Works matching IS 15250016 AND DT 2014 AND VI 22 AND IP 3

Results: 24

In This Issue.

Published in:: Molecular Therapy, 2014, v. 22, n. 3, p. 480, doi. 10.1038/mt.2014.9
Publication type:: Article

Research Highlights.

Published in:: Molecular Therapy, 2014, v. 22, n. 3, p. 481, doi. 10.1038/mt.2014.10
Publication type:: Article

Long-distance Axonal Transport of AAV9 Is Driven by Dynein and Kinesin-2 and Is Trafficked in a Highly Motile Rab7-positive Compartment.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 554, doi. 10.1038/mt.2013.237

By:

Castle, Michael J;
Perlson, Eran;
Holzbaur, Erika LF;
Wolfe, John H

Publication type:

Article

Clinical Assessment of a Novel Recombinant Simian Adenovirus ChAdOx1 as a Vectored Vaccine Expressing Conserved Influenza A Antigens.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 668, doi. 10.1038/mt.2013.284

By:

Antrobus, Richard D;
Coughlan, Lynda;
Berthoud, Tamara K;
Dicks, Matthew D;
Hill, Adrian VS;
Lambe, Teresa;
Gilbert, Sarah C

Publication type:

Article

Effective Intravenous Therapy for Neurodegenerative Disease With a Therapeutic Enzyme and a Peptide That Mediates Delivery to the Brain.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 547, doi. 10.1038/mt.2013.267

By:

Meng, Yu;
Sohar, Istvan;
Sleat, David E;
Richardson, Jason R;
Reuhl, Kenneth R;
Jenkins, Robert B;
Sarkar, Gobinda;
Lobel, Peter

Publication type:

Article

In Vivo Proof of Concept of Adoptive Immunotherapy for Hepatocellular Carcinoma Using Allogeneic Suicide Gene-modified Killer Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 634, doi. 10.1038/mt.2013.277

By:

Leboeuf, Céline;
Mailly, Laurent;
Wu, Tao;
Bour, Gaetan;
Durand, Sarah;
Brignon, Nicolas;
Ferrand, Christophe;
Borg, Christophe;
Tiberghien, Pierre;
Thimme, Robert;
Pessaux, Patrick;
Marescaux, Jacques;
Baumert, Thomas F.;
Robinet, Eric

Publication type:

Article

Targeted Drug Delivery to Intestinal Macrophages by Bioactive Nanovesicles Released from Grapefruit.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 522, doi. 10.1038/mt.2013.190

By:

Wang, Baomei;
Zhuang, Xiaoying;
Deng, Zhong-Bin;
Jiang, Hong;
Mu, Jingyao;
Wang, Qilong;
Xiang, Xiaoyu;
Guo, Haixun;
Zhang, Lifeng;
Dryden, Gerald;
Yan, Jun;
Miller, Donald;
Zhang, Huang-Ge

Publication type:

Article

Oral Delivery of Bioencapsulated Proteins Across Blood-Brain and Blood-Retinal Barriers.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 535, doi. 10.1038/mt.2013.273

By:

Kohli, Neha;
Westerveld, Donevan R;
Ayache, Alexandra C;
Verma, Amrisha;
Shil, Pollob;
Prasad, Tuhina;
Zhu, Ping;
Chan, Sic L;
Li, Qiuhong;
Daniell, Henry

Publication type:

Article

Chondrogenic Differentiation Increases Antidonor Immune Response to Allogeneic Mesenchymal Stem Cell Transplantation.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 655, doi. 10.1038/mt.2013.261

By:

Ryan, Aideen E;
Lohan, Paul;
O'Flynn, Lisa;
Treacy, Oliver;
Chen, Xizhe;
Coleman, Cynthia;
Shaw, Georgina;
Murphy, Mary;
Barry, Frank;
Griffin, Matthew D;
Ritter, Thomas

Publication type:

Article

The Impact of Unprotected T Cells in RNAi-based Gene Therapy for HIV-AIDS.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 596, doi. 10.1038/mt.2013.280

By:

Herrera-Carrillo, Elena;
Liu, Ying Poi;
Berkhout, Ben

Publication type:

Article

A Hitchhiker's Guide to the Blood-brain Barrier: In Trans Delivery of a Therapeutic Enzyme.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 483, doi. 10.1038/mt.2014.12

By:

Sands, Mark S

Publication type:

Article

AAV1.NT-3 Gene Therapy for Charcot-Marie-Tooth Neuropathy.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 511, doi. 10.1038/mt.2013.250

By:

Sahenk, Zarife;
Galloway, Gloria;
Clark, Kelly Reed;
Malik, Vinod;
Rodino-Klapac, Louise R;
Kaspar, Brian K.;
Chen, Lei;
Braganza, Cilwyn;
Montgomery, Chrystal;
Mendell, Jerry R

Publication type:

Article

Immunological and Antiviral Responses After Therapeutic DNA Immunization in Chronic Hepatitis B Patients Efficiently Treated by Analogues.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 675, doi. 10.1038/mt.2013.274

