Works matching IS 15250016 AND DT 2014 AND VI 22 AND IP 2

Results: 29

In This Issue.

Published in:: Molecular Therapy, 2014, v. 22, n. 2, p. 242, doi. 10.1038/mt.2013.293
Publication type:: Article

Successful Gene Therapy in the RPGRIP1-deficient Dog: a Large Model of Cone-Rod Dystrophy.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 265, doi. 10.1038/mt.2013.232

By:

Lhériteau, Elsa;
Petit, Lolita;
Weber, Michel;
Le Meur, Guylène;
Deschamps, Jack-Yves;
Libeau, Lyse;
Mendes-Madeira, Alexandra;
Guihal, Caroline;
François, Achille;
Guyon, Richard;
Provost, Nathalie;
Lemoine, Françoise;
Papal, Samantha;
El-Amraoui, Aziz;
Colle, Marie-Anne;
Moullier, Philippe;
Rolling, Fabienne

Publication type:

Article

Plasmapheresis Eliminates the Negative Impact of AAV Antibodies on Microdystrophin Gene Expression Following Vascular Delivery.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 338, doi. 10.1038/mt.2013.244

By:

Chicoine, LG;
Montgomery, CL;
Bremer, WG;
Shontz, KM;
Griffin, DA;
Heller, KN;
Lewis, S;
Malik, V;
Grose, WE;
Shilling, CJ;
Campbell, KJ;
Preston, TJ;
Coley, BD;
Martin, PT;
Walker, CM;
Clark, KR;
Sahenk, Z;
Mendell, JR;
Rodino-Klapac, LR

Publication type:

Article

Morpholino Treatment Improves Muscle Function and Pathology of Pitx1 Transgenic Mice.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 390, doi. 10.1038/mt.2013.263

By:

Pandey, Sachchida Nand;
Lee, Yi-Chien;
Yokota, Toshifumi;
Chen, Yi-Wen

Publication type:

Article

Harnessing the Immune System to Potentiate Oncolytics.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 239, doi. 10.1038/mt.2013.295

By:

Gottschalk, Stephen;
Rooney, Cliona M

Publication type:

Article

Extensive Ex Vivo Expansion of Functional Human Erythroid Precursors Established From Umbilical Cord Blood Cells by Defined Factors.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 451, doi. 10.1038/mt.2013.201

By:

Huang, Xiaosong;
Shah, Siddharth;
Wang, Jing;
Ye, Zhaohui;
Dowey, Sarah N;
Tsang, Kit Man;
Mendelsohn, Laurel G;
Kato, Gregory J;
Kickler, Thomas S;
Cheng, Linzhao

Publication type:

Article

Repression of Choroidal Neovascularization Through Actin Cytoskeleton Pathways by MicroRNA-24.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 378, doi. 10.1038/mt.2013.243

By:

Zhou, Qinbo;
Anderson, Chastain;
Zhang, Hongmei;
Li, Xinyu;
Inglis, Fiona;
Jayagopal, Ashwath;
Wang, Shusheng

Publication type:

Article

Treatment of Type 1 Myotonic Dystrophy by Engineering Site-specific RNA Endonucleases that Target (CUG)<sub>n</sub> Repeats.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 312, doi. 10.1038/mt.2013.251

By:

Zhang, Wenjing;
Wang, Yang;
Dong, Shuyun;
Choudhury, Rajarshi;
Jin, Yongfeng;
Wang, Zefeng

Publication type:

Article

Discovery of siRNA Lipid Nanoparticles to Transfect Suspension Leukemia Cells and Provide In Vivo Delivery Capability.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 359, doi. 10.1038/mt.2013.210

By:

He, Wei;
Bennett, Michael J;
Luistro, Leopoldo;
Carvajal, Daisy;
Nevins, Thomas;
Smith, Melissa;
Tyagi, Gaurav;
Cai, James;
Wei, Xin;
Lin, Tai-An;
Heimbrook, David C;
Packman, Kathryn;
Boylan, John F

Publication type:

Article

AAV9-mediated Expression of a Non-self Protein in Nonhuman Primate Central Nervous System Triggers Widespread Neuroinflammation Driven by Antigen-presenting Cell Transduction.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 329, doi. 10.1038/mt.2013.266

By:

