Works matching DE "THERAPEUTIC use of enzymes"


Results: 508
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    Kidney transplantation in patients with Fabry disease.

    Published in:
    Transplant International, 2009, v. 22, n. 4, p. 475, doi. 10.1111/j.1432-2277.2008.00824.x
    By:
    • Cybulla, Markus;
    • Walter, Kerstin Nanette;
    • Schwarting, Andreas;
    • DiVito, Raffaelle;
    • Feriozzi, Sandro;
    • Sunder-Plassmann, Gere
    Publication type:
    Article
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    Epidemiology of Mucopolysaccharidosis Type II According to the Register of the Russian Federation.

    Published in:
    Turkish Archives of Pediatrics, 2025, v. 60, n. 1, p. 41, doi. 10.5152/TurkArchPediatr.2025.24158
    By:
    • Buchinskaia, Natalia V.;
    • Zakharova, Ekaterina Yu.;
    • Koshevaya, Yulia S.;
    • Vechkasova, Anastasia O.;
    • Skitchenko, Rostislav K.;
    • Nikonov, Aleksandr M.;
    • Kurilova, Vera I.;
    • Maximova, Yulia V.;
    • Aksyanova, Khasyanya F.;
    • Bakulina, Elena G.;
    • Kononenko, Nina I.;
    • Osipova, Elena V.;
    • Kostik, Mikhail M.;
    • Kutsev, Sergei I.
    Publication type:
    Article
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    Therapeutic Enzymes:.

    Published in:
    Alternative & Complementary Therapies, 2005, v. 11, n. 2, p. 74, doi. 10.1089/act.2005.11.74
    By:
    • Meletis, Chris D.;
    • Barker, Jason E.
    Publication type:
    Article
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    LETTER FROM THE EDITOR.

    Published in:
    Gastroenterology & Hepatology, 2012, v. 8, n. 9, p. 562
    By:
    • Lichtenstein, Gary R.
    Publication type:
    Article
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    Childhood Pompe disease: clinical spectrum and genotype in 31 patients.

    Published in:
    2016
    By:
    • Van Capelle, C. I.;
    • Van der Meijden, J. C.;
    • Van den Hout, J. M. P.;
    • Jaeken, J.;
    • Baethmann, M.;
    • Voit, T.;
    • Kroos, M. A.;
    • Derks, T. G. J.;
    • Rubio-Gozalbo, M. E.;
    • Willemsen, M. A.;
    • Lachmann, R. H.;
    • Mengel, E.;
    • Michelakakis, H.;
    • de Jongste, J. C.;
    • Reuser, A. J. J.;
    • Van der Ploeg, A. T.
    Publication type:
    journal article
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    Alternative laronidase dose regimen for patients with mucopolysaccharidosis I: a multinational, retrospective, chart review case series.

    Published in:
    2016
    By:
    • Gandelman Horovitz, Dafne Dain;
    • Acosta, Angelina X.;
    • Giugliani, Roberto;
    • Hlavatá, Anna;
    • Hlavatá, Katarína;
    • Tchan, Michel C.;
    • Lopes Barth, Anneliese;
    • Cardoso Jr., Laercio;
    • Embiruçu de Araújo Leão, Emília Katiane;
    • Esposito, Ana Carolina;
    • Obikawa Kyosen, Sandra;
    • Moura De Souza, Carolina Fischinger;
    • Martins, Ana Maria;
    • Horovitz, Dafne Dain Gandelman;
    • Cardoso, Laercio Jr;
    • Kyosen, Sandra Obikawa;
    • De Souza, Carolina Fischinger Moura
    Publication type:
    journal article
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