Works about TREATMENT of Duchenne muscular dystrophy

Results: 262

Therapy Taping® Method: New Therapeutic Approach for Wheelchair Children with Duchenne Muscular Dystrophy.

Published in:

Journal of Health Sciences (2447-8938), 2019, v. 21, p. 313, doi. 10.17921/2447-8938.2019v21n3

By:

C., Iwabe;
C. D., Sanches;
Junior N., Morini;
A. L., Pinto

Publication type:

Article

Zidovudine ameliorates pathology in the mouse model of Duchenne muscular dystrophy via P2RX7 purinoceptor antagonism.

Published in:

Acta Neuropathologica Communications, 2018, v. 6, n. 1, p. N.PAG, doi. 10.1186/s40478-018-0530-4

By:

Al-Khalidi, Rasha;
Panicucci, Chiara;
Cox, Paul;
Chira, Natalia;
Róg, Justyna;
Young, Christopher N. J.;
McGeehan, Rhiannon E.;
Ambati, Kameshwari;
Ambati, Jayakrishna;
Zabłocki, Krzysztof;
Gazzerro, Elisabetta;
Arkle, Stephen;
Bruno, Claudio;
Górecki, Dariusz C.

Publication type:

Article

DMD Open‐access Variant Explorer (DOVE): A scalable, open‐access, web‐based tool to aid in clinical interpretation of genetic variants in the DMD gene.

Published in:

Molecular Genetics & Genomic Medicine, 2019, v. 7, n. 1, p. N.PAG, doi. 10.1002/mgg3.510

By:

Bailey, Mitchell;
Miller, Nicole

Publication type:

Article

Biochemical Changes in Blood of Patients with Duchenne Muscular Dystrophy Treated with Granulocyte-Colony Stimulating Factor.

Published in:

BioMed Research International, 2019, p. 1, doi. 10.1155/2019/4789101

By:

Sienkiewicz, Dorota;
Kułak, Wojciech;
Paszko-Patej, Grażyna;
Okurowska-Zawada, Bożena;
Sienkiewicz, Jerzy;
Kułak, Piotr

Publication type:

Article

Drug Repurposing for Duchenne Muscular Dystrophy: The Monoamine Oxidase B Inhibitor Safinamide Ameliorates the Pathological Phenotype in mdx Mice and in Myogenic Cultures From DMD Patients.

Published in:

Frontiers in Physiology, 2018, p. 1, doi. 10.3389/fphys.2018.01087

By:

Vitiello, Libero;
Marabita, Manuela;
Sorato, Elisa;
Nogara, Leonardo;
Forestan, Giada;
Mouly, Vincent;
Salviati, Leonardo;
Acosta, Manuel;
Blaauw, Bert;
Canton, Marcella

Publication type:

Article

The extraocular muscle stem cell niche is resistant to ageing and disease.

Published in:

Frontiers in Aging Neuroscience, 2014, v. 6, p. 1, doi. 10.3389/fnagi.2014.00328

By:

Formicola, Luigi;
Marazzi, Giovanna;
Sassoon, David A.

Publication type:

Article

Careful pre-anesthetic evaluation leading to a successful anesthetic management of an undiagnosed Duchenne muscular dystrophy child.

Published in:

2015

By:

P., Vogiatzaki;
P., Chloropoulou;
C., Iatrou

Publication type:

Letter to the Editor

Epigenetic Reprogramming of Muscle Progenitors: Inspiration for Clinical Therapies.

Published in:

Thrombosis, 2015, p. 1, doi. 10.1155/2016/6093601

By:

Consalvi, Silvia;
Sandoná, Martina;
Saccone, Valentina

Publication type:

Article

Fracture in Duchenne Muscular Dystrophy.

Published in:

Journal of Child Neurology, 2016, v. 31, n. 9, p. 1181, doi. 10.1177/0883073816650034

By:

Perera, Nadia;
Sampaio, Hugo;
Woodhead, Helen;
Farrar, Michelle

Publication type:

Article

Corticosteroids in Duchenne Muscular Dystrophy: A Reappraisal.

Published in:

Journal of Child Neurology, 2002, v. 17, n. 3, p. 183, doi. 10.1177/088307380201700306

By:

Wong, Brenda L.Y.;
Christopher, Caroline

Publication type:

Article

Naproxcinod shows significant advantages over naproxen in the mdx model of Duchenne Muscular Dystrophy.

