Works matching IS 19466234 AND DT 2025 AND VI 17 AND IP 787

Results: 6
    1

    BCKDHA-BCKDHB digenic gene therapy restores metabolic homeostasis in two mouse models and a calf with classic maple syrup urine disease.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 787, p. 1, doi. 10.1126/scitranslmed.ads0539
    By:
    • Wang, Jiaming;
    • Poskitt, Laura E.;
    • Gallagher, Jillian;
    • Puffenberger, Erik G.;
    • Wynn, R. Max;
    • Shishodia, Gauri;
    • Chuang, David T.;
    • Beever, Jonathan;
    • Hardin, Donald L.;
    • Brigatti, Karlla W.;
    • Baker, William C.;
    • Gately, Rachael;
    • Bertrand, Stephanie;
    • Rodrigues, Ashlin;
    • Benatti, Hector R;
    • Taghian, Toloo;
    • Hall, Erin;
    • Prestigiacomo, Rachel;
    • Liang, Jialing;
    • Chen, Gong
    Publication type:
    Article
    2
    3

    An electroadhesive hydrogel interface prolongs porcine gastrointestinal mucosal theranostics.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 787, p. 1, doi. 10.1126/scitranslmed.adq1975
    By:
    • Ying, Binbin;
    • Nan, Kewang;
    • Zhu, Qing;
    • Khuu, Tom;
    • Ro, Hana;
    • Qin, Sophia;
    • Wang, Shubing;
    • Jiang, Karen;
    • Chen, Yonglin;
    • Bao, Guangyu;
    • Jenkins, Josh;
    • Pettinari, Andrew;
    • Kuosmanen, Johannes;
    • Ishida, Keiko;
    • Fabian, Niora;
    • Lopes, Aaron;
    • Codreanu, Flavia;
    • Morimoto, Joshua;
    • Li, Jason;
    • Hayward, Alison
    Publication type:
    Article
    4

    Single-cell analysis of aplastic anemia reveals a convergence of NK and NK-like CD8<sup>+</sup> T cells with a disease-associated TCR signature.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 787, p. 1, doi. 10.1126/scitranslmed.adl6758
    By:
    • Lundgren, Sofie;
    • Huuhtanen, Jani;
    • Keränen, Mikko;
    • Feng, Xingmin;
    • Patel, Bhavisha A.;
    • Ryland, Georgina L.;
    • Fox, Lucy C.;
    • Bravo-Perez, Carlos;
    • Clemente, Michael;
    • Kerr, Cassandra;
    • Walldin, Gunilla;
    • Dufva, Olli;
    • Zaimoku, Yoshitaka;
    • Tuononen, Tiina;
    • Myllymäki, Mikko;
    • Ebeling, Freja;
    • Jokinen, Emmi;
    • Heinonen, Markus;
    • Kasanen, Tiina;
    • Klievink, Jay
    Publication type:
    Article
    5

    Reduced cerebellar rhythm by climbing fiber denervation is linked to motor rhythm deficits in mice and ataxia severity in patients.

    Published in:
    Science Translational Medicine, 2025, v. 17, n. 787, p. 1, doi. 10.1126/scitranslmed.adk3922
    By:
    • Lin, Chih-Chun;
    • Fang, Ke-Chu;
    • Balbo, Ilaria;
    • Liang, Ting-Yu;
    • Liu, Chia-Wei;
    • Liu, Wen-Chuan;
    • Wang, Yi-Mei;
    • Hung, Yen-Ling;
    • Yang, Kai-Chien;
    • Geng, Scott Kun;
    • Ni, Chun-Lun;
    • Driscoll, Christopher P.;
    • Ruff, David S.;
    • Kumar, Ami;
    • Amokrane, Nadia;
    • Desai, Natasha;
    • Faust, Phyllis L.;
    • Louis, Elan D.;
    • Kuo, Sheng-Han;
    • Pan, Ming-Kai
    Publication type:
    Article
    6