Works matching IS 15250016 AND DT 2014 AND VI 22 AND IP 4


Results: 25
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    In This Issue.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 688, doi. 10.1038/mt.2014.38
    Publication type:
    Article
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    Corrective GUSB Transfer to the Canine Mucopolysaccharidosis VII Brain.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 762, doi. 10.1038/mt.2013.283
    By:
    • Cubizolle, Aurelie;
    • Serratrice, Nicolas;
    • Skander, Nadia;
    • Colle, Marie-Anne;
    • Ibanes, Sandy;
    • Gennetier, Aurelie;
    • Bayo-Puxan, Neus;
    • Mazouni, Khalil;
    • Mennechet, Franck;
    • Joussemet, Beatrice;
    • Cherel, Yan;
    • Lajat, Yaouen;
    • Vite, Charles;
    • Bernex, Florence;
    • Kalatzis, Vasiliki;
    • Haskins, Mark E;
    • Kremer, Eric J
    Publication type:
    Article
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    Vascular Delivery of rAAVrh74.MCK.GALGT2 to the Gastrocnemius Muscle of the Rhesus Macaque Stimulates the Expression of Dystrophin and Laminin α2 Surrogates.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 713, doi. 10.1038/mt.2013.246
    By:
    • Chicoine, Louis G.;
    • Rodino-Klapac, Louise R.;
    • Shao, Guohong;
    • Xu, Rui;
    • Bremer, William G.;
    • Camboni, Marybeth;
    • Golden, Bethannie;
    • Montgomery, Chrystal L.;
    • Shontz, Kimberly;
    • Heller, Kristin N.;
    • Griffin, Danielle A.;
    • Lewis, Sarah;
    • Coley, Brian D.;
    • Walker, Christopher M.;
    • Clark, K. Reed;
    • Sahenk, Zarife;
    • Mendell, Jerry R.;
    • Martin, Paul T.
    Publication type:
    Article
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    Research Highlights.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 689, doi. 10.1038/mt.2014.39
    Publication type:
    Article
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    Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 4, p. 774, doi. 10.1038/mt.2014.3
    By:
    • Cesana, Daniela;
    • Ranzani, Marco;
    • Volpin, Monica;
    • Bartholomae, Cynthia;
    • Duros, Caroline;
    • Artus, Alexandre;
    • Merella, Stefania;
    • Benedicenti, Fabrizio;
    • Sergi Sergi, Lucia;
    • Sanvito, Francesca;
    • Brombin, Chiara;
    • Nonis, Alessandro;
    • Serio, Clelia Di;
    • Doglioni, Claudio;
    • von Kalle, Christof;
    • Schmidt, Manfred;
    • Cohen-Haguenauer, Odile;
    • Naldini, Luigi;
    • Montini, Eugenio
    Publication type:
    Article