Published in:

Orphanet Journal of Rare Diseases, 2015, v. 10, n. 1, p. 1, doi. 10.1186/s13023-015-0311-0

By:

Miglietta, Daniela;
De Palma, Clara;
Sciorati, Clara;
Vergani, Barbara;
Pisa, Viviana;
Villa, Antonello;
Ongini, Ennio;
Clementi, Emilio

Publication type:

Article

A comprehensive database of Duchenne and Becker muscular dystrophy patients (0-18 years old) in East China.

Published in:

Orphanet Journal of Rare Diseases, 2015, v. 10, n. 1, p. 1, doi. 10.1186/s13023-014-0220-7

By:

Xihua Li;
Lei Zhao;
Shuizhen Zhou;
Chaoping Hu;
Yiyun Shi;
Wei Shi;
Hui Li;
Fang Liu;
Bingbing Wu;
Yi Wang

Publication type:

Article

The effect of aerobic training on motor function and muscle architecture in children with Duchenne muscular dystrophy: A randomized controlled study.

Published in:

Clinical Rehabilitation, 2022, v. 36, n. 8, p. 1062, doi. 10.1177/02692155221095491

By:

Bulut, Numan;
Karaduman, Ayşe;
Alemdaroğlu-Gürbüz, İpek;
Yılmaz, Öznur;
Topaloğlu, Haluk;
Özçakar, Levent

Publication type:

Article

Quantitative muscle ultrasound detects disease progression in Duchenne muscular dystrophy.

Published in:

2017

By:

Zaidman, Craig M.;
Wu, Jim S.;
Kapur, Kush;
Pasternak, Amy;
Madabusi, Lavanya;
Yim, Sung;
Pacheck, Adam;
Szelag, Heather;
Harrington, Tim;
Darras, Basil T.;
Rutkove, Seward B.

Publication type:

journal article

Electrical impedance myography for assessment of Duchenne muscular dystrophy.

Published in:

2017

By:

Rutkove, Seward B.;
Kapur, Kush;
Zaidman, Craig M.;
Wu, Jim S.;
Pasternak, Amy;
Madabusi, Lavanya;
Yim, Sung;
Pacheck, Adam;
Szelag, Heather;
Harrington, Tim;
Darras, Basil T.

Publication type:

journal article

Serotonin and Histamine Therapy Increases Tetanic Forces of Myoblasts, Reduces Muscle Injury, and Improves Grip Strength Performance of Dmd<sup>mdx</sup> Mice.

Published in:

Dose-Response, 2015, v. 13, n. 4, p. 1, doi. 10.1177/1559325815616351

By:

Gurel, Volkan;
Lins, Jeremy;
Lambert, Kristyn;
Lazauski, Joan;
Spaulding, James;
McMichael, John

Publication type:

Article

Learning And Improvement In Hereditary Diseases.

Published in:

2016

By:

Morrison, Patrick J.

Publication type:

Speech

Physical training in boys with Duchenne Muscular Dystrophy: the protocol of the No Use is Disuse study.

Published in:

BMC Pediatrics, 2010, v. 10, p. 55, doi. 10.1186/1471-2431-10-55

By:

Jansen, Merel;
de Groot, Imelda J. M.;
van Alfen, Nens;
Geurts, Alexander C. H.

Publication type:

Article

Duchenne 型肌营养不良症运动疗法研究进展.

Published in:

Chinese Nursing Research, 2020, v. 34, n. 16, p. 2877, doi. 10.12102/j.issn.1009-6493.2020.16.013

By:

雷雨;
吴海龙;
刘杰;
黄啸

Publication type:

Article

P2RX7 purinoceptor: a therapeutic target for ameliorating the symptoms of duchenne muscular dystrophy.

Published in:

2015

By:

Sinadinos, Anthony;
Young, Christopher N. J.;
Al-Khalidi, Rasha;
Teti, Anna;
Kalinski, Paweł;
Mohamad, Shafini;
Floriot, Léonore;
Henry, Tiphaine;
Tozzi, Gianluca;
Jiang, Taiwen;
Wurtz, Olivier;
Lefebvre, Alexis;
Shugay, Mikhail;
Tong, Jie;
Vaudry, David;
Arkle, Stephen;
doRego, Jean-Claude;
Górecki, Dariusz C.

