Works matching IS 13518216 AND DT 2020 AND VI 26 AND IP 3


Results: 40
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    PROTECT VIII Kids: BAY 94‐9027 (PEGylated Recombinant Factor VIII) safety and efficacy in previously treated children with severe haemophilia A.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. e55, doi. 10.1111/hae.13963
    By:
    • Santagostino, Elena;
    • Kenet, Gili;
    • Fischer, Kathelijn;
    • Biss, Tina;
    • Ahuja, Sanjay;
    • Steele, MacGregor;
    • Martínez, M.;
    • Male, C.;
    • van Geet, C.;
    • Mondelaers, V.;
    • Kaleva, V.;
    • Stoyanova‐Deleva, A.;
    • Bobev, D.;
    • Blanchette, V.;
    • Zanon, E.;
    • Gagliano, F.;
    • Rageliene, L.;
    • Peters, M.;
    • Mlynarski, W.;
    • Badowska, W.
    Publication type:
    Article
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    Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. 443, doi. 10.1111/hae.13971
    By:
    • Pierce, Glenn F.;
    • Pasi, K. John;
    • Coffin, Donna;
    • Kaczmarek, Radoslaw;
    • Lillicrap, David;
    • Mahlangu, Johnny;
    • Rottellini, Dawn;
    • Sannié, Thomas;
    • Srivastava, Alok;
    • VandenDriessche, Thierry;
    • Weill, Alain;
    • Almeida, Antonio J.;
    • Baumann, Alain;
    • Brooker, Mark;
    • Durante, Luisa;
    • Naccache, Mayss;
    • Robinson, Fiona
    Publication type:
    Article
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    Witnessing the 1980s.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. 373, doi. 10.1111/hae.13968
    By:
    • Mannucci, Pier Mannuccio
    Publication type:
    Article
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    Issue Information.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. 175, doi. 10.1111/hae.13792
    Publication type:
    Article
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    North‐eastern Brazilian recommendations for the nurse professional role on the pharmacokinetic‐assisted prophylaxis individualization for haemophilia A.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. e120, doi. 10.1111/hae.13934
    By:
    • Morais Costa, Neuza Cavalcanti;
    • Costa, Íris Maciel;
    • Guimarães, Tânia Maria Rocha;
    • Souza, Hioga Pimentel;
    • Casaretto, Edilma Silva;
    • Medeiros, Tenille Capuxú;
    • Barbosa, Stella Maia;
    • Matos, Antônia Irineuma Esteves Lopes;
    • Oliveira, Evoneide Gomes;
    • Camelo, Ricardo Mesquita
    Publication type:
    Article