A New Series of Small Molecular Weight Compounds Induce Read Through of All Three Types of Nonsense Mutations in the ATM Gene.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1653, doi. 10.1038/mt.2013.150
- By:
- Publication type:
- Article
Works matching IS 15250016 AND DT 2013 AND VI 21 AND IP 9
Results: 23
1
2
Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1705, doi. 10.1038/mt.2013.106
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- Publication type:
- Article
3
The Novel Replication-defective Vaccinia Virus (Tiantan Strain)-based Hepatitis C Virus Vaccine Induces Robust Immunity in Macaques.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1787, doi. 10.1038/mt.2013.122
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- Publication type:
- Article
4
Research Highlights.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1643, doi. 10.1038/mt.2013.174
- Publication type:
- Article
5
Meganuclease-mediated Virus Self-cleavage Facilitates Tumor-specific Virus Replication.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1738, doi. 10.1038/mt.2013.117
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- Publication type:
- Article
6
Ultrasound-targeted Microbubble Destruction-mediated Gene Delivery Into Canine Livers.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1687, doi. 10.1038/mt.2013.107
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- Publication type:
- Article
7
Covert Warfare Against the Immune System: Decoy Capsids, Stealth Genomes, and Suppressors.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1648, doi. 10.1038/mt.2013.176
- By:
- Publication type:
- Article
8
Reading Frame Correction by Targeted Genome Editing Restores Dystrophin Expression in Cells From Duchenne Muscular Dystrophy Patients.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1718, doi. 10.1038/mt.2013.111
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- Publication type:
- Article
9
Modulation of CD8<sup>+</sup> T cell responses to AAV vectors with IgG-derived MHC class II epitopes.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1, doi. 10.1038/mt.2013.166
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- Publication type:
- Article
10
Generating SM(a)RTer Compounds for Translation Termination Suppression in A-T and Other Genetic Disorders.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1651, doi. 10.1038/mt.2013.177
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- Publication type:
- Article
11
Late Breaking Abstracts: Presented at the American Society of Gene & Cell Therapy's 16<sup>th</sup>Annual Meeting, May 15-18, 2013, Salt Lake City, Utah.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. e1, doi. 10.1038/mt.2013.140
- Publication type:
- Article
12
Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1695, doi. 10.1038/mt.2013.143
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- Publication type:
- Article
13
Third-party Mesenchymal Stem Cells Improved Human Islet Transplantation in a Humanized Diabetic Mouse Model.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1778, doi. 10.1038/mt.2013.147
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- Publication type:
- Article
14
The Evolution of Nonclinical Regulatory Science: Advanced Therapy Medicinal Products as a Paradigm.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1294, doi. 10.1038/mt.2013.175
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- Publication type:
- Article
15
Intrapleural Administration of AAV9 Improves Neural and Cardiorespiratory Function in Pompe Disease.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1661, doi. 10.1038/mt.2013.96
- By:
- Publication type:
- Article
16
Disruption of TAB1/p38α Interaction Using a Cell-permeable Peptide Limits Myocardial Ischemia/Reperfusion Injury.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1668, doi. 10.1038/mt.2013.90
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- Publication type:
- Article
17
Snail as a Potential Target Molecule in Cardiac Fibrosis: Paracrine Action of Endothelial Cells on Fibroblasts Through Snail and CTGF Axis.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1767, doi. 10.1038/mt.2013.146
- By:
- Publication type:
- Article
18
Therapeutic DNA Vaccination Using In Vivo Electroporation Followed by Standard of Care Therapy in Patients With Genotype 1 Chronic Hepatitis C.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1796, doi. 10.1038/mt.2013.119
- By:
- Publication type:
- Article
19
TP53-independent Function of miR-34a via HDAC1 and p21<sup>CIP1/WAF1</sup>.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1678, doi. 10.1038/mt.2013.148
- By:
- Publication type:
- Article
20
Suppression of Antiviral Innate Immunity by Sunitinib Enhances Oncolytic Virotherapy.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1749, doi. 10.1038/mt.2013.112
- By:
- Publication type:
- Article
21
Endothelial Differentiation of Adipose Tissue-Derived Mesenchymal Stromal Cells in Glioma Tumors: Implications for Cell-Based Therapy.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1758, doi. 10.1038/mt.2013.145
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- Publication type:
- Article
22
In This Issue.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1642, doi. 10.1038/mt.2013.173
- Publication type:
- Article
23
How to Design a Cell or Gene Therapy Clinical Trial: Advice from the FDA.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 9, p. 1639, doi. 10.1038/mt.2013.172
- By:
- Publication type:
- Article