Samaranch, Lluis;
Sebastian, Waldy San;
Kells, Adrian P;
Salegio, Ernesto A;
Heller, Gregory;
Bringas, John R;
Pivirotto, Philip;
DeArmond, Stephen;
Forsayeth, John;
Bankiewicz, Krystof S

Publication type:

Article

TRIM5α Variations Influence Transduction Efficiency With Lentiviral Vectors in Both Human and Rhesus CD34<sup>+</sup> Cells In Vitro and In Vivo.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 348, doi. 10.1038/mt.2013.256

By:

Evans, Molly E;
Kumkhaek, Chutima;
Hsieh, Matthew M;
Donahue, Robert E;
Tisdale, John F;
Uchida, Naoya

Publication type:

Article

One MicroRNA Controls Both Angiogenesis and TLR-mediated Innate Immunity to Nucleic Acids.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 249, doi. 10.1038/mt.2013.299

By:

Rogers, Geoffrey L;
Herzog, Roland W

Publication type:

Article

Genetically Modified Hematopoietic Stem Cell Transplantation for HIV-1-infected Patients: Can We Achieve a Cure?

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 257, doi. 10.1038/mt.2013.264

By:

Younan, Patrick;
Kowalski, John;
Kiem, Hans-Peter

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2014, v. 22, n. 2, p. 243, doi. 10.1038/mt.2013.294
Publication type:: Article

Therapeutic Evaluation of Epstein-Barr Virus-encoded Latent Membrane Protein-1 Targeted DNAzyme for Treating of Nasopharyngeal Carcinomas.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 371, doi. 10.1038/mt.2013.257

By:

Cao, Ya;
Yang, Lifang;
Jiang, Wuzhong;
Wang, Xiaoyi;
Liao, Weihua;
Tan, Guolin;
Liao, Yuping;
Qiu, Yuanzheng;
Feng, Deyun;
Tang, Faqing;
Hou, Bob L;
Zhang, Ling;
Fu, Jia;
He, Fengjiao;
Liu, Xiaoyu;
Jiang, Wenjuan;
Yang, Tubao;
Sun, Lun-Quan

Publication type:

Article

False-Positive HIV PCR Test Following Ex Vivo Lentiviral Gene Transfer Treatment of X-linked Severe Combined Immunodeficiency Vector.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 244, doi. 10.1038/mt.2013.296

By:

De Ravin, Suk See;
Gray, John T;
Throm, Robert E;
Spindler, Jon;
Kearney, Mary;
Wu, Xiaolin;
Coffin, John M;
Hughes, Stephen H;
Malderelli, Frank;
Sorrentino, Brian P;
Malech, Harry L

Publication type:

Article

Development of Preclinical Models for Immunogene Therapy of Brain Cancer: It's Not Monkey Business!

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 248, doi. 10.1038/mt.2013.298

By:

Lesniak, Maciej S

Publication type:

Article

Overexpressing Sonic Hedgehog Peptide Restores Periosteal Bone Formation in a Murine Bone Allograft Transplantation Model.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 430, doi. 10.1038/mt.2013.222

By:

Huang, Chunlan;
Tang, Minghui;
Yehling, Eric;
Zhang, Xinping

Publication type:

Article

An Efficient Antiviral Strategy for Targeting Hepatitis B Virus Genome Using Transcription Activator-Like Effector Nucleases.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 303, doi. 10.1038/mt.2013.212

By:

Chen, Jieliang;
Zhang, Wen;
Lin, Junyu;
Wang, Fan;
Wu, Min;
Chen, Cuncun;
Zheng, Ye;
Peng, Xiuhua;
Li, Jianhua;
Yuan, Zhenghong

Publication type:

Article

A Novel Cancer Therapeutic Using Thrombospondin 1 in Dendritic Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 292, doi. 10.1038/mt.2013.236

By:

Weng, Tzu-Yang;
Huang, Shih-Shien;
Yen, Meng-Chi;
Lin, Chi-Chen;
Chen, Yi-Ling;
Lin, Chiu-Mei;
Chen, Wei-Ching;
Wang, Chih-Yang;
Chang, Jang-Yang;
Lai, Ming-Derg

Publication type:

Article

There Must Be a Way Out of Here: Identifying a Safe and Efficient Combination of Promoter, Transgene, and Vector Backbone for Gene Therapy of Neurological Disease.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 246, doi. 10.1038/mt.2013.297

By:

Lowenstein, PR;
Yadav, Viveka Nand;
Chockley, Peter;
Castro, Maria

Publication type:

Article

Neurotrophin 3 Transduction Augments Remyelinating and Immunomodulatory Capacity of Neural Stem Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 440, doi. 10.1038/mt.2013.241

By:

Yang, Jingxian;
Yan, Yaping;
Xia, Yang;
Kang, Tingguo;
Li, Xing;
Ciric, Bogoljub;
Xu, Hui;
Rostami, Abdolmohamad;
Zhang, Guang-Xian

Publication type:

Article

The Clinical Potential of Targeted Nanomedicine: Delivering to Cancer Stem-like Cells.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 278, doi. 10.1038/mt.2013.231

By:

Kim, Sang-Soo;
Rait, Antonina;
Rubab, Farwah;
Rao, Abhi K;
Kiritsy, Michael C;
Pirollo, Kathleen F;
Wang, Shangzi;
Weiner, Louis M;
Chang, Esther H

Publication type:

Article

Oncolytic Virotherapy and Immunogenic Cancer Cell Death: Sharpening the Sword for Improved Cancer Treatment Strategies.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 251, doi. 10.1038/mt.2013.220

By:

Workenhe, Samuel T;
Mossman, Karen L

Publication type:

Article

TNF-α Gene Silencing Using Polymerized siRNA/Thiolated Glycol Chitosan Nanoparticles for Rheumatoid Arthritis.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 397, doi. 10.1038/mt.2013.245

By:

Lee, So Jin;
Lee, Aeju;
Hwang, Seung Rim;
Park, Jong-Sung;
Jang, Jiyeon;
Huh, Myung Sook;
Jo, Dong-Gyu;
Yoon, Soo-Young;
Byun, Youngro;
Kim, Sun Hwa;
Kwon, Ick Chan;
Youn, Inchan;
Kim, Kwangmeyung

Publication type:

Article

Maraba Virus as a Potent Oncolytic Vaccine Vector.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 420, doi. 10.1038/mt.2013.249

By:

Pol, Jonathan G;
Zhang, Liang;
Bridle, Byram W;
Stephenson, Kyle B;
Rességuier, Julien;
Hanson, Stephen;
Chen, Lan;
Kazdhan, Natasha;
Bramson, Jonathan L;
Stojdl, David F;
Wan, Yonghong;
Lichty, Brian D

Publication type:

Article

Intrathecal AAV Serotype 9-mediated Delivery of shRNA Against TRPV1 Attenuates Thermal Hyperalgesia in a Mouse Model of Peripheral Nerve Injury.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 409, doi. 10.1038/mt.2013.247

By:

Hirai, Takashi;
Enomoto, Mitsuhiro;
Kaburagi, Hidetoshi;
Sotome, Shinichi;
Yoshida-Tanaka, Kie;
Ukegawa, Madoka;
Kuwahara, Hiroya;
Yamamoto, Mariko;
Tajiri, Mio;
Miyata, Haruka;
Hirai, Yukihiko;
Tominaga, Makoto;
Shinomiya, Kenichi;
Mizusawa, Hidehiro;
Okawa, Atsushi;
Yokota, Takanori

Publication type:

Article

Ultrasound-activated Agents Comprised of 5FU-bearing Nanoparticles Bonded to Microbubbles Inhibit Solid Tumor Growth and Improve Survival.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 321, doi. 10.1038/mt.2013.259

By:

Burke, Caitlin W;
Alexander, Eben;
Timbie, Kelsie;
Kilbanov, Alexander L;
Price, Richard J

Publication type:

Article

Vaccine-elicited Human T Cells Recognizing Conserved Protein Regions Inhibit HIV-1.

Published in:

Molecular Therapy, 2014, v. 22, n. 2, p. 464, doi. 10.1038/mt.2013.248

By:

Borthwick, Nicola;
Ahmed, Tina;
Ondondo, Beatrice;
Hayes, Peter;
Rose, Annie;
Ebrahimsa, Umar;
Hayton, Emma-Jo;
Black, Antony;
Bridgeman, Anne;
Rosario, Maximillian;
Hill, Adrian VS;
Berrie, Eleanor;
Moyle, Sarah;
Frahm, Nicole;
Cox, Josephine;
Colloca, Stefano;
Nicosia, Alfredo;
Gilmour, Jill;
McMichael, Andrew J;
Dorrell, Lucy

Publication type:

Article