Works matching IS 15250016 AND DT 2012 AND VI 20 AND IP 6

Results: 28

Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1131, doi. 10.1038/mt.2012.39

By:

Keeler, Allison M;
Conlon, Thomas;
Walter, Glenn;
Zeng, Huadong;
Shaffer, Scott A;
Dungtao, Fu;
Erger, Kirsten;
Cossette, Travis;
Tang, Qiushi;
Mueller, Christian;
Flotte, Terence R

Publication type:

Article

Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy.

Published in:: Molecular Therapy, 2012, v. 20, n. 6, p. 1287, doi. 10.1038/mt.2012.106
Publication type:: Article

Loss of miR-29 in Myoblasts Contributes to Dystrophic Muscle Pathogenesis.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1222, doi. 10.1038/mt.2012.35

By:

Wang, Lijun;
Zhou, Liang;
Jiang, Peiyong;
Lu, Leina;
Chen, Xiaona;
Lan, Huiyao;
Guttridge, Denis C;
Sun, Hao;
Wang, Huating

Publication type:

Article

PEGylated Polyplex With Optimized PEG Shielding Enhances Gene Introduction in Lungs by Minimizing Inflammatory Responses.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1196, doi. 10.1038/mt.2012.20

By:

Uchida, Satoshi;
Itaka, Keiji;
Chen, Qixian;
Osada, Kensuke;
Ishii, Takehiko;
Shibata, Masa-Aki;
Harada-Shiba, Mariko;
Kataoka, Kazunori

Publication type:

Article

Stem Cells and Regenerative Medicine in Lung Biology and Diseases.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1116, doi. 10.1038/mt.2012.37

By:

Lau, Allison N;
Goodwin, Meagan;
Kim, Carla F;
Weiss, Daniel J

Publication type:

Article

Ex Vivo Adenoviral Vector Gene Delivery Results in Decreased Vector-associated Inflammation Pre- and Post-lung Transplantation in the Pig.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1204, doi. 10.1038/mt.2012.57

By:

Yeung, Jonathan C;
Wagnetz, Dirk;
Cypel, Marcelo;
Rubacha, Matthew;
Koike, Terumoto;
Chun, Yi-Min;
Hu, Jim;
Waddell, Thomas K;
Hwang, David M;
Liu, Mingyao;
Keshavjee, Shaf

Publication type:

Article

Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1084, doi. 10.1038/mt.2012.93

By:

Corrigan-Curay, Jacqueline;
Cohen-Haguenauer, Odile;
O'Reilly, Marina;
Ross, Susan R.;
Fan, Hung;
Rosenberg, Naomi;
Somia, Nikunj;
King, Nancy;
Friedmann, Theodore;
Dunbar, Cynthia;
Aiuti, Alessandro;
Naldini, Luigi;
Baum, Christopher;
von Kalle, Christof;
Kiem, Hans-Peter;
Montini, Eugenio;
Bushman, Frederic;
Sorrentino, Brian P;
Carrondo, Manuel;
Malech, Harry

Publication type:

Article

Isolation and Optimization of Murine IL-10 Receptor Blocking Oligonucleotide Aptamers Using High-throughput Sequencing.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1242, doi. 10.1038/mt.2012.18

By:

Berezhnoy, Alexey;
Stewart, C. Andrew;
Mcnamara II, James O.;
Thiel, William;
Giangrande, Paloma;
Trinchieri, Giorgio;
Gilboa, Eli

Publication type:

Article

Advances in Cell and Gene-based Therapies for Cystic Fibrosis Lung Disease.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1108, doi. 10.1038/mt.2012.32

By:

Oakland, Mayumi;
Sinn, Patrick L;
McCray Jr, Paul B

Publication type:

Article

Foamy Virus Vector-mediated Gene Correction of a Mouse Model of Wiskott-Aldrich Syndrome.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1270, doi. 10.1038/mt.2011.282

By:

Uchiyama, Toru;
Adriani, Marsilio;
Jagadeesh, G Jayashree;
Paine, Adam;
Candotti, Fabio

Publication type:

Article

Myocardial Repair and Regeneration: Bone Marrow or Cardiac Stem Cells?

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1102, doi. 10.1038/mt.2012.99

By:

Oldroyd, Keith G;
Berry, Colin;
Bartunek, Jozef

Publication type:

Article

In This Issue.

Published in:: Molecular Therapy, 2012, v. 20, n. 6, p. 1082, doi. 10.1038/mt.2012.105
Publication type:: Article

The Challenge of Using Gene- or Cell-Based Therapies to Treat Lung Disease.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1077, doi. 10.1038/mt.2012.91

By:

Crystal, Ronald G

Publication type:

Article

Cell Membrane-associated Heparan Sulfate Is a Receptor for Prototype Foamy Virus in Human, Monkey, and Rodent Cells.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1158, doi. 10.1038/mt.2012.41

By:

Nasimuzzaman, Md;
Persons, Derek A

Publication type:

Article

Novel Therapies, High-Risk Pediatric Research, and the Prospect of Benefit: Learning from the Ethical Disagreements.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1095, doi. 10.1038/mt.2012.90

By:

de Melo-Martín, Inmaculada;
Sondhi, Dolan;
Crystal, Ronald G

Publication type:

Article

miR-29 Inhibits Bleomycin-induced Pulmonary Fibrosis in Mice.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1251, doi. 10.1038/mt.2012.36

By:

Xiao, Jun;
Meng, Xiao-Ming;
Huang, Xiao R;
Chung, Arthur CK;
Feng, Yu-Lin;
Hui, David SC;
Yu, Cheuk-Man;
Sung, Joseph JY;
Lan, Hui Y

Publication type:

Article

Advances in Foamy Virus Vector Technology and Disease Correction Could Speed the Path to Clinical Application.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1105, doi. 10.1038/mt.2012.97

By:

Verhoeyen, Els

Publication type:

Article

ORFV: A Novel Oncolytic and Immune Stimulating Parapoxvirus Therapeutic.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1148, doi. 10.1038/mt.2011.301

By:

Rintoul, Julia L;
Lemay, Chantal G;
Tai, Lee-Hwa;
Stanford, Marianne M;
Falls, Theresa J;
de Souza, Christiano T;
Bridle, Byram W;
Daneshmand, Manijeh;
Ohashi, Pamela S;
Wan, Yonghong;
Lichty, Brian D;
Mercer, Andrew A;
Auer, Rebecca C;
Atkins, Harold L;
Bell, John C

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2012, v. 20, n. 6, p. 1083, doi. 10.1038/mt.2012.104
Publication type:: Article

Integration Frequency and Intermolecular Recombination of rAAV Vectors in Non-human Primate Skeletal Muscle and Liver.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1177, doi. 10.1038/mt.2012.47

By:

Nowrouzi, Ali;
Penaud-Budloo, Magalie;
Kaeppel, Christine;
Appelt, Uwe;
Le Guiner, Caroline;
Moullier, Philippe;
Kalle, Christof von;
Snyder, Richard O;
Schmidt, Manfred

Publication type:

Article

Lentiviral Vector Induced Insertional Haploinsufficiency of Ebf1 Causes Murine Leukemia.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1187, doi. 10.1038/mt.2012.59

By:

Heckl, Dirk;
Schwarzer, Adrian;
Haemmerle, Reinhard;
Steinemann, Doris;
Rudolph, Cornelia;
Skawran, Britta;
Knoess, Sabine;
Krause, Johanna;
Li, Zhixiong;
Schlegelberger, Brigitte;
Baum, Christopher;
Modlich, Ute

Publication type:

Article

A New Therapeutic Approach Using a Schizophyllan-based Drug Delivery System for Inflammatory Bowel Disease.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1234, doi. 10.1038/mt.2012.24

By:

Takedatsu, Hidetoshi;
Mitsuyama, Keiichi;
Mochizuki, Shinichi;
Kobayashi, Teppei;
Sakurai, Kazuo;
Takeda, Hiroshi;
Fujiyama, Yoshihide;
Koyama, Yoshikazu;
Nishihira, Jun;
Sata, Michio

Publication type:

Article

Expression of Immunomodulatory Neutrophil-activating Protein of Helicobacter pylori Enhances the Antitumor Activity of Oncolytic Measles Virus.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1139, doi. 10.1038/mt.2012.4

By:

Iankov, Ianko D;
Allen, Cory;
Federspiel, Mark J;
Myers, Rae M;
Peng, Kah Whye;
Ingle, James N;
Russell, Stephen J;
Galanis, Evanthia

Publication type:

Article

Engineering Multiple U7snRNA Constructs to Induce Single and Multiexon-skipping for Duchenne Muscular Dystrophy.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1212, doi. 10.1038/mt.2012.26

By:

Goyenvalle, Aurélie;
Wright, Jordan;
Babbs, Arran;
Wilkins, Vivienne;
Garcia, Luis;
Davies, Kay E

Publication type:

Article

A Small-molecule-controlled System for Efficient Pseudotyping of Prototype Foamy Virus Vectors.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1167, doi. 10.1038/mt.2012.61

By:

Ho, Yu-Ping;
Schnabel, Viktor;
Swiersy, Anka;
Stirnnagel, Kristin;
Lindemann, Dirk

Publication type:

Article

Cellular Therapy With Ixmyelocel-T to Treat Critical Limb Ischemia: The Randomized, Double-blind, Placebo-controlled RESTORE-CLI Trial.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1280, doi. 10.1038/mt.2012.52

By:

Powell, Richard J;
Marston, William A;
Berceli, Scott A;
Guzman, Raul;
Henry, Timothy D;
Longcore, Amy T;
Stern, Theresa P;
Watling, Sharon;
Bartel, Ronnda L

Publication type:

Article

Lipid-based Nanoparticle Delivery of Pre-miR-107 Inhibits the Tumorigenicity of Head and Neck Squamous Cell Carcinoma.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1261, doi. 10.1038/mt.2012.67

By:

Piao, Longzhu;
Zhang, Manchao;
Datta, Jharna;
Xie, Xiujie;
Su, Tizhi;
Li, Hong;
Teknos, Theodoros N;
Pan, Quintin

Publication type:

Article

It's Time to End RAC Review of Gene Therapy Protocols.

Published in:

Molecular Therapy, 2012, v. 20, n. 6, p. 1079, doi. 10.1038/mt.2012.92

By:

McGarrity, Gerard J

Publication type:

Article