Works matching IS 19466234 AND DT 2024 AND VI 16 AND IP 769


Results: 5
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    High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease.

    Published in:
    Science Translational Medicine, 2024, v. 16, n. 769, p. 1, doi. 10.1126/scitranslmed.adj6779
    By:
    • Bzhilyanskaya, Vera;
    • Ma, Linyuan;
    • Liu, Siyuan;
    • Fox, Lauren R.;
    • Whittaker, Madelynn N.;
    • Meis, Ronald J.;
    • Choi, Uimook;
    • Lawson, Amanda;
    • Ma, Michelle;
    • Theobald, Narda;
    • Burkett, Sandra;
    • Sweeney, Colin L.;
    • Lazzarotto, Cicera R.;
    • Tsai, Shengdar Q.;
    • Lack, Justin B.;
    • Wu, Xiaolin;
    • Dahl, Gary A.;
    • Malech, Harry L.;
    • Kleinstiver, Benjamin P.;
    • De Ravin, Suk See
    Publication type:
    Article
    4

    Melatonin receptor 1A variants as genetic cause of idiopathic osteoporosis.

    Published in:
    Science Translational Medicine, 2024, v. 16, n. 769, p. 1, doi. 10.1126/scitranslmed.adj0085
    By:
    • Bisikirska, Brygida;
    • Labella, Rossella;
    • Cuesta-Dominguez, Alvaro;
    • Luo, Na;
    • De Angelis, Jessica;
    • Mosialou, Ioanna;
    • Lin, Chyuan-Sheng;
    • Beck, David;
    • Lata, Sneh;
    • Shyu, Peter Timothy;
    • McMahon, Donald J.;
    • Guo, Edward;
    • Hagen, Jacob;
    • Chung, Wendy K.;
    • Shane, Elizabeth;
    • Cohen, Adi;
    • Kousteni, Stavroula
    Publication type:
    Article
    5

    Follistatin drives neuropathic pain in mice through IGF1R signaling in nociceptive neurons.

    Published in:
    Science Translational Medicine, 2024, v. 16, n. 769, p. 1, doi. 10.1126/scitranslmed.adi1564
    By:
    • Jiang, Bao-Chun;
    • Ling, Yue-Juan;
    • Xu, Meng-Lin;
    • Gu, Jun;
    • Wu, Xiao-Bo;
    • Sha, Wei-Lin;
    • Tian, Tian;
    • Bai, Xue-Hui;
    • Li, Nan;
    • Jiang, Chang-Yu;
    • Chen, Ouyang;
    • Ma, Ling-Jie;
    • Zhang, Zhi-Jun;
    • Qin, Yi-Bin;
    • Zhu, Meixuan;
    • Yuan, Hong-Jie;
    • Wu, Long-Jun;
    • Ji, Ru-Rong;
    • Gao, Yong-Jing
    Publication type:
    Article