Works matching IS 19466234 AND DT 2020 AND VI 12 AND IP 566


Results: 7
    1

    Toward allele-specific targeting therapy and pharmacodynamic marker for spinocerebellar ataxia type 3.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 566, p. 1, doi. 10.1126/scitranslmed.abb7086
    By:
    • Prudencio, Mercedes;
    • Garcia-Moreno, Hector;
    • Jansen-West, Karen R.;
    • AL-Shaikh, Rana Hanna;
    • Gendron, Tania F.;
    • Heckman, Michael G.;
    • Spiegel, Matthew R.;
    • Carlomagno, Yari;
    • Daughrity, Lillian M.;
    • Song, Yuping;
    • Dunmore, Judith A.;
    • Byron, Natalie;
    • Oskarsson, Björn;
    • Nicholson, Katharine A.;
    • Staff, Nathan P.;
    • Gorcenco, Sorina;
    • Puschmann, Andreas;
    • Lemos, João;
    • Januário, Cristina;
    • LeDoux, Mark S.
    Publication type:
    Article
    2
    3

    Calmodulin inhibitors improve erythropoiesis in Diamond-Blackfan anemia.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 566, p. 1, doi. 10.1126/scitranslmed.abb5831
    By:
    • Taylor, Alison M.;
    • Macari, Elizabeth R.;
    • Chan, Iris T.;
    • Blair, Megan C.;
    • Doulatov, Sergei;
    • Vo, Linda T.;
    • Raiser, David M.;
    • Siva, Kavitha;
    • Basak, Anindita;
    • Pirouz, Mehdi;
    • Shah, Arish N.;
    • McGrath, Katherine;
    • Humphries, Jessica M.;
    • Stillman, Emma;
    • Alter, Blanche P.;
    • Calo, Eliezer;
    • Gregory, Richard I.;
    • Sankaran, Vijay G.;
    • Flygare, Johan;
    • Ebert, Benjamin L.
    Publication type:
    Article
    4

    Aryl hydrocarbon receptor ligand production by the gut microbiota is decreased in celiac disease leading to intestinal inflammation.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 566, p. 1, doi. 10.1126/scitranslmed.aba0624
    By:
    • Lamas, Bruno;
    • Hernandez-Galan, Leticia;
    • Galipeau, Heather J.;
    • Constante, Marco;
    • Clarizio, Alexandra;
    • Jury, Jennifer;
    • Breyner, Natalia M.;
    • Caminero, Alberto;
    • Rueda, Gaston;
    • Hayes, Christina L.;
    • McCarville, Justin L.;
    • Bermudez Brito, Miriam;
    • Planchais, Julien;
    • Rolhion, Nathalie;
    • Murray, Joseph A.;
    • Langella, Philippe;
    • Loonen, Linda M. P.;
    • Wells, Jerry M.;
    • Bercik, Premysl;
    • Sokol, Harry
    Publication type:
    Article
    5

    Down-regulation of Beclin1 promotes direct cardiac reprogramming.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 566, p. 1, doi. 10.1126/scitranslmed.aay7856
    By:
    • Wang, Li;
    • Ma, Hong;
    • Huang, Peisen;
    • Xie, Yifang;
    • Near, David;
    • Wang, Haofei;
    • Xu, Jun;
    • Yang, Yuchen;
    • Xu, Yangxi;
    • Garbutt, Tiffany;
    • Zhou, Yang;
    • Liu, Ziqing;
    • Yin, Chaoying;
    • Bressan, Michael;
    • Taylor, Joan M.;
    • Liu, Jiandong;
    • Qian, Li
    Publication type:
    Article
    6
    7