Publication type:

journal article

An overview of recent US-approved gene therapies for Duchenne muscular dystrophy and their respective clinical development programs.

Published in:

Drugs & Therapy Perspectives, 2023, v. 39, n. 4, p. 156, doi. 10.1007/s40267-023-00986-2

By:

Yu, Dale

Publication type:

Article

Duchenne Muscular Dystrophy: From Diagnosis to Therapy.

Published in:

Molecules, 2015, v. 20, n. 10, p. 18168, doi. 10.3390/molecules201018168

By:

Falzarano, Maria Sofia;
Scotton, Chiara;
Passarelli, Chiara;
Ferlini, Alessandra

Publication type:

Article

Intraarterial Injection of Muscle-derived CD34[sup +]Sca-1[sup +] Stem Cells Restores Dystrophin....

Published in:

Journal of Cell Biology, 2001, v. 152, n. 2, p. 335, doi. 10.1083/jcb.152.2.335

By:

Torrente, Yuan;
Tremblay, Jacques-P

Publication type:

Article

Skipping Multiple Exons to Treat DMD--Promises and Challenges.

Published in:

Biomedicines, 2018, v. 6, n. 1, p. 1, doi. 10.3390/biomedicines6010001

By:

Aslesh, Tejal;
Maruyama, Rika;
Yokota, Toshifumi

Publication type:

Article

Pathophysiology and Therapy of Cardiac Dysfunction in Duchenne Muscular Dystrophy.

Published in:

American Journal of Cardiovascular Drugs, 2011, v. 11, n. 5, p. 287, doi. 10.2165/11594070-000000000-00000

By:

Judge, Daniel P.;
Kass, David A.;
Thompson, W. Reid;
Wagner, Kathryn R.

Publication type:

Article

Newborn screening of duchenne muscular dystrophy specifically targeting deletions amenable to exon-skipping therapy.

Published in:

Scientific Reports, 2021, v. 11, n. 1, p. 1, doi. 10.1038/s41598-021-82725-z

By:

Beckers, Pablo;
Caberg, Jean-Hubert;
Dideberg, Vinciane;
Dangouloff, Tamara;
den Dunnen, Johan T.;
Bours, Vincent;
Servais, Laurent;
Boemer, François

Publication type:

Article

PMO-based let-7c site blocking oligonucleotide (SBO) mediated utrophin upregulation in mdx mice, a therapeutic approach for Duchenne muscular dystrophy (DMD).

Published in:

Scientific Reports, 2020, v. 10, n. 1, p. 1, doi. 10.1038/s41598-020-76338-1

By:

Sengupta, Kasturi;
Loro, Emanuele;
Khurana, Tejvir S.

Publication type:

Article

Applications of CRISPR/Cas9 for the Treatment of Duchenne Muscular Dystrophy.

Published in:

Journal of Personalized Medicine, 2018, v. 8, n. 4, p. 38, doi. 10.3390/jpm8040038

By:

Lim, Kenji Rowel Q.;
Yoon, Chantal;
Yokota, Toshifumi

Publication type:

Article

Multiple Exon Skipping in the Duchenne Muscular Dystrophy Hot Spots: Prospects and Challenges.

Published in:

Journal of Personalized Medicine, 2018, v. 8, n. 4, p. 41, doi. 10.3390/jpm8040041

By:

Echigoya, Yusuke;
Lim, Kenji Rowel Q.;
Nakamura, Akinori;
Yokota, Toshifumi

Publication type:

Article

Beneficial cilostazol therapeutic effects in mdx dystrophic skeletal muscle.

Published in:

Clinical & Experimental Pharmacology & Physiology, 2016, v. 43, n. 2, p. 259, doi. 10.1111/1440-1681.12521

By:

Hermes, Túlio de Almeida;
Macedo, Aline Barbosa;
Fogaça, Aline Reis;
Moraes, Luis Henrique Rapucci;
Faria, Felipe Meira;
Kido, Larissa Akemi;
Cagnon, Valéria Helena Alves;
Minatel, Elaine

Publication type:

Article

Increased sphingosine-1-phosphate improves muscle regeneration in acutely injured mdx mice.

