Works matching IS 13518216 AND DT 2025 AND VI 31


Results: 53
    1

    Author Index.

    Published in:
    Haemophilia, 2025, v. 31, p. 110, doi. 10.1111/hae.70058
    Publication type:
    Article
    2

    Issue Information.

    Published in:
    Haemophilia, 2025, v. 31, p. 1, doi. 10.1111/hae.15043
    Publication type:
    Article
    3

    Book of Abstracts.

    Published in:
    Haemophilia, 2025, v. 31, p. 21, doi. 10.1111/hae.70032
    Publication type:
    Article
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    Impact of Systematic Joint Examination (Ultrasound, Functional and Physical) on Treatment Management Decisions in Patients With Haemophilia A in France: Final Data From the Prospective, Observational A‐MOVE Study.

    Published in:
    Haemophilia, 2025, v. 31, n. 2, p. 239, doi. 10.1111/hae.70012
    By:
    • Drillaud, Nicolas;
    • Barbay, Virginie;
    • Valentin, Jean Baptiste;
    • Jailler, Romain;
    • Lebreton, Aurélien;
    • Pan‐Petesch, Brigitte;
    • Marie Castet, Sabine;
    • Frotscher, Birgit;
    • Frenzel, Laurent;
    • Jousse‐Joulin, Sandrine;
    • Chambost, Hervé;
    • Alenäs, Mikaela;
    • Fusser, Markus;
    • Gandossi, Corinne;
    • Zidi, Meriem;
    • Mahdout, Oussama;
    • Repessé, Yohann;
    • d'Oiron, Roseline;
    • Oudot, Caroline;
    • Genre‐Volot, Fabienne
    Publication type:
    Article
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    Operationalising a Haemophilia Gene Editing Lexicon for Practical Use.

    Published in:
    Haemophilia, 2025, v. 31, n. 2, p. 207, doi. 10.1111/hae.15155
    By:
    • McKeown, William;
    • Hermans, Cedric;
    • Unzu, Carmen;
    • Kay, Mark A.;
    • Peyvandi, Flora;
    • Smith, Penni;
    • Miesbach, Wolfgang;
    • Pierce, Glenn F.;
    • Khair, Kate;
    • Valentino, Leonard A.;
    • Pipe, Steven W.;
    • Pillai, Monisha;
    • Jones, Micheala;
    • Delwart, Virginie;
    • Sindhurakar, Anil;
    • Gutstein, David E.;
    • Kessler, Craig M.
    Publication type:
    Article
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    Pharmacokinetic Studies, Assessing the Efficiency of FVIII/VWF Concentrates and Intravenous Human Immunoglobulin, Revealed the Etiopathogenesis of Acquired von Willebrand Disease in Patient With MGUS.

    Published in:
    Haemophilia, 2025, v. 31, n. 2, p. 340, doi. 10.1111/hae.15137
    By:
    • Miele, Ciro;
    • D'Auria, Francesca;
    • Manfredi, Luca;
    • Conca, Paolo;
    • Cimino, Ernesto;
    • Mormile, Rosaria;
    • De Simone, Sabrina;
    • Scudiero, Olga;
    • Savoia, Marcella;
    • Tufano, Antonella;
    • Di Minno, Matteo Nicola Dario;
    • Capasso, Filomena;
    • Mazzaccara, Cristina
    Publication type:
    Article
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    Issue Information.

    Published in:
    Haemophilia, 2025, v. 31, n. 2, p. 169, doi. 10.1111/hae.15045
    Publication type:
    Article
    29

    Author Index.

    Published in:
    Haemophilia, 2025, v. 31, p. 230, doi. 10.1111/hae.15158
    Publication type:
    Article
    30

    Issue Information.

    Published in:
    Haemophilia, 2025, v. 31, p. 1, doi. 10.1111/hae.15157
    Publication type:
    Article
    31

    Committee List.

    Published in:
    Haemophilia, 2025, v. 31, p. 3, doi. 10.1111/hae.15152
    Publication type:
    Article
    32

    Abstract.

    Published in:
    Haemophilia, 2025, v. 31, p. 4, doi. 10.1111/hae.15148
    Publication type:
    Article
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    Mortality in Haemophilia Patients in India: A National Cohort Study.

    Published in:
    Haemophilia, 2025, v. 31, n. 1, p. 132, doi. 10.1111/hae.15143
    By:
    • Shetty, Shrimati;
    • Ross, Cecil;
    • John, M. Joseph;
    • Kshirsagar, Shrinath;
    • Kulkarni, Nimish;
    • Pavitra, D. S.;
    • Sarwan, Diksha;
    • Misha, P. K.;
    • Paul, Antony;
    • More, Apurva;
    • Kaunchale, Nazish;
    • D'silva, Magdalene;
    • Masurkar, Shrushti;
    • Kharat, Shruti;
    • Patil, Kranti;
    • Patel, Shalaka;
    • Mehendale, Priti;
    • Sarvaiya, Prachi;
    • Rangarajan, Savita
    Publication type:
    Article
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    A phase 1/2 safety and efficacy study of TAK‐754 gene therapy: The challenge of achieving durable factor VIII expression in haemophilia A clinical trials.

    Published in:
    Haemophilia, 2025, v. 31, n. 1, p. 108, doi. 10.1111/hae.15121
    By:
    • Chapin, John;
    • Álvarez Román, Maria Teresa;
    • Ayash‐Rashkovsky, Mila;
    • Diogo, Dorothee;
    • Kenniston, Jon;
    • Lopez‐Jaime, Francisco‐Jose;
    • Maggiore, Caterina;
    • Mingot‐Castellano, María‐Eva;
    • Rajavel, Kavitha;
    • Rauch, Antoine;
    • Susen, Sophie;
    • von Grotthuss, Marcin;
    • Wagoner, Matt;
    • Wang, Qin
    Publication type:
    Article
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