Works matching DE "GENE therapy"

Results: 5000

Dual therapeutic benefit of electroporation-mediated DNA vaccination in vivo.

Published in:

2014

By:

Calvet, Christophe Y;
André, Franck M;
Mir, Lluis M

Publication type:

Opinion

A novel system for cloning human TCRs.

Published in:

OncoImmunology, 2014, v. 3, n. 1, p. N.PAG, doi. 10.4161/onci.27258

By:

Kobayashi, Eiji;
Kishi, Hiroyuki;
Muraguchi, Atsushi

Publication type:

Article

Combining cellular and gene therapy approaches for treatment of intracranial tumors.

Published in:

OncoImmunology, 2013, v. 2, n. 10, p. e25989-1, doi. 10.4161/onci.25989

By:

Hickey, Michelle J.;
Kasahara, Noriyuki;
Mueller, Barbara M.;
Kruse, Carol A.

Publication type:

Article

Strong emerging rationale for combining oncogene-targeted agents with immunotherapy.

Published in:

OncoImmunology, 2013, v. 2, n. 2, p. e22730-1, doi. 10.4161/onci.22730

By:

Lizée, Gregory;
Hwu, Patrick;
Yan Yang

Publication type:

Article

Limitations for TCR gene therapy by MHC-restricted fratricide and TCR-mediated hematopoietic stem cell toxicity.

Published in:

OncoImmunology, 2013, v. 2, n. 1, p. e22410-1, doi. 10.4161/onci.22410

By:

Schendel, Dolores J.;
Frankenberger, Bernhard

Publication type:

Article

Cell cycle progression score predicts metastatic progression of clear cell renal cell carcinoma after resection.

Published in:

Cancer Biomarkers, 2015, v. 15, n. 6, p. 861, doi. 10.3233/CBM-150530

By:

Askeland, Eric J.;
Chehval, Vincent A.;
Askeland, Ryan W.;
Fosso, Placede G.;
Sangale, Zaina;
Xu, Nafei;
Rajamani, Saradha;
Stone, Steven;
Brown, James A.

Publication type:

Article

MicroRNA in non-melanoma skin cancer.

Published in:

Cancer Biomarkers, 2012, v. 11, n. 6, p. 253, doi. 10.3233/CBM-2012-0274

By:

Sand, Michael;
Sand, Daniel;
Altmeyer, Peter;
Bechara, Falk G.

Publication type:

Article

Hypermethylation of collagen α2 (I) gene (COL1A2) is an independent predictor of survival in head and neck cancer.

Published in:

Cancer Biomarkers, 2012, v. 10, n. 3/4, p. 135, doi. 10.3233/CBM-2012-0242

By:

Misawa, Kiyoshi;
Kanazawa, Takeharu;
Misawa, Yuki;
Imai, Atsushi;
Endo, Shiori;
Hakamada, Katsura;
Mineta, Hiroyuki

Publication type:

Article

Breast cancer predisposition and brain hemispheric laterality specification likely share a common genetic cause.

Published in:

Breast Disease, 2012, v. 33, n. 1, p. 49

By:

Klar, Amar J. S.

Publication type:

Article

Gene Therapy for Breast and Ovarian Cancer with BRCA1.

Published in:

Breast Disease, 1998, v. 10, n. 1/2, p. 89, doi. 10.3233/BD-1998-101-211

By:

Tait, David L.;
Jensen, Roy A.;
Holt, Jeffrey T.;
Johnson, David H.;
Gralow, Julie;
King, Mary-Claire

Publication type:

Article

Neurotrophic factors for Parkinson's disease: Current status, progress, and remaining questions. Conclusions from a 2023 workshop.

Published in:

Journal of Parkinson's Disease, 2024, v. 14, n. 8, p. 1659, doi. 10.1177/1877718X241301041

By:

Barker, Roger A;
Saarma, Mart;
Svendsen, Clive N;
Morgan, Catherine;
Whone, Alan;
Fiandaca, Massimo S;
Luz, Matthias;
Bankiewicz, Krystof S;
Fiske, Brian;
Isaacs, Lyndsey;
Roach, Arthur;
Phipps, Thomas;
Kordower, Jeffrey H;
Lane, Emma L;
Huttunen, Henri J;
Sullivan, Aideen;
O'Keeffe, Gerard;
Yartseva, Valeria;
Federoff, Howard

Publication type:

Article

GDNF Therapy: Can We Make It Work?

