Works matching IS 15250016 AND DT 2006 AND VI 13

Results: 1257

859. Cats Produce a CTL Response That Reduces Expression of Human Factor IX and Human Factor VIII after Neonatal Gene Transfer and Represent an Important Model for Translation into Humans.

Published in:

Molecular Therapy, 2006, v. 13, p. S331, doi. 10.1016/j.ymthe.2006.08.945

By:

Lingfei Xu;
Manxue Mei;
Haskins, Mark E.;
O'Donnell, Patty;
Cullen, Karyn;
Ponder, Katherine P.

Publication type:

Article

860. Sustained Long-Term In Vivo Expression of Human Factor IX from Keratinocytes Transduced with HIV-Based Vectors.

Published in:

Molecular Therapy, 2006, v. 13, p. S331, doi. 10.1016/j.ymthe.2006.08.946

By:

Escarti-Nebot, Angeles;
Serrano, Fernando;
del Rio, Marcela;
Larcher, Fernando;
Bernad, Antonio

Publication type:

Article

861. Recombinant Adeno-Associated Virus Vector Mediated Gene Therapy of Adenosine Deaminase Deficiency in a Mouse Model.

Published in:

Molecular Therapy, 2006, v. 13, p. S331, doi. 10.1016/j.ymthe.2006.08.947

By:

Crawford, Jennifer M.;
Teh-sheng Chan;
Chan, Lillian L.

Publication type:

Article

862. Feasibility of Cutaneous Gene Therapy Using a Factor VIII Gene and a Marker Gene in Factor VIII-Deficient Mice by Non-Invasive Electroporation.

Published in:

Molecular Therapy, 2006, v. 13, p. S332, doi. 10.1016/j.ymthe.2006.08.948

By:

Lei Zhang;
Goldbeck, Amy;
Hongbo Lu;
Nolan, Edward;
Rabussay, Dietmar;
Fakharzadeh, Steve

Publication type:

Article

863. Liver Gene Therapy for Hemophilia with phiC31 Integrase.

Published in:

Molecular Therapy, 2006, v. 13, p. S332, doi. 10.1016/j.ymthe.2006.08.949

By:

Woodard, Lauren E.;
Keravala, Annahita;
Hillman, Robert T.;
Sage, Julien;
Calos, Michele P.

Publication type:

Article

864. Characterization of Transgenic Mice Over-Expressing Arylsulfatase A: Implications for Gene Therapy and Sulfatases Activation Mechanisms.

Published in:

Molecular Therapy, 2006, v. 13, p. S332, doi. 10.1016/j.ymthe.2006.08.950

By:

Capotondo, Alessia;
Venneri, Mary A.;
Cosma, Maria P.;
Pallavicini, Isabella;
Ballabio, Andrea;
Naldini, Luigi;
Biffi, Alessandra

Publication type:

Article

865. In Vivo Gene Transfer of Prostacyclin Synthase by Using AAV Vector Prevents Monocrotaline-Induced Pulmonary Hypertension and Pulmonary Vasoconstriction in Rats.

Published in:

Molecular Therapy, 2006, v. 13, p. S333, doi. 10.1016/j.ymthe.2006.08.953

By:

Ito, Takayuki;
Okada, Takashi;
Mimuro, Jun;
Miyashita, Hiroshi;
Nonaka-Sarukawa, Mutsuko;
Mizukami, Hiroaki;
Kume, Akihiro;
Takahashi, Masafumi;
Yamamoto, Keiji;
Shimada, Kazuyuki;
Ozawa, Keiya

Publication type:

Article

866. Aortic Disease in Mucopolysaccharidodis I Mice Is Due to Increased Expression of Matrix Metalloproteinase 12 (MMP 12) Can Be Prevented with Neonatal Retroviral Vector-Mediated Gene Therapy.

Published in:

Molecular Therapy, 2006, v. 13, p. S333, doi. 10.1016/j.ymthe.2006.08.954

By:

Xiucui Ma;
Tittiger, Mindy;
Knutson, Russ;
Mecham, Robert;
Schaller, Laura;
Ponder, Katherine

Publication type:

Article

867. Spliceosome Mediated RNA Trans-Splicing To Increase Blood Levels of Apolipoprotein A-I and High Density Lipoproteins<sup>*</sup>.

