Works matching IS 15250016 AND DT 2009 AND VI 17 AND IP 6


Results: 24
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    Lentiviral-mediated Genetic Correction of Hematopoietic and Mesenchymal Progenitor Cells From Fanconi Anemia Patients.

    Published in:
    Molecular Therapy, 2009, v. 17, n. 6, p. 1083, doi. 10.1038/mt.2009.26
    By:
    • Jacome, Ariana;
    • Navarro, Susana;
    • Río, Paula;
    • Yañez, Rosa M.;
    • González-Murillo, Africa;
    • Lozano, M. Luz;
    • Lamana, Maria Luisa;
    • Sevilla, Julian;
    • Olive, Teresa;
    • Diaz-Heredia, Cristina;
    • Badell, Isabel;
    • Estella, Jesus;
    • Madero, Luis;
    • Guenechea, Guillermo;
    • Casado, José;
    • Segovia, Jose C.;
    • Bueren, Juan A.
    Publication type:
    Article
    6

    Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models.

    Published in:
    Molecular Therapy, 2009, v. 17, n. 6, p. 1073, doi. 10.1038/mt.2009.31
    By:
    • Marangoni, Francesco;
    • Bosticardo, Marita;
    • Charrier, Sabine;
    • Draghici, Elena;
    • Locci, Michela;
    • Scaramuzza, Samantha;
    • Panaroni, Cristina;
    • Ponzoni, Maurilio;
    • Sanvito, Francesca;
    • Doglioni, Claudio;
    • Liabeuf, Marie;
    • Gjata, Bernard;
    • Montus, Marie;
    • Siminovitch, Katherine;
    • Aiuti, Alessandro;
    • Naldini, Luigi;
    • Dupré, Loïc;
    • Roncarolo, Maria Grazia;
    • Galy, Anne;
    • Villa, Anna
    Publication type:
    Article
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