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Works matching IS 19466234 AND DT 2025 AND VI 17 AND IP 798

Results: 6

1

Intra-amniotic antisense oligonucleotide treatment improves phenotypes in preclinical models of spinal muscular atrophy.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adv4656

By:

Borges, Beltran;
Brown, Stephen M.;
Chen, Wan-Jin;
Clarke, Maria T.;
Herzeg, Akos;
Park, Jae Hong;
Ross, Joshua;
Kong, Lingling;
Denton, Madeline;
Smith, Amy K.;
Lum, Tony;
Zada, Fareha Moulana;
Cordero, Marco;
Gupta, Nalin;
Cook, Sarah E.;
Murray, Heather;
Matson, John;
Klein, Stephanie;
Bennett, C. Frank;
Krainer, Adrian R.

Publication type:

Article

2

Rapid closure and hemostasis of ruptured soft tissues using a modified human tropoelastin-based sealant in preclinical models.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adr6458

By:

Ghovvati, Mahsa;
Jain, Saumya;
Cheng, George Z.;
Kaneko, Naoki;
Boys, Joshua A.;
Imahori, Taichiro;
De Maeseneer, Tess;
Haghniaz, Reihaneh;
Cameron, Robert B.;
Weiss, Anthony S.;
Annabi, Nasim

Publication type:

Article

3

An AAV variant selected through NHP screens robustly transduces the brain and drives secreted protein expression in NHPs and mice.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adr2531

By:

Tecedor, Luis;
Chen, Yong Hong;
Leib, David E.;
Ranum, Paul T.;
Keiser, Megan S.;
Lewandowski, Brian C.;
Carrell, Elli M.;
Lysenko, Elena;
Huerta-Ocampo, Icnelia;
Arora, Sakshi;
Cheng, Congsheng;
Liu, Xueyuan;
Davidson, Beverly L.

Publication type:

Article

4

Expanded T cell clones with lymphoma driver somatic mutations accumulate in refractory celiac disease.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adp6812

By:

Singh, Mandeep;
Louie, Raymond H. Y.;
Samir, Jerome;
Field, Matthew A.;
Milthorpe, Claire;
Adikari, Thiruni;
Mackie, Joseph;
Roper, Ellise;
Faulks, Megan;
Jackson, Katherine J. L.;
Calcino, Andrew;
Hardy, Melinda Y.;
Blombery, Piers;
Amos, Timothy G.;
Deveson, Ira W.;
Wende, Helen Vander;
Floor, Stephen N.;
Read, Scott A.;
Shek, Dmitri;
Guerin, Antoine

Publication type:

Article

5

MEK1/2 inhibitors suppress pathological α-synuclein and neurotoxicity in cell models and a humanized mouse model of Parkinson's disease.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adp4625

By:

Wang, Huilan;
Wang, Qing;
Xu, Haoxiang;
Wu, Yuanzheng;
Cheung, Siulam;
Xu, Qianhui;
Pan, Chengfang;
Cao, Jingyu;
Cao, Zhiyuan;
Yang, Ruonan;
Ding, Yu;
Fei, Yiyan;
Chen, Yongfeng;
Wang, Jian;
Liu, Cong;
Lu, Boxun

Publication type:

Article

6

An oral norovirus vaccine generates mucosal immunity and reduces viral shedding in a phase 2 placebo-controlled challenge study.

Published in:

Science Translational Medicine, 2025, v. 17, n. 798, p. 1, doi. 10.1126/scitranslmed.adh9906

By:

Flitter, Becca A.;
Gillard, Joshua;
Greco, Susan N.;
Apkarian, Maria D.;
D'Amato, Nick P.;
Nguyen, Lam Quynh;
Neuhaus, Elena D.;
Hailey, Darreann Carmela M.;
Pasetti, Marcela F.;
Shriver, Mallory;
Quigley, Christina;
Frenck Jr., Robert W.;
Lindesmith, Lisa C.;
Baric, Ralph S.;
Wei, Lee-Jen;
Tucker, Sean N.;
Cummings, James F.

Publication type:

Article