Published in:

Molecular Therapy, 2006, v. 13, p. S334, doi. 10.1016/j.ymthe.2006.08.955

By:

Puttaraju, Madaiah;
Jun Wang;
Remaley, Alan T.;
Brewer, Jr., Bryan H.;
Garcia-Blanco, Mariano A.;
McGarrity, Gerard J.

Publication type:

Article

868. Novel Strategies To Inhibit Ocular Neovascularization Based on Sonic Hedgehog Pathway Blockade.

Published in:

Molecular Therapy, 2006, v. 13, p. S334, doi. 10.1016/j.ymthe.2006.08.956

By:

Cotugno, Gabriella;
Suace, Enrico M.;
Auricchio, Alberto

Publication type:

Article

869. Accelerated Re-Endothelilization in eNOS Transduced Iliac Artery Following Gene Delivery from an Adenoviral Eluting Stent.

Published in:

Molecular Therapy, 2006, v. 13, p. S334, doi. 10.1016/j.ymthe.2006.08.957

By:

Sharif, Faisal;
Hynes, Sean O.;
Crowley, James;
Daly, Kieran;
O'Brien, Timothy

Publication type:

Article

870. NOS Isoforms, Intimal Hyperplasia and Endothelial Regeneration after Balloon Injury.

Published in:

Molecular Therapy, 2006, v. 13, p. S335, doi. 10.1016/j.ymthe.2006.08.958

By:

Cooney, Ronan;
Hynes, Sean O.;
Faisal, Sharif;
O'Brien, Timothy

Publication type:

Article

871. Surface Modification of Adenovectors with TAT- and Antp-Containing Polymers Protects Them from Neutralizing Antibodies and Increases Expression of Reporter Genes In Vitro and In Vivo.

Published in:

Molecular Therapy, 2006, v. 13, p. S335, doi. 10.1016/j.ymthe.2006.08.959

By:

Fishbein, Ilia;
Alferiev, Ivan S.;
Gaster, Richard;
Lai, Meizan;
Levy, Robert J.

Publication type:

Article

872. Highly Efficient Virus-Mediated Gene Transfer to Human Vein Grafts Via Intraluminal Pressure Delivery.

Published in:

Molecular Therapy, 2006, v. 13, p. S335, doi. 10.1016/j.ymthe.2006.08.960

By:

Bernecker, Oliver Y.;
Stigler, Robert;
Semsroth, Severin;
Laufer, Guenther;
Bonatti, Johannes

Publication type:

Article

873. Development of High Throughput Functional Screening of Cardiovascular Therapeutic Genes Using the HVJ-E Vector.

Published in:

Molecular Therapy, 2006, v. 13, p. S336, doi. 10.1016/j.ymthe.2006.08.961

By:

Nishikawa, Tomoyuki;
Nakagami, Hironori;
Matsuki, Atsuhi;
Saito, Yukihiro;
Morishita, Ryuichi;
Tamai, Katsuto;
Kaneda, Yasufumi

Publication type:

Article

874. Prolonged Adenovirus and Adeno-Associated Virus-Mediated Gene Delivery to Rabbit Iliac Arteries Using Gene-Eluting Stents: A Direct Comparison.

Published in:

Molecular Therapy, 2006, v. 13, p. S336, doi. 10.1016/j.ymthe.2006.08.962

By:

Sharif, Faisal;
Hynes, Sean;
McMahon, Jill;
Crowley, James;
Daly, Kieran

Publication type:

Article

875. Development of Human Skin Gene Therapy for Systemic In Vivo Delivery of Atrial Natriuretic Peptide (ANP) To Treat Hypertension.

Published in:

Molecular Therapy, 2006, v. 13, p. S337, doi. 10.1016/j.ymthe.2006.08.963

By:

Therrien, Jean-Philippe;
Tock, Christine L.;
Vogel, Jonathan C.

