Works matching Gene therapy


Results: 5000
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    Viral Vectors in Gene Replacement Therapy.

    Published in:
    Biochemistry (00062979), 2023, v. 88, n. 12/13, p. 2157, doi. 10.1134/S0006297923120179
    By:
    • Minskaia, Ekaterina;
    • Galieva, Alima;
    • Egorov, Alexander D.;
    • Ivanov, Roman;
    • Karabelsky, Alexander
    Publication type:
    Article
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    Gene therapy for the treatment of pituitary tumors.

    Published in:
    Expert Review of Endocrinology & Metabolism, 2009, v. 4, n. 4, p. 359, doi. 10.1586/EEM.09.16
    By:
    • Rodriguez, Silvia S.;
    • Castro, Maria G.;
    • Brown, Oscar A.;
    • Goya, Rodolfo G.;
    • Console, Gloria M.
    Publication type:
    Article
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    An Update on Gene Therapy for Inherited Retinal Dystrophy: Experience in Leber Congenital Amaurosis Clinical Trials.

    Published in:
    International Journal of Molecular Sciences, 2021, v. 22, n. 9, p. 4534, doi. 10.3390/ijms22094534
    By:
    • Chiu, Wei;
    • Lin, Ting-Yi;
    • Chang, Yun-Chia;
    • Isahwan-Ahmad Mulyadi Lai, Henkie;
    • Lin, Shen-Che;
    • Ma, Chun;
    • Yarmishyn, Aliaksandr A.;
    • Lin, Shiuan-Chen;
    • Chang, Kao-Jung;
    • Chou, Yu-Bai;
    • Hsu, Chih-Chien;
    • Lin, Tai-Chi;
    • Chen, Shih-Jen;
    • Chien, Yueh;
    • Yang, Yi-Ping;
    • Hwang, De-Kuang;
    • Joachim, Stephanie C.
    Publication type:
    Article
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    Ocular Gene Therapy: A Literature Review with Special Focus on Immune and Inflammatory Responses.

    Published in:
    Clinical Ophthalmology, 2022, v. 16, p. 1753, doi. 10.2147/OPTH.S364200
    By:
    • Ghoraba, Hashem H;
    • Akhavanrezayat, Amir;
    • Karaca, Irmak;
    • Yavari, Negin;
    • Lajevardi, Sherin;
    • Hwang, Jaclyn;
    • Regenold, Jonathan;
    • Matsumiya, Wataru;
    • Pham, Brandon;
    • Zaidi, Moosa;
    • Mobasserian, Azadeh;
    • DongChau, Anthony Toan;
    • Or, Christopher;
    • Yasar, Cigdem;
    • Mishra, Kapil;
    • Do, Diana;
    • Nguyen, Quan Dong
    Publication type:
    Article
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    Gene therapy and its applications.

    Published in:
    Journal of Medical Evidence, 2023, v. 4, n. 1, p. 46, doi. 10.4103/JME.JME_65_21
    By:
    • Bansal, Alka;
    • Prakash, Ravi;
    • Agarwal, Swati;
    • Advani, Uma
    Publication type:
    Article
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    Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.

    Published in:
    Haemophilia, 2020, v. 26, n. 3, p. 443, doi. 10.1111/hae.13971
    By:
    • Pierce, Glenn F.;
    • Pasi, K. John;
    • Coffin, Donna;
    • Kaczmarek, Radoslaw;
    • Lillicrap, David;
    • Mahlangu, Johnny;
    • Rottellini, Dawn;
    • Sannié, Thomas;
    • Srivastava, Alok;
    • VandenDriessche, Thierry;
    • Weill, Alain;
    • Almeida, Antonio J.;
    • Baumann, Alain;
    • Brooker, Mark;
    • Durante, Luisa;
    • Naccache, Mayss;
    • Robinson, Fiona
    Publication type:
    Article
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    The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the world.

    Published in:
    Haemophilia, 2019, v. 25, n. 2, p. 189, doi. 10.1111/hae.13673
    By:
    • Pierce, Glenn F.;
    • Coffin, Donna;
    • Lillicrap, David;
    • Ozelo, Margareth;
    • Pasi, John;
    • Rotellini, Dawn;
    • Marquez, Safadi;
    • Sannié, Thomas;
    • Srivastava, Alok;
    • Berg, Marijke;
    • Weill, Alain;
    • Almeida, Antonio;
    • Baumann, Alain;
    • Brooker, Mark;
    • Durante, Luisa;
    • Naccache, Mayss;
    • Robinson, Fiona;
    • Bagley, Lisa;
    • Chapin, John;
    • Diop, Saliou
    Publication type:
    Article
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    Nanoparticles for death-induced gene therapy in cancer (Review).

    Published in:
    Molecular Medicine Reports, 2018, v. 17, n. 1, p. 1413, doi. 10.3892/mmr.2017.8091
    By:
    • Roacho-Perez, Jorge A.;
    • Gallardo-Blanco, Hugo L.;
    • Sanchez-Dominguez, Margarita;
    • Garcia-Casillas, Perla E.;
    • Chapa-Gonzalez, Christian;
    • Sanchez-Dominguez, Celia N.
    Publication type:
    Article
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    Gene therapy for renal diseases.

    Published in:
    Kidney International Supplement, 1997, n. 61, p. S-85, doi. 10.1111/1523-1755.ep17695596
    By:
    • Lien, Yeong-Hau H.;
    • Li-Wen Lai
    Publication type:
    Article
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