Published in:

Skeletal Muscle, 2013, v. 3, n. 1, p. 1, doi. 10.1186/2044-5040-3-20

By:

Ieronimakis, Nicholas;
Pantoja, Mario;
Hays, Aislinn L.;
Dosey, Timothy L.;
Qi, Junlin;
Fischer, Karin A.;
Hoofnagle, Andrew N.;
Sadilek, Martin;
Chamberlain, Jeffrey S.;
Ruohola-Baker, Hannele;
Reyes, Morayma

Publication type:

Article

Genomics and cure: understanding narratives of patients with Duchenne muscular dystrophy in Japan.

Published in:

Anthropology & Medicine, 2018, v. 25, n. 1, p. 85, doi. 10.1080/13648470.2018.1427695

By:

Kato, Masae

Publication type:

Article

Genetic counseling for the dystrophinopathies—Practice resource of the National Society of Genetic Counselors.

Published in:

Journal of Genetic Counseling, 2025, v. 34, n. 1, p. 1, doi. 10.1002/jgc4.1892

By:

Pickart, Angela M.;
Martin, Ann S.;
Gross, Brianna N.;
Dellefave‐Castillo, Lisa M.;
McCallen, Leslie M.;
Nagaraj, Chinmayee B.;
Rippert, Alyssa L.;
Schultz, Catherine P.;
Ulm, Elizabeth A.;
Armstrong, Niki

Publication type:

Article

Transgenic expression of a myostatin inhibitor derived from follistatin increases skeletal muscle mass and ameliorates dystrophic pathology in mdx mice.

Published in:

FASEB Journal, 2008, v. 22, n. 2, p. 477, doi. 10.1096/fj.07-8673com

By:

Nakatani, Masashi;
Takehara, Yuka;
Sugino, Hiromu;
Matsumoto, Mitsuru;
Hashimoto, Osamu;
Hasegawa, Yoshihisa;
Murakami, Tatsuya;
Uezumi, Akiyoshi;
Takeda, Shin'ichi;
Noji, Sumihare;
Sunada, Yoshihide;
Tsuchida, Kunihiro

Publication type:

Article

Cardiac profile of asymptomatic children with Becker and Duchenne muscular dystrophy under treatment with steroids and with/without perindopril.

Published in:

2017

By:

Mavrogeni, Sophie;
Giannakopoulou, Aikaterini;
Papavasiliou, Antigoni;
Markousis-Mavrogenis, George;
Pons, Roser;
Karanasios, Evangelos;
Noutsias, Michel;
Kolovou, Genovefa;
Papadopoulos, George

Publication type:

journal article

Prednisolone in Duchenne muscular dystrophy with imminent loss of ambulation.

Published in:

Journal of Neurology, 2006, v. 253, n. 10, p. 1309, doi. 10.1007/s00415-006-0212-1

By:

Pradhan, Sunil;
Ghosh, Debabrata;
Srivastava, Niraj Kumar;
Kumar, Ashok;
Mittal, Balraj;
Pandey, Chandra Mani;
Singh, Uttam

Publication type:

Article

Duchenne muscular dystrophy: Still an incurable disease.

Published in:

2019

By:

Arora, Harneet

Publication type:

journal article

Commonly available outcome measures for use in Indian boys with Duchenne muscular dystrophy.

Published in:

2018

By:

Arora, Harneet

Publication type:

journal article

Elemental analysis of biological tissues of Dmd/J and C57BL/6J mice strains investigated by neutron activation analysis.

Published in:

Journal of Radioanalytical & Nuclear Chemistry, 2013, v. 296, n. 1, p. 579, doi. 10.1007/s10967-012-2005-6

By:

Metairon, Sabrina;
Zamboni, Cibele;
Suzuki, Miriam;
Bueno Junior, Carlos;
Sant'Anna, Osvaldo

Publication type:

Article

Rapamycin Ameliorates Dystrophic Phenotype in mdx Mouse Skeletal Muscle.

Published in:

Molecular Medicine, 2011, v. 17, n. 9/10, p. 917, doi. 10.2119/molmed.2010.00256

By:

Eghtesad, Saman;
Jhunjhunwala, Siddharth;
Little, Steven R.;
Clemens, Paula R.

Publication type:

Article

Assessing the Benefits and Harms Associated with Early Diagnosis from the Perspective of Parents with Multiple Children Diagnosed with Duchenne Muscular Dystrophy.