Publication type:

Article

876. Development of Novel Angiogenic DNA Medicine Using a Genomic/cDNA Hybrid of Hepatocyte Growth Factor Gene.

Published in:

Molecular Therapy, 2006, v. 13, p. S337, doi. 10.1016/j.ymthe.2006.08.964

By:

Woong Hahn;
Dong-Sik Kim;
Wook-Bum Pyun;
Won-Sun Yoo;
Sun-young Kim;
Jong-Mook Kim

Publication type:

Article

877. Differential Expression of Indoleamine 2,3-dioxygenase (IDO) by Endothelial Cells and Its Overexpression by Gene Transfer: Implications for Cardiovascular Biology.

Published in:

Molecular Therapy, 2006, v. 13, p. S337, doi. 10.1016/j.ymthe.2006.08.965

By:

Tan, Peng H.;
George, Andrew J. T.

Publication type:

Article

878. Overexpression of Fibromodulin Inhibits Neointima Formation in Cultured Human Saphenous Veins.

Published in:

Molecular Therapy, 2006, v. 13, p. S338, doi. 10.1016/j.ymthe.2006.08.966

By:

Ranjzad, Parisa;
Salem, Husein K.;
Kingston, Paul A.

Publication type:

Article

879. Effects of Continuous Expression of Activated Protein C (APC) in Novel Murine Thrombosis Models.

Published in:

Molecular Therapy, 2006, v. 13, p. S338, doi. 10.1016/j.ymthe.2006.08.967

By:

Freguia, Christian Furlan;
Schuettrumpf, Joerg;
Baila, Stefano;
Jianhua Liu;
Bunte, Ralph;
Camire, Rodney M.;
Arruda, Valder R.

Publication type:

Article

880. Towards a Gene Therapy Treatment for Peripheral Vascular Disease – High Level of Expression of Angiogenic Genes in Rat Limb Muscle Following Intravenous Delivery of Plasmid DNAs.

Published in:

Molecular Therapy, 2006, v. 13, p. S339, doi. 10.1016/j.ymthe.2006.08.968

By:

Weijun Cheng;
Hegge, Julia O.;
Subbotin, Vladimir;
Coakley, Steven;
Hagstrom, James E.

Publication type:

Article

881. Safety, Efficacy and Biodistribution of Recombinant AAV2-RPE65 Vector Delivered by Ocular Subretinal Injection.

Published in:

Molecular Therapy, 2006, v. 13, p. S339, doi. 10.1016/j.ymthe.2006.08.970

By:

Jacobson, Samuel G.;
Acland, Gregory M.;
Aguirre, Gustavo D.;
Aleman, Tomas S.;
Boye, Sanford L.;
Schwartz, Sharon B.;
Cideciyan, Artur V.;
Zeiss, Caroline J.;
Komaromy, Andras M.;
Roman, Alejandro J.;
Windsor, Elizabeth A. M.;
Sumaroka, Alexander;
Pearce-Kelling, Susan E.;
Conlon, Thomas J.;
Quihong Li;
Chiodo, Vincent A.;
Flotte, Terence R.;
Maguire, Albert M.;
Bennett, Jean;
Hauswirth, William W.

Publication type:

Article

882. Non-Viral Ocular Gene Transfer for Hereditary Retinal Degeneration.

Published in:

Molecular Therapy, 2006, v. 13, p. S340, doi. 10.1016/j.ymthe.2006.08.971

By:

Naash, Muna I.;
Ballard, Ron M.;
Skaggs, Jeff;
Nash, Zack;
Quiambao, Alexander B.;
Cooper, Mark J.;
Farjo, Rafal

Publication type:

Article

883. AAV-2 Based Gene Therapy Using Novel Anti-VEGF Molecules for Inhibition of Angiogenesis in the Eye.

Published in:

Molecular Therapy, 2006, v. 13, p. S340, doi. 10.1016/j.ymthe.2006.08.972

By:

Scaria, Abraham;
Pechan, Peter;
Rubin, Hillard;
Lukason, Michael;
Barry, Elizabeth;
Ardinger, Jeffrey;
Huawei Qiu;
Qiuhong Li;
Peterson, James;
Hauswirth, William;
Wadsworth, Samuel

Publication type:

