne muscular dystrophy.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 67, doi. 10.1002/acn3.51933
    By:
    • Willcocks, Rebecca J.;
    • Barnard, Alison M.;
    • Daniels, Michael J.;
    • Forbes, Sean C.;
    • Triplett, William T.;
    • Brandsema, John F.;
    • Finanger, Erika L.;
    • Rooney, William D.;
    • Kim, Sarah;
    • Wang, Dah‐Jyuu;
    • Lott, Donovan J.;
    • Senesac, Claudia R.;
    • Walter, Glenn A.;
    • Sweeney, H. Lee;
    • Vandenborne, Krista
    Publication type:
    Article
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    Issue Information.

    Published in:
    Annals of Clinical & Translational Neurology, 2024, v. 11, n. 1, p. 1, doi. 10.1002/acn3.51803
    Publication type:
    Article