Works matching IS 15250016 AND DT 2015 AND VI 23 AND IP 1

Results: 27

A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 192, doi. 10.1038/mt.2014.200

By:

Mendell, Jerry R;
Sahenk, Zarife;
Malik, Vinod;
Gomez, Ana M;
Flanigan, Kevin M;
Lowes, Linda P;
Alfano, Lindsay N;
Berry, Katherine;
Meadows, Eric;
Lewis, Sarah;
Braun, Lyndsey;
Shontz, Kim;
Rouhana, Maria;
Clark, Kelly Reed;
Rosales, Xiomara Q;
Al-Zaidy, Samiah;
Govoni, Alessandra;
Rodino-Klapac, Louise R;
Hogan, Mark J;
Kaspar, Brian K

Publication type:

Article

The Molecular Therapy Family: Past, Present, and Future.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 1, doi. 10.1038/mt.2014.227

By:

Ylä-Herttuala, Seppo

Publication type:

Article

Encapsulated Stem Cells Loaded With Hyaluronidase-expressing Oncolytic Virus for Brain Tumor Therapy.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 108, doi. 10.1038/mt.2014.204

By:

Martinez-Quintanilla, Jordi;
He, Derek;
Wakimoto, Hiroaki;
Alemany, Ramon;
Shah, Khalid

Publication type:

Article

Baculovirus-Mediated miRNA Regulation to Suppress Hepatocellular Carcinoma Tumorigenicity and Metastasis.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 79, doi. 10.1038/mt.2014.126

By:

Chen, Chiu-Ling;
Wu, Jaw-Ching;
Chen, Guan-Yu;
Yuan, Pei-Hsiang;
Tseng, Yen-Wen;
Li, Kuei-Chang;
Hwang, Shiaw-Min;
Hu, Yu-Chen

Publication type:

Article

In This Issue.

Published in:: Molecular Therapy, 2015, v. 23, n. 1, p. 2, doi. 10.1038/mt.2014.228
Publication type:: Article

Genome-wide Computational Analysis Reveals Cardiomyocyte-specific Transcriptional Cis-regulatory Motifs That Enable Efficient Cardiac Gene Therapy.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 43, doi. 10.1038/mt.2014.178

By:

Rincon, Melvin Y;
Sarcar, Shilpita;
Danso-Abeam, Dina;
Keyaerts, Marleen;
Matrai, Janka;
Samara-Kuko, Ermira;
Acosta-Sanchez, Abel;
Athanasopoulos, Takis;
Dickson, George;
Lahoutte, Tony;
De Bleser, Pieter;
VandenDriessche, Thierry;
Chuah, Marinee K

Publication type:

Article

Mesenchymal Stem/Stromal Cells Protect the Ocular Surface by Suppressing Inflammation in an Experimental Dry Eye.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 139, doi. 10.1038/mt.2014.159

By:

Lee, Min Joung;
Ko, Ah Young;
Ko, Jung Hwa;
Lee, Hyun Ju;
Kim, Mee Kum;
Wee, Won Ryang;
Khwarg, Sang In;
Oh, Joo Youn

Publication type:

Article

An AAVS1-Targeted Minigene Platform for Correction of iPSCs From All Five Types of Chronic Granulomatous Disease.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 147, doi. 10.1038/mt.2014.195

By:

Merling, Randall K;
Sweeney, Colin L;
Chu, Jessica;
Bodansky, Aaron;
Choi, Uimook;
Priel, Debra Long;
Kuhns, Douglas B;
Wang, Hongmei;
Vasilevsky, Sam;
De Ravin, Suk See;
Winkler, Thomas;
Dunbar, Cynthia E;
Zou, Jizhong;
Zarember, Kol A;
Gallin, John I;
Holland, Steven M;
Malech, Harry L

Publication type:

Article

First-in-man Study of Western Reserve Strain Oncolytic Vaccinia Virus: Safety, Systemic Spread, and Antitumor Activity.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 202, doi. 10.1038/mt.2014.194

By:

Zeh, Herbert J;
Downs-Canner, Stephanie;
McCart, J Andrea;
Guo, Zong Sheng;
Rao, Uma N M;
Ramalingam, Lekshmi;
Thorne, Stephen H;
Jones, Heather L;
Kalinski, Pawel;
Wieckowski, Eva;
O'Malley, Mark E;
Daneshmand, Manijeh;
Hu, Kang;
Bell, John C;
Hwang, Tae-Ho;
Moon, Anne;
Breitbach, Caroline J;
Kirn, David H;
Bartlett, David L

