Works matching IS 15250016 AND DT 2012 AND VI 20 AND IP 10

Results: 24

1α,25(OH)<sub>2</sub>-Vitamin D3 Increases Dysferlin Expression in vitro and in a Human Clinical Trial.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1988, doi. 10.1038/mt.2012.156

By:

Luna, Noemi De;
Díaz-Manera, Jordi;
Paradas, Carmen;
Iturriaga, Cristina;
Rojas-García, Ricardo;
Araque, Josefa;
Genebriera, Mireia;
Gich, Ignasi;
Illa, Isabel;
Gallardo, Eduard

Publication type:

Article

Conditional Negative Selection of Gene-Modified Hematopoietic Stem Cells.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1841, doi. 10.1038/mt.2012.195

By:

Baum, Christopher

Publication type:

Article

In This Issue.

Published in:: Molecular Therapy, 2012, v. 20, n. 10, p. 1834, doi. 10.1038/mt.2012.198
Publication type:: Article

Thymidine Kinase Suicide Gene-mediated Ganciclovir Ablation of Autologous Gene-modified Rhesus Hematopoiesis.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1932, doi. 10.1038/mt.2012.166

By:

Barese, Cecilia N;
Krouse, Allen E;
Metzger, Mark E;
King, Connor A;
Traversari, Catia;
Marini, Frank C;
Donahue, Robert E;
Dunbar, Cynthia E

Publication type:

Article

Ribosomal DNA Integrating rAAV-rDNA Vectors Allow for Stable Transgene Expression.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1912, doi. 10.1038/mt.2012.164

By:

Lisowski, Leszek;
Lau, Ashley;
Wang, Zhongya;
Zhang, Yue;
Zhang, Feijie;
Grompe, Markus;
Kay, Mark A

Publication type:

Article

AAV Vectors for the Nucleolus.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1842, doi. 10.1038/mt.2012.193

By:

Russell, David W

Publication type:

Article

Phase II Trial of Intravenous Administration of Reolysin<sup>®</sup> (Reovirus Serotype-3-dearing Strain) in Patients with Metastatic Melanoma.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1998, doi. 10.1038/mt.2012.146

By:

Galanis, Evanthia;
Markovic, Svetomir N;
Suman, Vera J;
Nuovo, Gerard J;
Vile, Richard G;
Kottke, Timothy J;
Nevala, Wendy K;
Thompson, Michael A;
Lewis, Jean E;
Rumilla, Kandelaria M;
Roulstone, Victoria;
Harrington, Kevin;
Linette, Gerald P;
Maples, William J;
Coffey, Matt;
Zwiebel, James;
Kendra, Kari

Publication type:

Article

Local In Vivo GSK3β Knockdown Promotes Pancreatic β Cell and Acinar Cell Regeneration in 90% Pancreatectomized Rat.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1944, doi. 10.1038/mt.2012.112

By:

Figeac, Florence;
Ilias, Anissa;
Bailbe, Danielle;
Portha, Bernard;
Movassat, Jamileh

Publication type:

Article

High-efficiency Transduction of Rhesus Hematopoietic Repopulating Cells by a Modified HIV1-based Lentiviral Vector.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1882, doi. 10.1038/mt.2012.159

By:

Uchida, Naoya;
Hargrove, Phillip W.;
Lap, Coen J.;
Evans, Molly E.;
Phang, Oswald;
Bonifacino, Aylin C.;
Krouse, Allen E.;
Metzger, Mark E.;
Nguyen, Anh-Dao;
Hsieh, Matthew M.;
Wolfsberg, Tyra G.;
Donahue, Robert E.;
Persons, Derek A.;
Tisdale, John F.

Publication type:

Article

Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1831, doi. 10.1038/mt.2012.194

By:

Ylä-Herttuala, Seppo

Publication type:

Article

Administration of Anti-CD3 Antibodies Modulates the Immune Response to an Infusion of α-glucosidase in Mice.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1924, doi. 10.1038/mt.2012.133

By:

Ohashi, Toya;
Iizuka, Sayoko;
Shimada, Yohta;
Higuchi, Takashi;
Eto, Yoshikatsu;
Ida, Hiroyuki;
Kobayashi, Hiroshi

Publication type:

Article

AAV Vectors Containing rDNA Homology Display Increased Chromosomal Integration and Transgene Persistence.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1902, doi. 10.1038/mt.2012.157

By:

Wang, Zhongya;
Lisowski, Leszek;
Finegold, Milton J;
Nakai, Hiroyuki;
Kay, Mark A;
Grompe, Markus

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2012, v. 20, n. 10, p. 1835, doi. 10.1038/mt.2012.199
Publication type:: Article

