Works matching IS 15250016 AND DT 2011 AND VI 19 AND IP 11

Results: 24

A Double-modulation Strategy in Cancer Treatment With a Chemotherapeutic Agent and siRNA.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2040, doi. 10.1038/mt.2011.174

By:

Nakamura, Kazuya;
Abu Lila, Amr S;
Matsunaga, Mariko;
Doi, Yusuke;
Ishida, Tatsuhiro;
Kiwada, Hiroshi

Publication type:

Article

Retroviral Gene Therapy for X-linked Chronic Granulomatous Disease: Results From Phase I/II Trial.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2092, doi. 10.1038/mt.2011.166

By:

Kang, Hyoung Jin;
Bartholomae, Cynthia C;
Paruzynski, Anna;
Arens, Anne;
Kim, Sujeong;
Yu, Seung Shin;
Hong, Youngtae;
Joo, Chang-Wan;
Yoon, Nam-Kyung;
Rhim, Jung-Woo;
Kim, Joong Gon;
Von Kalle, Christof;
Schmidt, Manfred;
Kim, Sunyoung;
Ahn, Hyo Seop

Publication type:

Article

AAV Vector Biology in Primates: Finding the Missing Link?

Published in:

2011

By:

Herzog, Roland W;
Davidoff, Andrew M;
Markusic, David M;
Nathwani, Amit C

Publication type:

Editorial

N-acetylcysteine Enhances Cystic Fibrosis Sputum Penetration and Airway Gene Transfer by Highly Compacted DNA Nanoparticles.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1981, doi. 10.1038/mt.2011.160

By:

Suk, Jung Soo;
Boylan, Nicholas J;
Trehan, Kanika;
Tang, Benjamin C;
Schneider, Craig S;
Lin, Jung-Ming G;
Boyle, Michael P;
Zeitlin, Pamela L;
Lai, Samuel K;
Cooper, Mark J;
Hanes, Justin

Publication type:

Article

Intranasal Administration of Adeno-associated Virus Type 12 (AAV12) Leads to Transduction of the Nasal Epithelia and Can Initiate Transgene-specific Immune Response.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1990, doi. 10.1038/mt.2011.146

By:

Quinn, Kathrina;
Quirion, Mary R;
Lo, Chia-Yun;
Misplon, Julia A;
Epstein, Suzanne L;
Chiorini, John A

Publication type:

Article

Hepatorenal Correction in Murine Glycogen Storage Disease Type I With a Double-stranded Adeno-associated Virus Vector.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1961, doi. 10.1038/mt.2011.126

By:

Luo, Xiaoyan;
Hall, Gentzon;
Li, Songtao;
Bird, Andrew;
Lavin, Peter J;
Winn, Michelle P;
Kemper, Alex R;
Brown, Talmage T;
Koeberl, Dwight D

Publication type:

Article

RNA Interference Improves Myopathic Phenotypes in Mice Over-expressing FSHD Region Gene 1 (FRG1).

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2048, doi. 10.1038/mt.2011.118

By:

Wallace, Lindsay M;
Garwick-Coppens, Sara E;
Tupler, Rossella;
Harper, Scott Q

Publication type:

Article

A 10 Patient Case Report on the Impact of Plasmapheresis Upon Neutralizing Factors Against Adeno-associated Virus (AAV) Types 1, 2, 6, and 8.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2084, doi. 10.1038/mt.2011.108

By:

Monteilhet, Virginie;
Saheb, Samir;
Boutin, Sylvie;
Leborgne, Christian;
Veron, Philippe;
Montus, Marie-Françoise;
Moullier, Philippe;
Benveniste, Olivier;
Masurier, Carole

Publication type:

Article

Research Highlights.

Published in:: Molecular Therapy, 2011, v. 19, n. 11, p. 1927, doi. 10.1038/mt.2011.225
Publication type:: Article

Erythropoietin Gene-enhanced Marrow Mesenchymal Stromal Cells Decrease Cisplatin-induced Kidney Injury and Improve Survival of Allogeneic Mice.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2072, doi. 10.1038/mt.2011.162

By:

Eliopoulos, Nicoletta;
Zhao, Jing;
Forner, Kathy;
Birman, Elena;
Young, Yoon Kow;
Bouchentouf, Manaf

Publication type:

Article

AAV6-mediated Systemic shRNA Delivery Reverses Disease in a Mouse Model of Facioscapulohumeral Muscular Dystrophy.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2055, doi. 10.1038/mt.2011.153

By:

Bortolanza, Sergia;
Nonis, Alessandro;
Sanvito, Francesca;
Maciotta, Simona;
Sitia, Giovanni;
Wei, Jessica;
Torrente, Yvan;
Di Serio, Clelia;
Chamberlain, Joel R;
Gabellini, Davide

Publication type:

Article

An Intravenous Stimulus Package for Oncolytic Virotherapy.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1930, doi. 10.1038/mt.2011.217

By:

Vile, Richard;
Melcher, Alan

Publication type:

Article

Capsid-specific T-cell Responses to Natural Infections With Adeno-associated Viruses in Humans Differ From Those of Nonhuman Primates.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2021, doi. 10.1038/mt.2011.81