Published in:

Journal of Parkinson's Disease, 2021, v. 11, n. 3, p. 1019, doi. 10.3233/JPD-212706

By:

Björklund, Anders

Publication type:

Article

Gene Therapy for Parkinson's Disease Associated with GBA1 Mutations.

Published in:

2021

By:

Abeliovich, Asa;
Hefti, Franz;
Sevigny, Jeffrey;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Case Study

An Update on Gene Therapy Approaches for Parkinson's Disease: Restoration of Dopaminergic Function.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S173, doi. 10.3233/JPD-212724

By:

Van Laar, Amber D.;
Van Laar, Victor S.;
San Sebastian, Waldy;
Merola, Aristide;
Elder, J. Bradley;
Lonser, Russell R.;
Bankiewicz, Krystof S.;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Improved Delivery Methods for Gene Therapy and Cell Transplantation in Parkinson's Disease.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S199, doi. 10.3233/JPD-212710

By:

Larson, Paul S.;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Bringing Advanced Therapies for Parkinson's Disease to the Clinic: The Scientist's Perspective.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S135, doi. 10.3233/JPD-212685

By:

Tomishima, Mark;
Kirkeby, Agnete;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Gene Therapy to Modulate Alpha-Synuclein in Synucleinopathies.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S189, doi. 10.3233/JPD-212679

By:

Sandoval, Ivette M.;
Marmion, David J.;
Meyers, Kimberly T.;
Manfredsson, Fredric P.;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Next-Generation Gene Therapy for Parkinson's Disease Using Engineered Viral Vectors.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S209, doi. 10.3233/JPD-212674

By:

Björklund, Tomas;
Davidsson, Marcus;
Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Part II: Cell and gene therapies.

Published in:

Journal of Parkinson's Disease, 2021, v. 11, p. S157

By:

Björklund, Anders;
Bloem, Bastiaan R.;
Brundin, Patrik;
Federoff, Howard

Publication type:

Article

Forecasts for the Attainment of Major Research Milestones in Parkinson's Disease.

Published in:

Journal of Parkinson's Disease, 2020, v. 10, n. 3, p. 1047, doi. 10.3233/JPD-201933

By:

Kane, Patrick Bodilly;
Benjamin, Daniel M.;
Barker, Roger A.;
Lang, Anthony E.;
Sherer, Todd;
Kimmelman, Jonathan

Publication type:

Article

CLINICAL TRIAL HIGHLIGHTS: 1. GENE THERAPY FOR PARKINSON'S, 2. PHASE 3 STUDY IN FOCUS - INTEC PHARMA'S ACCORDION PILL, 3. CLINICAL TRIALS RESOURCES.

Published in:

Journal of Parkinson's Disease, 2019, v. 9, n. 2, p. 251, doi. 10.3233/JPD-199001

By:

McFarthing, Kevin;
Prakash, Neha;
Simuni, Tanya

Publication type:

Article

Gene Therapy for Parkinson’s Disease, An Update.

Published in:

Journal of Parkinson's Disease, 2018, v. 8, n. 2, p. 195, doi. 10.3233/JPD-181331

By:

Axelsen, Tobias M.;
Woldbye, David P.D.

Publication type:

Article

Post-modern therapeutic approaches for progressive myoclonus epilepsy.

Published in:

Epileptic Disorders, 2016, v. 18, p. S154, doi. 10.1684/epd.2016.0862

By:

Minassian, Berge A.

Publication type:

Article

Update on Application of Oncolytic Virus‐Based Combination Therapy in the Treatment of Hepatocellular Carcinoma.

Published in:

Journal of Biochemical & Molecular Toxicology, 2025, v. 39, n. 6, p. 1, doi. 10.1002/jbt.70327

By:

Abd, Mariam Ayad;
Asiri, Mohammed;
Farhan, Shahd Rajab;
Sanghvi, Gaurav;
Roopashree, Rangaswamy;
Kashyap, Aditya;
Anand, D. Alex;
Panigrahi, Rajashree;
Mustafa, Yasser Fakri;
Gabaal, Baneen C.