In Vivo Selection of Transplanted Hepatocytes by Pharmacological Inhibition of Fumarylacetoacetate Hydrolase in Wild-type Mice.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1981, doi. 10.1038/mt.2012.154

By:

Paulk, Nicole K;
Wursthorn, Karsten;
Haft, Annelise;
Pelz, Carl;
Clarke, Gregory;
Newell, Amy H;
Olson, Susan B;
Harding, Cary O;
Finegold, Milton J;
Bateman, Raymond L;
Witte, John F;
McClard, Ronald;
Grompe, Markus

Publication type:

Article

Balloon Catheter Delivery of Helper-dependent Adenoviral Vector Results in Sustained, Therapeutic hFIX Expression in Rhesus Macaques.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1863, doi. 10.1038/mt.2012.143

By:

Brunetti-Pierri, Nicola;
Liou, Aimee;
Patel, Priti;
Palmer, Donna;
Grove, Nathan;
Finegold, Milton;
Piccolo, Pasquale;
Donnachie, Elizabeth;
Rice, Karen;
Beaudet, Arthur;
Mullins, Charles;
Ng, Philip

Publication type:

Article

Valproic Acid Confers Functional Pluripotency to Human Amniotic Fluid Stem Cells in a Transgene-free Approach.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1953, doi. 10.1038/mt.2012.117

By:

Moschidou, Dafni;
Mukherjee, Sayandip;
Blundell, Michael P;
Drews, Katharina;
Jones, Gemma N;
Abdulrazzak, Hassan;
Nowakowska, Beata;
Phoolchund, Anju;
Lay, Kenneth;
Ramasamy, T Selvee;
Cananzi, Mara;
Nettersheim, Daniel;
Sullivan, Mark;
Frost, Jennifer;
Moore, Gudrun;
Vermeesch, Joris R;
Fisk, Nicholas M;
Thrasher, Adrian J;
Atala, Anthony;
Adjaye, James

Publication type:

Article

Retargeting Sleeping Beauty Transposon Insertions by Engineered Zinc Finger DNA-binding Domains.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1852, doi. 10.1038/mt.2012.126

By:

Voigt, Katrin;
Gogol-Döring, Andreas;
Miskey, Csaba;
Chen, Wei;
Cathomen, Toni;
Izsvák, Zsuzsanna;
Ivics, Zoltán

Publication type:

Article

Long-term Survival of the Juvenile Lethal Arginase-deficient Mouse With AAV Gene Therapy.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1844, doi. 10.1038/mt.2012.129

By:

Lee, Eun K.;
Hu, Chuhong;
Bhargava, Ragini;
Rozengurt, Nora;
Stout, David;
Grody, Wayne W;
Cederbaum, Stephen D;
Lipshutz, Gerald S

Publication type:

Article

Incorporation of the B18R Gene of Vaccinia Virus Into an Oncolytic Herpes Simplex Virus Improves Antitumor Activity.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1871, doi. 10.1038/mt.2012.113

By:

Fu, Xinping;
Rivera, Armando;
Tao, Lihua;
Zhang, Xiaoliu

Publication type:

Article

Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1968, doi. 10.1038/mt.2012.110

By:

van Til, Niek P;
de Boer, Helen;
Mashamba, Nomusa;
Wabik, Agnieszka;
Huston, Marshall;
Visser, Trudi P;
Fontana, Elena;
Poliani, Pietro Luigi;
Cassani, Barbara;
Zhang, Fang;
Thrasher, Adrian J;
Villa, Anna;
Wagemaker, Gerard

Publication type:

Article

Taking a Break From Huntingtin.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1838, doi. 10.1038/mt.2012.191

By:

Davidson, Beverly L

Publication type:

Article

Merits of Combination Cortical, Subcortical, and Cerebellar Injections for the Treatment of Niemann-Pick Disease Type A.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1893, doi. 10.1038/mt.2012.118

By:

Bu, Jie;
Ashe, Karen M;
Bringas, John;
Marshall, John;
Dodge, James C;
Cabrera-Salazar, Mario A;
Forsayeth, John;
Schuchman, Edward H;
Bankiewicz, Krystof S;
Cheng, Seng H;
Shihabuddin, Lamya S.;
Passini, Marco A

Publication type:

Article

Gene Therapy for Deaf Mice Goes Viral.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1836, doi. 10.1038/mt.2012.196

By:

Holt, Jeffrey R;
Vandenberghe, Luk H

Publication type:

Article

Pushing the Reset Button: Chemical-Induced Conversion of Amniotic Fluid Stem Cells Into a Pluripotent State.

Published in:

Molecular Therapy, 2012, v. 20, n. 10, p. 1839, doi. 10.1038/mt.2012.192

By:

Diecke, Sebastian;
Wu, Joseph C

Publication type:

Article