By:

Li, Hua;
Lasaro, Marcio O;
Jia, Bei;
Lin, Shih Wen;
Haut, Larissa H;
High, Katherine A;
Ertl, Hildegund CJ

Publication type:

Article

Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1950, doi. 10.1038/mt.2011.107

By:

Mattar, Citra NZ;
Nathwani, Amit C;
Waddington, Simon N;
Dighe, Niraja;
Kaeppel, Christine;
Nowrouzi, Ali;
Mcintosh, Jenny;
Johana, Nuryanti B;
Ogden, Bryan;
Fisk, Nicholas M;
Davidoff, Andrew M;
David, Anna;
Peebles, Donald;
Valentine, Marcus B;
Appelt, Jens-Uwe;
von Kalle, Christof;
Schmidt, Manfred;
Biswas, Arijit;
Choolani, Mahesh;
Chan, Jerry KY

Publication type:

Article

Insertion Sites in Engrafted Cells Cluster Within a Limited Repertoire of Genomic Areas After Gammaretroviral Vector Gene Therapy.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2031, doi. 10.1038/mt.2011.178

By:

Deichmann, Annette;
Brugman, Martijn H;
Bartholomae, Cynthia C;
Schwarzwaelder, Kerstin;
Verstegen, Monique MA;
Howe, Steven J;
Arens, Anne;
Ott, Marion G;
Hoelzer, Dieter;
Seger, Reinhard;
Grez, Manuel;
Hacein-Bey-Abina, Salima;
Cavazzana-Calvo, Marina;
Fischer, Alain;
Paruzynski, Anna;
Gabriel, Richard;
Glimm, Hanno;
Abel, Ulrich;
Cattoglio, Claudia;
Mavilio, Fulvio

Publication type:

Article

AAV8-mediated Hepatic Gene Transfer in Infant Rhesus Monkeys (Macaca mulatta).

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2012, doi. 10.1038/mt.2011.151

By:

Wang, Lili;
Bell, Peter;
Lin, Jianping;
Calcedo, Roberto;
Tarantal, Alice F;
Wilson, James M

Publication type:

Article

Corrigendum to 'Long-term Regulation of Genetically Modified Primary Hematopoietic Cells in Dogs'.

Published in:

2011

By:

Okazuka, Kiyoshi;
Beard, Brian C;
Emery, David W;
Schwarzwaelder, Kerstin;
Spector, Michele R;
Sale, George E;
von Kalle, Christof;
Torok-Storb, Beverly;
Kiem, Hans-Peter;
Blau, C Anthony

Publication type:

Correction Notice

New Generation of Plasmid Backbones Devoid of Antibiotic Resistance Marker for Gene Therapy Trials.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1942, doi. 10.1038/mt.2011.182

By:

Vandermeulen, Gaëlle;
Marie, Corinne;
Scherman, Daniel;
Préat, Véronique

Publication type:

Article

In This Issue.

Published in:: Molecular Therapy, 2011, v. 19, n. 11, p. 1926, doi. 10.1038/mt.2011.224
Publication type:: Article

Derivation of Insulin Producing Cells From Human Endometrial Stromal Stem Cells and Use in the Treatment of Murine Diabetes.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 2065, doi. 10.1038/mt.2011.173

By:

Santamaria, Xavier;
Massasa, Efi E;
Feng, Yuzhe;
Wolff, Erin;
Taylor, Hugh S

Publication type:

Article

Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1971, doi. 10.1038/mt.2011.157

By:

Bevan, Adam K;
Duque, Sandra;
Foust, Kevin D;
Morales, Pablo R;
Braun, Lyndsey;
Schmelzer, Leah;
Chan, Curtis M;
McCrate, Mary;
Chicoine, Louis G;
Coley, Brian D;
Porensky, Paul N;
Kolb, Stephen J;
Mendell, Jerry R;
Burghes, Arthur HM;
Kaspar, Brian K

Publication type:

Article

A Shift From Cell Cultures to Creatures: In Vivo Imaging of Small Animals in Experimental Regenerative Medicine.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1933, doi. 10.1038/mt.2011.194

By:

Studwell, Anna J;
Kotton, Darrell N

Publication type:

Article

Personalized Cell Transfer Immunotherapy for B-Cell Malignancies and Solid Cancers.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1928, doi. 10.1038/mt.2011.223

By:

Rosenberg, Steven A;
Kochenderfer, James N

Publication type:

Article

Systemic Administration of AAV8-α-galactosidase A Induces Humoral Tolerance in Nonhuman Primates Despite Low Hepatic Expression.

Published in:

Molecular Therapy, 2011, v. 19, n. 11, p. 1999, doi. 10.1038/mt.2011.119

By:

Nietupski, Jennifer B;
Hurlbut, Gregory D;
Ziegler, Robin J;
Chu, Qiuming;
Hodges, Bradley L;
Ashe, Karen M;
Bree, Mark;
Cheng, Seng H;
Gregory, Richard J;
Marshall, John;
Scheule, Ronald K

Publication type:

Article