Works matching IS 19466234 AND DT 2019 AND VI 11 AND IP 485


Results: 10
    1

    In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis.

    Published in:
    Science Translational Medicine, 2019, v. 11, n. 485, p. N.PAG, doi. 10.1126/scitranslmed.aau7531
    By:
    • Sun, Xingshen;
    • Yi, Yaling;
    • Yan, Ziying;
    • Liang, Bo;
    • Winter, Michael C.;
    • Evans, T. Idil Apak;
    • Rotti, Pavana G.;
    • Yang, Yu;
    • Gray, Jaimie S.;
    • Park, Soo Yeun;
    • Zhou, Weihong;
    • Zhang, Yulong;
    • Moll, Shashanna R.;
    • Rosen, Bradley H.;
    • Engelhardt, John F.;
    • Woody, Lisa;
    • Tran, Dao M.;
    • Jiang, Licong;
    • Negulescu, Paul;
    • Van Goor, Fred
    Publication type:
    Article
    2
    4

    A pannexin 1 channelopathy causes human oocyte death.

    Published in:
    Science Translational Medicine, 2019, v. 11, n. 485, p. N.PAG, doi. 10.1126/scitranslmed.aav8731
    By:
    • Sang, Qing;
    • Zhang, Zhihua;
    • Chen, Biaobang;
    • Mu, Jian;
    • Li, Qiaoli;
    • Jin, Li;
    • Wang, Lei;
    • Shi, Juanzi;
    • Sun, Xiaoxi;
    • Li, Bin;
    • Yan, Zheng;
    • Ai, Ai;
    • Lyu, Qifeng;
    • Wu, Ling;
    • Mao, Xiaoyan;
    • Kuang, Yanping;
    • Xue, Songguo;
    • Li, Wei;
    • Zhang, Jilin;
    • Sun, Qiang
    Publication type:
    Article
    5
    6
    7
    8

    GPRC5D is a target for the immunotherapy of multiple myeloma with rationally designed CAR T cells.

    Published in:
    Science Translational Medicine, 2019, v. 11, n. 485, p. N.PAG, doi. 10.1126/scitranslmed.aau7746
    By:
    • Staehr, Mette;
    • Masakayan, Reed;
    • Purdon, Terence J.;
    • Smith, Eric L.;
    • De Larrea, Carlos Fernandez;
    • Brentjens, Renier J.;
    • Harrington, Kim;
    • Jones, Jon;
    • Long, Thomas J.;
    • Ghoddusi, Majid;
    • Do, Trevor;
    • Pham, Minh Thu;
    • Brown, Jessica M.;
    • Olson, Eric;
    • Sather, Blythe;
    • Ng, Khong Y.;
    • Peguero, Elizabeth;
    • Wendel, Hans-Guido;
    • Wang, Xiuyan;
    • Riviere, Isabelle
    Publication type:
    Article
    9
    10

    A farnesyltransferase inhibitor activates lysosomes and reduces tau pathology in mice with tauopathy.

    Published in:
    Science Translational Medicine, 2019, v. 11, n. 485, p. N.PAG, doi. 10.1126/scitranslmed.aat3005
    By:
    • Hernandez, Israel;
    • Luna, Gabriel;
    • Rauch, Jennifer N.;
    • Giroux, Michel;
    • Boctor, Daniel;
    • Sibih, Youssef E.;
    • Kang, Alexander A.;
    • Hinman, Cassidy R.;
    • Cerovac, Vesna;
    • Guzman, Elmer;
    • Zhou, Honjun;
    • Fisher, Steven K.;
    • Kosik, Kenneth S.;
    • Reis, Surya A.;
    • Haggarty, Stephen J.;
    • Karch, Celeste M.;
    • Storm, Nadia J.;
    • Diaz, Antonio;
    • Kaushik, Susmita;
    • Cuervo, Ana M.
    Publication type:
    Article