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2015, v. 23, n. 1, p. 3, doi. 10.1038/mt.2014.229
Publication type:: Article

Engager T Cells: A New Class of Antigen-specific T Cells That Redirect Bystander T Cells.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 171, doi. 10.1038/mt.2014.156

By:

Iwahori, Kota;
Kakarla, Sunitha;
Velasquez, Mireya P;
Yu, Feng;
Yi, Zongzhen;
Gerken, Claudia;
Song, Xiao-Tong;
Gottschalk, Stephen

Publication type:

Article

Graft Versus Leukemia Response Without Graft-versus-host Disease Elicited By Adoptively Transferred Multivirus-specific T-cells.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 179, doi. 10.1038/mt.2014.192

By:

Melenhorst, Jan J;
Castillo, Paul;
Hanley, Patrick J;
Keller, Michael D;
Krance, Robert A;
Margolin, Judith;
Leen, Ann M;
Heslop, Helen E;
Barrett, A John;
Rooney, Cliona M;
Bollard, Catherine M

Publication type:

Article

Treatment of CD33-directed Chimeric Antigen Receptor-modified T Cells in One Patient With Relapsed and Refractory Acute Myeloid Leukemia.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 184, doi. 10.1038/mt.2014.164

By:

Wang, Quan-shun;
Wang, Yao;
Lv, Hai-yan;
Han, Qing-wang;
Fan, Hui;
Guo, Bo;
Wang, Li-li;
Han, Wei-dong

Publication type:

Article

A Functional Variant of Elafin With Improved Anti-inflammatory Activity for Pulmonary Inflammation.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 24, doi. 10.1038/mt.2014.162

By:

Small, Donna M;
Zani, Marie-Louise;
Quinn, Derek J;
Dallet-Choisy, Sandrine;
Glasgow, Arlene MA;
O'Kane, Cecilia;
McAuley, Danny F;
McNally, Paul;
Weldon, Sinéad;
Moreau, Thierry;
Taggart, Clifford C

Publication type:

Article

Fractalkine Over Expression Suppresses α-Synuclein-mediated Neurodegeneration.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 17, doi. 10.1038/mt.2014.175

By:

Nash, Kevin R;
Moran, Peter;
Finneran, Dylan J;
Hudson, Charles;
Robinson, Jesse;
Morgan, Dave;
Bickford, Paula C

Publication type:

Article

Antitumor Activity of miR-1280 in Melanoma by Regulation of Src.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 71, doi. 10.1038/mt.2014.176

By:

Sun, Vera;
Zhou, Wen B;
Nosrati, Mehdi;
Majid, Shahana;
Thummala, Suresh;
de Semir, David;
Bezrookove, Vladimir;
de Feraudy, Sebastien;
Chun, Liane;
Schadendorf, Dirk;
Debs, Robert;
Kashani-Sabet, Mohammed;
Dar, Altaf A

Publication type:

Article

miR-382 Inhibits Osteosarcoma Metastasis and Relapse by Targeting Y Box-Binding Protein 1.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 89, doi. 10.1038/mt.2014.197

By:

Xu, Meng;
Jin, Hua;
Xu, Cheng-Xiong;
Sun, Bo;
Song, Zhi-Gang;
Bi, Wen-Zhi;
Wang, Yan

Publication type:

Article

Corrigendum to 'Use of miRNA Response Sequences to Block Off-target Replication and Increase the Safety of an Unattenuated, Glioblastoma-targeted Oncolytic HSV'.

