Works matching Genetic disorder treatment

Results: 993
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    Gold Nanoparticle-Mediated Gene Therapy.

    Published in:
    Cancers, 2022, v. 14, n. 21, p. 5366, doi. 10.3390/cancers14215366
    By:
    • Kanu, Gayathri A.;
    • Parambath, Javad B. M.;
    • Abu Odeh, Raed O.;
    • Mohamed, Ahmed A.
    Publication type:
    Article
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    HotSpots.

    Published in:
    Clinical Genetics, 2001, v. 60, n. 2, p. 102, doi. 10.1034/j.1399-0004.2001.6002023.x
    By:
    • Devon, Rebecca S;
    • Chopra, Vikramjit;
    • van Raamsdonk, Jeremy M
    Publication type:
    Article
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    In vivo genome editing restores haemostasis in a mouse model of haemophilia.

    Published in:
    Nature, 2011, v. 475, n. 7355, p. 217, doi. 10.1038/nature10177
    By:
    • Hojun Li;
    • Haurigot, Virginia;
    • Doyon, Yannick;
    • Tianjian Li;
    • Wong, Sunnie Y.;
    • Bhagwat, Anand S.;
    • Malani, Nirav;
    • Anguela, Xavier M.;
    • Sharma, Rajiv;
    • Ivanciu, Lacramiora;
    • Murphy, Samuel L.;
    • Finn, Jonathan D.;
    • Khazi, Fayaz R.;
    • Shangzhen Zhou;
    • Paschon, David E.;
    • Rebar, Edward J.;
    • Bushman, Frederic D.;
    • Gregory, Philip D.;
    • Holmes, Michael C.;
    • High, Katherine A.
    Publication type:
    Article
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    Human genetics in health care.

    Published in:
    European Journal of Pediatrics, 2000, v. 159, n. 15, p. S170, doi. 10.1007/PL00014397
    By:
    • van Ommen, Gert-Jan B.
    Publication type:
    Article
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