Publication type:

Article

Ethical Debate Continues Over Access to Investigational Cell- and Gene-Based Interventions.

Published in:: Medical Ethics Advisor, 2025, v. 41, n. 7, p. 1
Publication type:: Article

Съвременните технологии на генното инженерство за редактиране на генома.

Published in:

Medical Review / Meditsinski Pregled, 2025, v. 61, n. 4, p. 64

By:

Vekov, T.;
Dimova, L.;
Becheva-Kraychir, E.;
Belcheva, V.

Publication type:

Article

An all-in-one MnO₂-DNA assembly nanoplatform for imaging, detection, and gene-chemodynamic combination therapy of MCF-7 cells.

Published in:

Microchimica Acta, 2025, v. 192, n. 6, p. 1, doi. 10.1007/s00604-025-07282-y

By:

Zhang, Ruyan;
Zhang, Zhiqing;
Zhang, Guodong;
Zhuang, Jingyun;
Huo, Xiaobing;
Ning, Gan;
Weng, Tianxin;
Wang, Xiufeng;
Zhou, Ting;
Wang, Fang

Publication type:

Article

Lipid nanoparticle delivery of the CRISPR/Cas9 system directly into the mitochondria of cells carrying m.7778G>T mutation in MtDNA (mt-Atp8).

Published in:

Scientific Reports, 2025, v. 15, n. 1, p. 1, doi. 10.1038/s41598-025-03671-8

By:

Norota, Kaede;
Ishizuka, Sen;
Hirose, Misa;
Sato, Yusuke;
Maeki, Masatoshi;
Tokeshi, Manabu;
Ibrahim, Saleh M.;
Harashima, Hideyoshi;
Yamada, Yuma

Publication type:

Article

Psychosocial Care During Novel Therapies in Haemophilia: A Psychological Framework.

Published in:

Haemophilia, 2025, v. 31, n. 3, p. 585, doi. 10.1111/hae.70008

By:

Haverman, Lotte;
Teela, Lorynn;
O'Brien, Gráinne;
Bučková, Petra;
Golan, Gaby;
Rooney, Gloria;
Bartels, Karolien;
Torres‐Ortuño, Ana;
Burgess, Christina

Publication type:

Article

Recommendations for Psychosocial Support during Gene Therapy: Results From an EAHAD Interdisciplinary Roundtable.

Published in:

Haemophilia, 2025, v. 31, n. 3, p. 578, doi. 10.1111/hae.70005

By:

Teela, Lorynn;
O'Brien, Gráinne;
Bučková, Petra;
Golan, Gaby;
Rooney, Gloria;
Bartels, Karolien;
Torres‐Ortuño, Ana;
Burgess, Christina;
Haverman, Lotte

Publication type:

Article

A synthetic platform for developing recombinant adeno‐associated virus type 8 producer cell lines.

Published in:

Biotechnology Progress, 2025, v. 41, n. 3, p. 1, doi. 10.1002/btpr.70009

By:

Lin, Yu‐Chieh;
Kuo, Han‐Jung;
Lu, Min;
Mahl, Thomas;
Aslanidi, George;
Hu, Wei‐Shou

Publication type:

Article

Stipulations of cell and gene therapy and the ties to biomanufacturing.

Published in:

Biotechnology Progress, 2025, v. 41, n. 3, p. 1, doi. 10.1002/btpr.3521

By:

Allisha, Justin;
Das, Juthika;
Dunnigan, Thomas;
Sharfstein, Susan T.;
Datta, Payel

Publication type:

Article

Comparison of the efficiency of different promoters driving foreign gene expression in microglia.

Published in:

Journal of Capital Normal University (Natural Science Edition), 2025, v. 46, n. 3, p. 59, doi. 10.19789/j.1004-9398.2025.03.009

By:

QIN Hongni;
XIE Yuzhen;
ZHANG Nannan;
ZHANG Qingshuo;
WU Fan

Publication type:

Article

Adeno-associated virus vector modification based on directed evolution technology for gene therapy targeting head and neck squamous cell carcinoma.

