Works matching IS 19466234 AND DT 2011 AND VI 3 AND IP 97
Results: 5
A Tale of Two SCIDs.
- Published in:
- Science Translational Medicine, 2011, v. 3, n. 97, p. 1, doi. 10.1126/scitranslmed.3002594
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- Publication type:
- Article
Hematopoietic Stem Cell Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Leads to Long-Term Immunological Recovery and Metabolic Correction.
- Published in:
- Science Translational Medicine, 2011, v. 3, n. 97, p. 1, doi. 10.1126/scitranslmed.3002716
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- Publication type:
- Article
Potent Kinetic Stabilizers That Prevent Transthyretin-Mediated Cardiomyocyte Proteotoxicity.
- Published in:
- Science Translational Medicine, 2011, v. 3, n. 97, p. 1, doi. 10.1126/scitranslmed.3002473
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- Publication type:
- Article
Herding CATS.
- Published in:
- Science Translational Medicine, 2011, v. 3, n. 97, p. 1, doi. 10.1126/scitranslmed.3002837
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- Publication type:
- Article
Long-Term Persistence of a Polyclonal T Cell Repertoire After Gene Therapy for X-Linked Severe Combined Immunodeficiency.
- Published in:
- Science Translational Medicine, 2011, v. 3, n. 97, p. 1, doi. 10.1126/scitranslmed.3002715
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- Publication type:
- Article