Published in:

International Journal of Neonatal Screening (IJNS), 2024, v. 10, n. 2, p. 32, doi. 10.3390/ijns10020032

By:

Bhattacharyya, Oindrila;
Campoamor, Nicola B.;
Armstrong, Niki;
Freed, Megan;
Schrader, Rachel;
Crossnohere, Norah L.;
Bridges, John F. P.

Publication type:

Article

Cognitive and Behavioral Profile of Egyptian Children with Duchenne Muscular Dystrophy.

Published in:

Alexandria Journal of Pediatrics, 2023, v. 36, n. 1, p. 51, doi. 10.4103/ajop.ajop_12_23

By:

Khalil, Mona;
Morsy, Nourhan Mohamed;
Elmaksoud, Marwa Abd

Publication type:

Article

Assessment of Treatment Effect With Multiple Outcomes in 2 Clinical Trials of Patients With Duchenne Muscular Dystrophy.

Published in:

JAMA Network Open, 2020, v. 3, n. 2, p. e1921306, doi. 10.1001/jamanetworkopen.2019.21306

By:

Li, Daniel;
McDonald, Craig M.;
Elfring, Gary L.;
Souza, Marcio;
McIntosh, Joseph;
Kim, Dae Hyun;
Wei, Lee-Jen

Publication type:

Article

Co-administration of deflazacort and doxycycline: a potential pharmacotherapy for Duchenne muscular dystrophy.

Published in:

Clinical & Experimental Pharmacology & Physiology, 2015, v. 42, n. 7, p. 788, doi. 10.1111/1440-1681.12417

By:

Pereira, Juliano Alves;
Marques, Maria Julia;
Santo Neto, Humberto

Publication type:

Article

Myoblots: dystrophin quantification by in‐cell western assay for a streamlined development of Duchenne muscular dystrophy (DMD) treatments.

Published in:

Neuropathology & Applied Neurobiology, 2018, v. 44, n. 5, p. 463, doi. 10.1111/nan.12448

By:

Ruiz‐Del‐Yerro, E.;
Garcia‐Jimenez, I.;
Mamchaoui, K.;
Arechavala‐Gomeza, V.

Publication type:

Article

Specific profiles of neurocognitive and reading functions in a sample of 42 Italian boys with Duchenne Muscular Dystrophy.

Published in:

Child Neuropsychology, 2013, v. 19, n. 4, p. 350, doi. 10.1080/09297049.2012.660912

By:

Lorusso, MariaLuisa;
Civati, Federica;
Molteni, Massimo;
Turconi, AnnaCarla;
Bresolin, Nereo;
D'Angelo, MariaGrazia

Publication type:

Article

Stem Cell Therapies to Treat Muscular Dystrophy.

Published in:

BioDrugs, 2010, v. 24, n. 4, p. 237, doi. 10.2165/11534300-000000000-00000

By:

Meregalli, Mirella;
Farini, Andrea;
Parolini, Daniele;
Maciotta, Simona;
Torrente, Yvan

Publication type:

Article

Přehled nových, a ještě novějších léků na Duchennovu svalovou dystrofii a spinální svalovou atrofii.

Published in:

Czecho-Slovak Pediatrics / Česko-Slovenská Pediatrie, 2019, v. 74, n. 3, p. 141

By:

Bálintová, Z.;
Juříková, L.;
Havlín, O.

Publication type:

Article

Autonomic Modulation in Duchenne Muscular Dystrophy during a Computer Task: A Prospective Control Trial.

Published in:

PLoS ONE, 2017, v. 12, n. 1, p. 1, doi. 10.1371/journal.pone.0169633

By:

Alvarez, Mayra Priscila Boscolo;
Silva, Talita Dias da;
Favero, Francis Meire;
Valenti, Vitor Engrácia;
Raimundo, Rodrigo Daminello;
Vanderlei, Luiz Carlos Marques;
Garner, David M.;
Monteiro, Carlos Bandeira de Mello

Publication type:

Article

Long-Term Quercetin Dietary Enrichment Partially Protects Dystrophic Skeletal Muscle.

Published in:

PLoS ONE, 2016, v. 11, n. 12, p. 1, doi. 10.1371/journal.pone.0168293

By:

Spaulding, Hannah R.;
Ballmann, Christopher G.;
Quindry, John C.;
Selsby, Joshua T.

Publication type:

Article