Published in:

Frontiers in Oncology, 2025, p. 1, doi. 10.3389/fonc.2025.1566584

By:

Zhu, Yiyuan;
Ji, Wei;
Zhang, Qi;
Dong, Yanbo;
Liu, Liangfa

Publication type:

Article

Blueprint for clinical N-of-1 strategies with off-label precision treatments in monogenic epilepsies.

Published in:

Orphanet Journal of Rare Diseases, 2025, v. 20, n. 1, p. 1, doi. 10.1186/s13023-025-03750-z

By:

Defelippe, Victoria M.;
Brilstra, Eva H.;
Otte, Willem M.;
van Thiel, Ghislaine J. M. W.;
Cross, Helen J.;
O'Callaghan, Finbar;
De Giorgis, Valentina;
Perucca, Emilio;
Braun, Kees P. J.;
Jansen, Floor E.

Publication type:

Article

Alloimmunization as a barrier to gene therapy in sickle cell disease.

Published in:

Transfusion, 2025, v. 65, n. 6, p. 1035, doi. 10.1111/trf.18266

By:

Abrams, Hannah R.;
Saifee, Nabiha H.;
Miller, William S.;
Cortez, Antonio;
Hasan, Rida A.;
Panch, Sandhya R.;
Fertrin, Kleber Y.

Publication type:

Article

Delivery of a Muscle-Targeted Adeno-Associated Vector Via Ex Vivo Normothermic Perfusion Is Efficient, Durable, and Safe in a Preclinical Porcine Heart Transplant Model.

Published in:

Transplant International, 2025, p. 1, doi. 10.3389/ti.2025.13971

By:

Dewan, Krish C.;
Chen, Jeng-Wei;
Lobo, Alejandro A.;
Gross, Ryan T.;
Wang, Chunbo;
Rivera, Karla G.;
Tran, Keely Dieplin;
Ngeve, Smith;
Johnston, Violet G.;
Wendell, David;
Glass, Carolyn K.;
Evans, Amy;
Ho, Sam;
Lezberg, Paul;
Casy, Widler;
Bazile, Marla;
Patel, Kruti;
Cockrell, Adam S.;
Milano, Carmelo A.;
Bowles, Dawn

Publication type:

Article

Rôle de l'écho-endoscopie dans la prise en charge du cancer du pancréas.

Published in:

2025

By:

Buscail, Louis

Publication type:

Editorial

Improving the Efficiency and Safety of Human CCR5 Gene Editing by Selection of Optimal Guide RNAs for SpCAS9 and CAS12A.

Published in:

Molecular Biology, 2025, v. 59, n. 2, p. 205, doi. 10.1134/S0026893324700833

By:

Mintaev, R. R.;
Glazkova, D. V.;
Taran, J. A.;
Bogoslovskaya, E. V.;
Shipulin, G. A.

Publication type:

Article

Transdermal delivery of CRISPR/Cas9-mediated melanoma gene therapy via polyamines-modified thermosensitive hydrogels.

Published in:

Journal of Nanobiotechnology, 2025, v. 23, n. 1, p. 1, doi. 10.1186/s12951-025-03523-7

By:

Li, Meng;
Zhou, Songli;
Zhang, Suqin;
Xie, Xingyu;
Nie, Junqi;
Wang, Qi;
Ma, Lixin;
Cheng, Yibin;
Luo, Jingwen

Publication type:

Article

Systematic Identification of Candidate Genes for Inherited Retinal Disease Gene Therapy Integrating Worldwide IRD Cohort and Single‐Cell Analysis.

Published in:

Journal of Ophthalmology, 2025, v. 2025, p. 1, doi. 10.1155/joph/7014745

By:

Wang, Ching-Yun;
Chen, Lawrence;
Lin, Ting-Yi;
Huang, Shun-Ping;
Ahmadieh, Hamid

Publication type:

Article

Neutralizing Antibodies: Role in Immune Response and Viral Vector Based Gene Therapy.

Published in:

International Journal of Molecular Sciences, 2025, v. 26, n. 11, p. 5224, doi. 10.3390/ijms26115224

By:

Tsaregorodtseva, Tatiana S.;
Gubaidullina, Aigul A.;
Kayumova, Beata R.;
Shaimardanova, Alisa A.;
Issa, Shaza S.;
Solovyeva, Valeriya V.;
Sufianov, Albert A.;
Sufianova, Galina Z.;
Rizvanov, Albert A.