Article

884. Anti-Oxidant Gene Delivery to Retinal Epithelial Cells: A Gene Therapy Approach for Macular Degeneration.

Published in:

Molecular Therapy, 2006, v. 13, p. S340, doi. 10.1016/j.ymthe.2006.08.973

By:

McGinley, Lisa;
Cosgrave, Gillian;
Duffy, Aoife;
O'Brien, Timothy;
M. Strappe, Padraig

Publication type:

Article

885. AAV-Mediated Gene Transfer of Constitutively and Pharmacologically-Activated Glial Cell-Derived Neurotrophic Factor Receptor To Inhibit Retinal Degeneration.

Published in:

Molecular Therapy, 2006, v. 13, p. S341, doi. 10.1016/j.ymthe.2006.08.974

By:

Allocca, Mariacarmela;
Di Vicino, Umberto;
Domenici, Luciano;
Rivera, Victor M.;
Auricchio, Alberto

Publication type:

Article

886. AAV-Mediated Somatic Gene Transfer as an Approach To Delineate Pathogenic Mechanisms in an Autosomal Dominant Blindness Disorder Resembling Age-Related Macular Degeneration (AMD).

Published in:

Molecular Therapy, 2006, v. 13, p. S341, doi. 10.1016/j.ymthe.2006.08.975

By:

Keiser, Nicholas W.;
Maminishkis, Arvydas;
Bennicelli, Jeannette L.;
Miller, Sheldon S.;
Bennett, Jean

Publication type:

Article

887. G Protein-Coupled Receptor Kinase Interacting Protein 1 Slows down the Apoptosis Process of Retinal Ganglion Cells in a Rat Model.

Published in:

Molecular Therapy, 2006, v. 13, p. S341, doi. 10.1016/j.ymthe.2006.08.976

By:

Ann-Shung Lieu;
Yi Wang;
Webb, Donna;
Hankins, Gerold R.;
Helm, Gergory A.;
Jin Zhong Li

Publication type:

Article

888. Characterization of New Murine Models of Globoid Cell Leukodystrophy: Relevance for Gene Therapy Applications and Studies on Disease Pathogenesis.

Published in:

Molecular Therapy, 2006, v. 13, p. S342, doi. 10.1016/j.ymthe.2006.08.977

By:

Visigalli, Ilaria;
del Carro, Ubaldo;
Politi, Letterio;
Quattrini, Angelo;
Luzi, Paola;
Wenger, David;
Naldini, Luigi;
Biffi, Alessandra

Publication type:

Article

889. Adeno-Associated Virus Gene Therapy of Feline Gangliosidosis.

Published in:

Molecular Therapy, 2006, v. 13, p. S342, doi. 10.1016/j.ymthe.2006.08.978

By:

Martin, Douglas R.;
Cachon-Gonzalez, Begona;
Sena-Esteves, Miguel;
Hwang, Misako;
Gentry, Atoska S.;
Morrison, Nancy E.;
Cox, Nancy R.;
Cox, Timothy M.;
Baker, Henry J.

Publication type:

Article

890. Improvement of Behavior and Mortality Following CNS Administration of AAVrh.10hCLN2 to CLN2 −/− Mice, a Model LINCL (Battan Disease) a Fatal Childhood Neurological Disorder (Batten Disease).

Published in:

Molecular Therapy, 2006, v. 13, p. S343, doi. 10.1016/j.ymthe.2006.08.979

By:

Sondhi, Dolan;
Hackett, Neil R.;
Peterson, Daniel A.;
Vassallo, Elizabeth;
Stratton, Jamie A.;
Travis, Kelly;
O'Connor, Timothy P.;
Wilson, James M.;
Crystal, Ronald G.

Publication type:

Article

891. Correction of Established Neurologic Disease and Evidences of In Vivo Cross Correction in the Mouse Model of Metachromatic Leukodystrophy.

