Works matching IS 19466234 AND DT 2023 AND VI 15 AND IP 698

Results: 5

    • PSMC3 proteasome subunit variants are associated with neurodevelopmental delay and type I interferon production.

      Published in:
      Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.abo3189
      By:
      • Ebstein, Frédéric;
      • Küry, Sébastien;
      • Most, Victoria;
      • Rosenfelt, Cory;
      • Scott-Boyer, Marie-Pier;
      • van Woerden, Geeske M.;
      • Besnard, Thomas;
      • Papendorf, Jonas Johannes;
      • Studencka-Turski, Maja;
      • Wang, Tianyun;
      • Hsieh, Tzung-Chien;
      • Golnik, Richard;
      • Baldridge, Dustin;
      • Forster, Cara;
      • de Konink, Charlotte;
      • Teurlings, Selina M.W.;
      • Vignard, Virginie;
      • van Jaarsveld, Richard H.;
      • Ades, Lesley;
      • Cogné, Benjamin
      Publication type:
      Article

    • Gene-edited and -engineered stem cell platform drives immunotherapy for brain metastatic melanomas.

      Published in:
      Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.ade8732
      By:
      • Kanaya, Nobuhiko;
      • Kitamura, Yohei;
      • Lopez Vazquez, Maria;
      • Franco, Arnaldo;
      • Chen, Kok-Siong;
      • van Schaik, Thijs A.;
      • Farzani, Touraj Aligholipour;
      • Borges, Paulo;
      • Ichinose, Toru;
      • Seddiq, Waleed;
      • Kuroda, Shinji;
      • Boland, Genevieve;
      • Jahan, Nusrat;
      • Fisher, David;
      • Wakimoto, Hiroaki;
      • Shah, Khalid
      Publication type:
      Article

    • Constitutive IL-1RA production by modified immune cells protects against IL-1–mediated inflammatory disorders.

      Published in:
      Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.ade3856
      By:
      • Colantuoni, Mariasilvia;
      • Jofra Hernandez, Raisa;
      • Pettinato, Emanuela;
      • Basso-Ricci, Luca;
      • Magnani, Laura;
      • Andolfi, Grazia;
      • Rigamonti, Chiara;
      • Finardi, Annamaria;
      • Romeo, Valentina;
      • Soldi, Monica;
      • Sergi Sergi, Lucia;
      • Rocchi, Martina;
      • Scala, Serena;
      • Hoffman, Hal M.;
      • Gregori, Silvia;
      • Kajaste-Rudnitski, Anna;
      • Sanvito, Francesca;
      • Muzio, Luca;
      • Naldini, Luigi;
      • Aiuti, Alessandro
      Publication type:
      Article

    • Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia.

      Published in:
      Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.abq3679
      By:
      • Aprile, Annamaria;
      • Raggi, Laura;
      • Bolamperti, Simona;
      • Villa, Isabella;
      • Storto, Mariangela;
      • Morello, Gaia;
      • Marktel, Sarah;
      • Tripodo, Claudio;
      • Cappellini, Maria Domenica;
      • Motta, Irene;
      • Rubinacci, Alessandro;
      • Ferrari, Giuliana
      Publication type:
      Article

    • Indian Hedgehog release from TNF-activated renal epithelia drives local and remote organ fibrosis.

      Published in:
      Science Translational Medicine, 2023, v. 15, n. 698, p. 1, doi. 10.1126/scitranslmed.abn0736
      By:
      • O'Sullivan, Eoin D.;
      • Mylonas, Katie J.;
      • Xin, Cuiyan;
      • Baird, David P.;
      • Carvalho, Cyril;
      • Docherty, Marie-Helena;
      • Campbell, Ross;
      • Matchett, Kylie P.;
      • Waddell, Scott H.;
      • Walker, Alexander D.;
      • Gallagher, Kevin M.;
      • Jia, Siyang;
      • Leung, Steve;
      • Laird, Alexander;
      • Wilflingseder, Julia;
      • Willi, Michaela;
      • Reck, Maximilian;
      • Finnie, Sarah;
      • Pisco, Angela;
      • Gordon-Keylock, Sabrina
      Publication type:
      Article