Publication type:

Article

Adoptive Transfer of Lepr + Bone Marrow Cells Attenuates the Osteopetrotic Phenotype of db / db Mice.

Published in:

International Journal of Molecular Sciences, 2025, v. 26, n. 11, p. 5120, doi. 10.3390/ijms26115120

By:

Turner, Russell T.;
Wong, Carmen P.;
Philbrick, Kenneth A.;
Keune, Jessica A.;
Labut, Edwin M.;
Menn, Scott A.;
Branscum, Adam J.;
Iwaniec, Urszula T.

Publication type:

Article

Surface Modification, Toxicity, and Applications of Carbon Dots to Cancer Theranosis: A Review.

Published in:

Nanomaterials (2079-4991), 2025, v. 15, n. 11, p. 781, doi. 10.3390/nano15110781

By:

Tegafaw, Tirusew;
Mulugeta, Endale;
Zhao, Dejun;
Liu, Ying;
Chen, Xiaoran;
Baek, Ahrum;
Kim, Jihyun;
Chang, Yongmin;
Lee, Gang Ho

Publication type:

Article

Improved productivity of recombinant adeno-associated virus (rAAV) via triple transfection of HEK293 cells using perfusion cultivation.

Published in:

Bioprocess & Biosystems Engineering, 2025, v. 48, n. 7, p. 1159, doi. 10.1007/s00449-025-03167-9

By:

Nie, Jianqi;
Xu, Zhaojing;
Sun, Yang;
Ren, He;
Song, Zichuan;
Zhang, Yan;
Bai, Zhonghu

Publication type:

Article

Correction: Reporting preclinical gene therapy studies in the field of Niemann-Pick type C disease according to the ARRIVE guidelines.

Published in:

2025

By:

Rasmussen, Charlotte Laurfelt Munch;
Burkhart, Annette;
Moos, Torben;
Thomsen, Louiza Bohn

Publication type:

Correction Notice

Advances in the molecular signaling mechanisms of VEGF/VEGFR2 in fundus neovascularization disease (Review).

Published in:

Experimental & Therapeutic Medicine, 2025, v. 30, n. 1, p. N.PAG, doi. 10.3892/etm.2025.12893

By:

Li, Huan Shen;
Huang, Xiong Gao

Publication type:

Article

Anticancer effects of zinc ion-mediated DNA demethylation in oesophageal squamous cell carcinoma.

Published in:

Frontiers in Pharmacology, 2025, p. 1, doi. 10.3389/fphar.2025.1559675

By:

Zhou, Bin;
Wang, Changchun;
Huang, Yueyu;
Yang, Xuping;
Ye, Ting;
Shen, Lize;
Lv, Qiaoli;
Mao, Weimin;
Zhao, An

Publication type:

Article

An update on diagnosis and treatments of childhood interstitial lung diseases.

Published in:

Breathe, 2025, v. 21, n. 2, p. 1, doi. 10.1183/20734735.0004-2025

By:

Marczak, Honorata;
Krenke, Katarzyna;
Griese, Matthias;
Carlens, Julia;
Seidl, Elias;
Gilbert, Carlee;
Emiralioglu, Nagehan;
Torrent-Vernetta, Alba;
Willemse, Brigitte;
Epaud, Ralph;
Delestrain, Celine;
Louvrier, Camille;
Koucky, Václav;
Nathan, Nadia

Publication type:

Article

DNA Nanotubule‐Based Nanodevices with ATP‐Responsive Gating for Direct Cytosolic Delivery of Nucleic Acids and Proteins.

Published in:

Angewandte Chemie, 2025, v. 137, n. 24, p. 1, doi. 10.1002/ange.202505290

By:

Gao, Di;
Xu, Ziqi;
Li, Xiangli;
Zhao, Yuhan;
Min, Qianhao;
Chen, Zixuan;
Xu, Qin;
Tian, Ye;
Xu, Junpeng;
Zhu, Jun‐Jie

Publication type:

Article