Published in:

Molecular Therapy, 2006, v. 13, p. S343, doi. 10.1016/j.ymthe.2006.08.980

By:

Biffi, Alessandra;
Capotondo, Alessia;
Fasano, Stefania;
del Carro, Ubaldo;
Marchesini, Sergio;
Azuma, Hisaya;
Brambilla, Riccardo;
Grompe, Markus;
Bordignon, Claudio;
Quattrini, Angelo;
Naldini, Luigi

Publication type:

Article

892. Neural Deficits Contribute to Respiratory Insufficiency in Pompe Disease: A Therapeutic Approach with AAV1.

Published in:

Molecular Therapy, 2006, v. 13, p. S344, doi. 10.1016/j.ymthe.2006.08.981

By:

DeRuisseau, Lara R.;
Mah, Cathryn;
Fuller, David D.;
Byrne, Barry J.

Publication type:

Article

893. Second Generation Gene Therapy Vector for Classical Late Infantile Neuronal Ceroid Lipofuscinosis.

Published in:

Molecular Therapy, 2006, v. 13, p. S344, doi. 10.1016/j.ymthe.2006.08.982

By:

Cabrera-Salazar, Mario A.;
Hodges, Bradley L.;
Yew, Nelson S.;
Jie Bu;
Fidler, Jonathan A.;
Roskelley, Eric M.;
Scheule, Ronald K.;
Sleat, David E.;
Lobel, Peter;
Cheng, Seng H.;
Passini, Marco A.

Publication type:

Article

894. Selective Targeting of GABAergic Neurons Using rAAV: The Potential Role of EAAC1 in Seizure Susceptibility.

Published in:

Molecular Therapy, 2006, v. 13, p. S344, doi. 10.1016/j.ymthe.2006.08.983

By:

Weller, Melodie L.;
Maki, Christopher J.;
Stone, Ida M.;
Poulsen, David J.

Publication type:

Article

895. Separate rAAV1 Vectors Co-Infect Striatal Neurons Efficiently.

Published in:

Molecular Therapy, 2006, v. 13, p. S345, doi. 10.1016/j.ymthe.2006.08.984

By:

Manfredsson, Fredric P.;
Rising, Aaron C.;
Mandel, Ronald J.

Publication type:

Article

896. Long Term Transgene Expression in the Brain Delivered by SV40-Derived Vectors.

Published in:

Molecular Therapy, 2006, v. 13, p. S345, doi. 10.1016/j.ymthe.2006.08.985

By:

Louboutin, Jean-Pierre;
Reyes, Beverly A. S.;
Agrawal, Lokesh;
van Bockstaele, Elisabeth J.;
Strayer, David S.

Publication type:

Article

897. Na,K-ATPase β1-Mediated Selective Gene Transfer into Neurons.

Published in:

Molecular Therapy, 2006, v. 13, p. S346, doi. 10.1016/j.ymthe.2006.08.986

By:

Ishii, Keiji;
Nakamura, Kiminori;
Kawaguchi, Satoshi;
Rong Li;
Hirai, Sachie;
Sakuragi, Naoya;
Wada, Takuro;
Kato, Kazunori;
Yamashita, Toshihiko;
Hamada, Hirofumi

Publication type:

Article

898. Intracerebral Exon Skipping Restores Dystrophin Expression in CA1 Pyramidal Neurons of mdx Mice.

Published in:

Molecular Therapy, 2006, v. 13, p. S346, doi. 10.1016/j.ymthe.2006.08.987

By:

Peltekian, Elise;
Ros, Karine;
Goyenvalle, Aurelie;
Gruszczynski, Carole;
Vaillend, Cyrille;
Laroche, Serge;
Garcia, Luis;
Danos, Olivier

Publication type:

Article

899. Utilizing the Vector Transport Properties of AAV-9 as a Method To Get Widespread Distribution of a Therapeutic Gene within the CNS.

Published in:

Molecular Therapy, 2006, v. 13, p. S346, doi. 10.1016/j.ymthe.2006.08.988

By:

Cearley, Cassia N.;
Wolfe, John H.

Publication type:

Article

900. Specific AAV Serotypes Stably Transduce Hippocampal and Cortical Cultures with High Efficiency and Low Toxicity.

Published in:

Molecular Therapy, 2006, v. 13, p. S347, doi. 10.1016/j.ymthe.2006.08.989

By:

Royo, Nicolas C.;
Vandenberghe, Luk H.;
Johnston, Julie;
Maronski, Margaret;
Dichter, Marc A.;
Wilson, James M.;
Watson, Deborah J.

