Works matching IS 22143599 AND DT 2025 AND VI 12

Results: 29
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    Long-term safety of cyclical rozanolixizumab in patients with generalized myasthenia gravis: Results from the Phase 3 MycarinG study and an open-label extension.

    Published in:
    Journal of Neuromuscular Diseases, 2025, v. 12, n. 2, p. 231, doi. 10.1177/22143602241308181
    By:
    • Habib, Ali A;
    • Drużdż, Artur;
    • Grosskreutz, Julian;
    • Mantegazza, Renato;
    • Sacconi, Sabrina;
    • Utsugisawa, Kimiaki;
    • Vu, Tuan;
    • Vissing, John;
    • Gayfieva, Maryam;
    • Pulido-Valdeolivas, Irene;
    • Tarancón, Thaïs;
    • Woltering, Franz;
    • Bril, Vera
    Publication type:
    Article
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    A rare case of myopathy with fatigability due to PYROXD1 variation.

    Published in:
    Journal of Neuromuscular Diseases, 2025, v. 12, n. 2, p. 293, doi. 10.1177/22143602241301635
    By:
    • Baskar, Dipti;
    • Thomas, Aneesha;
    • Boddu, Vijay Kumar;
    • Santhoshkumar, Rashmi;
    • Anjanappa, Ram Murthy;
    • Nashi, Saraswati;
    • Srivastava, Kosha;
    • Polavarapu, Kiran;
    • Arunachal, Gautham;
    • Kotambail, Ananthapadmanabha;
    • Rao, Bhoomika;
    • Mahadevan, Anita;
    • Nalini, Atchayaram;
    • Vengalil, Seena
    Publication type:
    Article
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    Taking ACTION to detect myocarditis related to recombinant gene transfer therapy for Duchenne Muscular Dystrophy; Consensus recommendations for cardiac surveillance.

    Published in:
    Journal of Neuromuscular Diseases, 2025, v. 12, n. 2, p. 173, doi. 10.1177/22143602241303357
    By:
    • Kaufman, Beth D.;
    • Veerapandiyan, Aravindhan;
    • Soslow, Jonathan H;
    • Wittlieb-Weber, Carol;
    • Esteso, Paul;
    • Olson, Aaron K.;
    • Shih, Renata;
    • Bansal, Neha;
    • Lal, Ashwin;
    • Gambetta, Katheryn;
    • Hsu, Daphne;
    • Cripe, Linda;
    • Villa, Chet;
    • Nandi, Deipanjan
    Publication type:
    Article
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    A Parent Project Muscular Dystrophy-sponsored International Workshop Report on Endocrine and Bone Issues in Patients with Duchenne Muscular Dystrophy: An Ever-changing Landscape.

    Published in:
    Journal of Neuromuscular Diseases, 2025, v. 12, n. 1, p. 116, doi. 10.1177/22143602241303370
    By:
    • Ward, Leanne M;
    • Weber, David R;
    • Wong, Sze Choong;
    • Apkon, Susan;
    • Clemens, Paula R;
    • Cripe, Linda H;
    • McMillan, Hugh J;
    • Mercuri, Eugenio;
    • Nasomyont, Nat;
    • Phung, Kim;
    • Renthal, Nora E;
    • Rutter, Meilan M;
    • Tian, Cuixia;
    • Wood, Claire L;
    • Zeitler, Philip S;
    • Buccella, Filippo;
    • Kinnett, Kathi;
    • Furlong, Pat
    Publication type:
    Article
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    Characterization of swallowing biomechanics and function in untreated infants with spinal muscular atrophy: A natural history dataset.

    Published in:
    Journal of Neuromuscular Diseases, 2025, v. 12, n. 1, p. 70, doi. 10.1177/22143602241308762
    By:
    • McGrattan, Katlyn Elizabeth;
    • Graham, Robert J;
    • Mohr, Alicia Hofelich;
    • Miles, Anna;
    • Allen, Jacqui;
    • Ochura, Juliet;
    • Hernandez, Kayla;
    • Walsh, Katie;
    • Rao, Vamshi;
    • Stevens, Melanie;
    • Alfano, Lindsay;
    • Coker, Mackenzi;
    • Leon-Astudillo, Carmen;
    • Smith, Leann Schow;
    • Brandsema, John;
    • Farah, Hiba;
    • Welc, Julia;
    • Levy, Deborah Salle;
    • Clements, Miranda;
    • Tang, Whitney J
    Publication type:
    Article
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