By:

Godon, O;
Fontaine, H;
Kahi, S;
Meritet, JF;
Scott-Algara, D;
Pol, S;
Michel, ML;
Bourgine, M

Publication type:

Article

Therapeutic Potential of Genetically Modified Mesenchymal Stem Cells After Neonatal Hypoxic-Ischemic Brain Damage.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 645, doi. 10.1038/mt.2013.260

By:

van Velthoven, Cindy TJ;
Braccioli, Luca;
Willemen, Hanneke LDM;
Kavelaars, Annemieke;
Heijnen, Cobi J

Publication type:

Article

From Gut to Brain: Bioencapsulated Therapeutic Protein Reduces Amyloid Load Upon Oral Delivery.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 485, doi. 10.1038/mt.2014.13

By:

Mäger, Imre;
Roberts, Thomas C;
Wood, Matthew JA;
EL Andaloussi, Samir

Publication type:

Article

Broad Therapeutic Benefit After RNAi Expression Vector Delivery to Deep Cerebellar Nuclei: Implications for Spinocerebellar Ataxia Type 1 Therapy.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 588, doi. 10.1038/mt.2013.279

By:

Keiser, Megan S;
Boudreau, Ryan L;
Davidson, Beverly L

Publication type:

Article

Development of a Web Course on Gene Therapy by the International Consortium of Gene Therapy.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 482, doi. 10.1038/mt.2014.11

By:

Tremblay, Jacques P;
Aartsma-Rus, Annemieke;
Bogdanove, Adam;
Ferreira, Marcello Bossois;
Bueren, Juan;
Huard, Johnny

Publication type:

Article

CARs Move To the Fast Lane.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 477, doi. 10.1038/mt.2014.8

By:

Davila, Marco L;
Papapetrou, Eirini P

Publication type:

Article

Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 607, doi. 10.1038/mt.2013.265

By:

Carbonaro, Denise A;
Zhang, Lin;
Jin, Xiangyang;
Montiel-Equihua, Claudia;
Geiger, Sabine;
Carmo, Marlene;
Cooper, Aaron;
Fairbanks, Lynette;
Kaufman, Michael L;
Sebire, Neil J;
Hollis, Roger P;
Blundell, Michael P;
Senadheera, Shantha;
Fu, Pei-Yu;
Sahaghian, Arineh;
Chan, Rebecca Y;
Wang, Xiaoyan;
Cornetta, Kenneth;
Thrasher, Adrian J;
Kohn, Donald B

Publication type:

Article

Design of a Novel Integration-deficient Lentivector Technology That Incorporates Genetic and Posttranslational Elements to Target Human Dendritic Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 575, doi. 10.1038/mt.2013.278

By:

Tareen, Semih U;
Kelley-Clarke, Brenna;
Nicolai, Christopher J;
Cassiano, Linda A;
Nelson, Lisa T;
Slough, Megan M;
Vin, Chintan D;
Odegard, Jared M;
Sloan, Derek D;
Van Hoeven, Neal;
Allen, James M;
Dubensky, Thomas W;
Robbins, Scott H

Publication type:

Article

Integration-deficient Lentiviral Vectors Expressing Codon-optimized R338L Human FIX Restore Normal Hemostasis in Hemophilia B Mice.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 567, doi. 10.1038/mt.2013.188

By:

Suwanmanee, Thipparat;
Hu, Genlin;
Gui, Tong;
Bartholomae, Cynthia C;
Kutschera, Ina;
von Kalle, Christof;
Schmidt, Manfred;
Monahan, Paul E;
Kafri, Tal

Publication type:

Article

Kinetics of Tumor Destruction by Chimeric Antigen Receptor-modified T Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 623, doi. 10.1038/mt.2013.262

By:

Anurathapan, Usanarat;
Chan, Robert C;
Hindi, Hakeem F;
Mucharla, Roopa;
Bajgain, Pradip;
Hayes, Brendan C;
Fisher, William E;
Heslop, Helen E;
Rooney, Cliona M;
Brenner, Malcolm K;
Leen, Ann M;
Vera, Juan F

Publication type:

Article

Parkinson's Disease Gene Therapy: Success by Design Meets Failure by Efficacy.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 487, doi. 10.1038/mt.2013.281

By:

Bartus, Raymond T;
Weinberg, Marc S;
Samulski, R. Jude

Publication type:

Article

Adeno-associated Virus-mediated Delivery of a Recombinant Single-chain Antibody Against Misfolded Superoxide Dismutase for Treatment of Amyotrophic Lateral Sclerosis.

Published in:

Molecular Therapy, 2014, v. 22, n. 3, p. 498, doi. 10.1038/mt.2013.239

By:

Patel, Priyanka;
Kriz, Jasna;
Gravel, Mathieu;
Soucy, Geneviève;
Bareil, Christine;
Gravel, Claude;
Julien, Jean-Pierre

Publication type:

Article