Publication type:

Article

901. Targeting of Viral Vectors to Motor Neurons by Botulinum Toxin Binding Domain To Treat ALS.

Published in:

Molecular Therapy, 2006, v. 13, p. S347, doi. 10.1016/j.ymthe.2006.08.990

By:

Yang Lu;
Adams, Robert;
Wenji Sun;
Lee, Iris;
Debromilskaya, Irina;
Drachman, Daniel B.

Publication type:

Article

902. Modulation of Voltage-Gated Potassium Channels in Dorsal Root Ganglion Neurons by an Inducible Adenoviral Vector In Vivo.

Published in:

Molecular Therapy, 2006, v. 13, p. S347, doi. 10.1016/j.ymthe.2006.08.991

By:

Chao Ma;
LaMotte, Robert H.;
Rosenzweig, Jason M.;
Gehlbach, Peter L.;
Johns, David C.

Publication type:

Article

903. Re-Administration of Recombinant AAV2 and AAV5 in the Brain.

Published in:

Molecular Therapy, 2006, v. 13, p. S348, doi. 10.1016/j.ymthe.2006.08.992

By:

Reimsnider, Sharon K.;
Manfredsson, Fredric P.;
Burger, Corinna;
Muzczyka, Nicholas;
Mandel, Ronald J.

Publication type:

Article

904. The Systemic Human Immune Response to Intraparenchymal Administration of AAV.

Published in:

Molecular Therapy, 2006, v. 13, p. S348, doi. 10.1016/j.ymthe.2006.08.993

By:

McPhee, Scott W. J.;
Janson, Chris G.;
Chengwen Li;
Samulski, R. Jude;
Camp, Angelique S.;
Francis, Jeremy S.;
Shera, David;
Freese, Andrew;
Aita, Anthony L.;
Goldman, H. Warren;
Leone, Paola

Publication type:

Article

905. The Use of Gene Immunisation To Study the Role of Antibodies to Voltage Gated Potassium Channels in Neuroimmunological Disease.

Published in:

Molecular Therapy, 2006, v. 13, p. S349, doi. 10.1016/j.ymthe.2006.08.994

By:

McMenamin, Mary;
McKnight, Karen M.;
Wood, Matthew J. A.;
Lang, Bethan;
Horwood, Nikki J.;
Vincent, Angela C.

Publication type:

Article

906. Effective Repetitive Dystrophin Gene Transfer into Skeletal Muscle of Adult mdx Mice Using a Helper-Dependent Adenovirus Vector Expressing the Coxsackievirus and Adenovirus Receptor (CAR) and Dystrophin.

Published in:

Molecular Therapy, 2006, v. 13, p. S349, doi. 10.1016/j.ymthe.2006.08.996

By:

Uchida, Yuji;
Maeda, Yasushi;
Kimura, En;
Uchino, Makoto

Publication type:

Article

907. Development of Recombinant Novel Adeno-Associated Viral (rAAV) Vectors Encoding Optimised Microdystrophin cDNAs for Duchenne Muscular Dystrophy (DMD).

Published in:

Molecular Therapy, 2006, v. 13, p. S349, doi. 10.1016/j.ymthe.2006.08.997

By:

Athanasopoulos, Takis;
Graham, Ian;
Trollet, Capucine;
Foster, Helen;
Perez, Norma;
Hill, Vanessa;
Moullier, Phillippe;
Dickson, George

Publication type:

Article

908. Design and Optimization of U7snRNAs for Skipping of Exon 51 in DMD: Promising Tools for Future Clinical Trials.

Published in:

Molecular Therapy, 2006, v. 13, p. S350, doi. 10.1016/j.ymthe.2006.08.998

By:

Goyenvalle, Aurelie;
Vulin, Adeline;
Lorain, Stephanie;
Aartsma-Rus, Annemieke;
van Deutekom, Judith C. T.;
Danos, Olivier;
Garcia, Luis

Publication type:

Article