Published in:: Molecular Therapy, 2015, v. 23, n. 1, p. 215, doi. 10.1038/mt.2014.216
Publication type:: Article

SCL/TAL1-mediated Transcriptional Network Enhances Megakaryocytic Specification of Human Embryonic Stem Cells.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 158, doi. 10.1038/mt.2014.196

By:

Toscano, Miguel G;
Navarro-Montero, Oscar;
Ayllon, Veronica;
Ramos-Mejia, Veronica;
Guerrero-Carreno, Xiomara;
Bueno, Clara;
Romero, Tamara;
Lamolda, Mar;
Cobo, Marien;
Martin, Francisco;
Menendez, Pablo;
Real, Pedro J

Publication type:

Article

Interventional Magnetic Resonance Imaging-guided Cell Transplantation Into the Brain With Radially Branched Deployment.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 119, doi. 10.1038/mt.2014.155

By:

Silvestrini, Matthew T;
Yin, Dali;
Martin, Alastair J;
Coppes, Valerie G;
Mann, Preeti;
Larson, Paul S;
Starr, Philip A;
Zeng, Xianmin;
Gupta, Nalin;
Panter, S S;
Desai, Tejal A;
Lim, Daniel A

Publication type:

Article

EZH2 Modulates Angiogenesis In Vitro and in a Mouse Model of Limb Ischemia.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 32, doi. 10.1038/mt.2014.163

By:

Mitić, Tijana;
Caporali, Andrea;
Floris, Ilaria;
Meloni, Marco;
Marchetti, Micol;
Urrutia, Raul;
Angelini, Gianni D;
Emanueli, Costanza

Publication type:

Article

Use of miRNA Response Sequences to Block Off-target Replication and Increase the Safety of an Unattenuated, Glioblastoma-targeted Oncolytic HSV.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 99, doi. 10.1038/mt.2014.177

By:

Mazzacurati, Lucia;
Marzulli, Marco;
Reinhart, Bonnie;
Miyagawa, Yoshitaka;
Uchida, Hiroaki;
Goins, William F;
Li, Aofei;
Kaur, Balveen;
Caligiuri, Michael;
Cripe, Timothy;
Chiocca, Nino;
Amankulor, Nduka;
Cohen, Justus B;
Glorioso, Joseph C;
Grandi, Paola

Publication type:

Article

CD133-targeted Gene Transfer Into Long-term Repopulating Hematopoietic Stem Cells.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 63, doi. 10.1038/mt.2014.173

By:

Brendel, Christian;
Goebel, Benjamin;
Daniela, Abriss;
Brugman, Martijn;
Kneissl, Sabrina;
Schwäble, Joachim;
Kaufmann, Kerstin B;
Müller-Kuller, Uta;
Kunkel, Hana;
Chen-Wichmann, Linping;
Abel, Tobias;
Serve, Hubert;
Bystrykh, Leonid;
Buchholz, Christian J;
Grez, Manuel

Publication type:

Article

Widespread and Efficient Transduction of Spinal Cord and Brain Following Neonatal AAV Injection and Potential Disease Modifying Effect in ALS Mice.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 53, doi. 10.1038/mt.2014.180

By:

Ayers, Jacob I;
Fromholt, Susan;
Sinyavskaya, Olga;
Siemienski, Zoe;
Rosario, Awilda M;
Li, Andrew;
Crosby, Keith W;
Cruz, Pedro E;
DiNunno, Nadia M;
Janus, Christopher;
Ceballos-Diaz, Carolina;
Borchelt, David R;
Golde, Todd E;
Chakrabarty, Paramita;
Levites, Yona

Publication type:

Article

Targeting Channelrhodopsin-2 to ON-bipolar Cells With Vitreally Administered AAV Restores ON and OFF Visual Responses in Blind Mice.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 7, doi. 10.1038/mt.2014.154

By:

Macé, Emilie;
Caplette, Romain;
Marre, Olivier;
Sengupta, Abhishek;
Chaffiol, Antoine;
Barbe, Peggy;
Desrosiers, Mélissa;
Bamberg, Ernst;
Sahel, Jose-Alain;
Picaud, Serge;
Duebel, Jens;
Dalkara, Deniz

Publication type:

Article

Hitting the Target Without Pulling the Trigger.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 4, doi. 10.1038/mt.2014.230

By:

VandenDriessche, Thierry;
Chuah, Marinee K

Publication type:

Article

Mesenchymal Stem Cells Improve Motor Functions and Decrease Neurodegeneration in Ataxic Mice.

Published in:

Molecular Therapy, 2015, v. 23, n. 1, p. 130, doi. 10.1038/mt.2014.143

By:

Jones, Jonathan;
Estirado, Alicia;
Redondo, Carolina;
Pacheco-Torres, Jesus;
Sirerol-Piquer, Maria-Salomé;
Garcia-Verdugo, José M;
Martinez, Salvador

Publication type:

Article