Works matching IS 09646906 AND DT 2011 AND VI 20 AND IP R1

Results: 18

The Sleeping Beauty transposon system: a non-viral vector for gene therapy.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R14, doi. 10.1093/hmg/ddr140

By:

Aronovich, Elena L.;
McIvor, R. Scott;
Hackett, Perry B.

Publication type:

Article

Combination therapies for lysosomal storage disease: is the whole greater than the sum of its parts?

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R54, doi. 10.1093/hmg/ddr112

By:

Hawkins-Salsbury, Jacqueline A.;
Reddy, Adarsh S.;
Sands, Mark S.

Publication type:

Article

Genetic therapies for cystic fibrosis lung disease.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R79, doi. 10.1093/hmg/ddr104

By:

Sinn, Patrick L.;
Anthony, Reshma M.;
McCray, Paul B.

Publication type:

Article

Gene therapy for leukodystrophies.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R42, doi. 10.1093/hmg/ddr142

By:

Biffi, Alessandra;
Aubourg, Patrick;
Cartier, Nathalie

Publication type:

Article

RNAi medicine for the brain: progresses and challenges.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R21, doi. 10.1093/hmg/ddr137

By:

Boudreau, Ryan L.;
Rodríguez-Lebrón, Edgardo;
Davidson, Beverly L.

Publication type:

Article

Genetic therapy for the nervous system.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R28, doi. 10.1093/hmg/ddr110

By:

Bowers, William J.;
Breakefield, Xandra O.;
Sena-Esteves, Miguel

Publication type:

Article

Ex vivo gene transfer for improved adoptive immunotherapy of cancer.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R93, doi. 10.1093/hmg/ddr102

By:

Ngo, Minhtran C.;
Rooney, Cliona M.;
Howard, Jeffrey M.;
Heslop, Helen E.

Publication type:

Article

Ex vivo gene therapy for HIV-1 treatment.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R100, doi. 10.1093/hmg/ddr160

By:

Scherer, Lisa J.;
Rossi, John J.

Publication type:

Article

Cover Page.

Published in:: Human Molecular Genetics, 2011, v. 20, n. R1, p. NP, doi. 10.1093/hmg/ddr219
Publication type:: Article

Large-scale recombinant adeno-associated virus production.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R2, doi. 10.1093/hmg/ddr141

By:

Kotin, Robert M.

Publication type:

Article

Subscription Page.

Published in:: Human Molecular Genetics, 2011, v. 20, n. R1, p. NP, doi. 10.1093/hmg/ddr222
Publication type:: Article

Gene Therapy Grows into Young Adulthood: Special Review Issue.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R1, doi. 10.1093/hmg/ddr188

By:

Lee, Brendan;
Davidson, Beverly L.

Publication type:

Article

Editorial Board.

Published in:: Human Molecular Genetics, 2011, v. 20, n. R1, p. NP, doi. 10.1093/hmg/ddr221
Publication type:: Article

Gene therapy for alpha-1 antitrypsin deficiency.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R87, doi. 10.1093/hmg/ddr156

By:

Flotte, Terence R.;
Mueller, Christian

Publication type:

Article

Pompe disease gene therapy.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R61, doi. 10.1093/hmg/ddr174

By:

Byrne, Barry J.;
Falk, Darin J.;
Pacak, Christina A.;
Nayak, Sushrusha;
Herzog, Roland W.;
Elder, Melissa E.;
Collins, Shelley W.;
Conlon, Thomas J.;
Clement, Nathalie;
Cleaver, Brian D.;
Cloutier, Denise A.;
Porvasnik, Stacy L.;
Islam, Saleem;
Elmallah, Mai K.;
Martin, Anatole;
Smith, Barbara K.;
Fuller, David D.;
Lawson, Lee Ann;
Mah, Cathryn S.

Publication type:

Article

Helper-dependent adenoviral vectors for liver-directed gene therapy.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R7, doi. 10.1093/hmg/ddr143

By:

Brunetti-Pierri, Nicola;
Ng, Philip

Publication type:

Article

Contents Page.

Published in:: Human Molecular Genetics, 2011, v. 20, n. R1, p. NP, doi. 10.1093/hmg/ddr220
Publication type:: Article

Therapeutic approaches to muscular dystrophy.

Published in:

Human Molecular Genetics, 2011, v. 20, n. R1, p. R69, doi. 10.1093/hmg/ddr105

By:

Goyenvalle, Aurélie;
Seto, Jane T.;
Davies, Kay E.;
Chamberlain, Jeffrey

Publication type:

Article