Works about GAUCHER'S disease treatment
Results: 111
Total synthesis of N -butyl-1-deoxynojirimycin.
- Published in:
- Journal of Carbohydrate Chemistry, 2016, v. 35, n. 8/9, p. 445, doi. 10.1080/07328303.2017.1330415
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- Publication type:
- Article
Successful mobilization with plerixafor and autologous hematopoietic SCT in a patient with refractory Hodgkin's lymphoma and Gaucher disease.
- Published in:
- 2011
- By:
- Publication type:
- Letter
QUALITY OF LIFE OF PATIENTS WITH GAUCHER DISEASE.
- Published in:
- Journal of Nursing UFPE / Revista de Enfermagem UFPE, 2017, v. 11, n. 11, p. 4282, doi. 10.5205/reuol.23542-49901-1-ED.1111201702
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- Publication type:
- Article
Small Bowel Mucosal Involvement and Mesenteric Mass Formation in a Young Female with Type 3 Gaucher Disease. A.
- Published in:
- 2018
- By:
- Publication type:
- Case Study
Shire's replacement enzymes validate gene activation.
- Published in:
- Nature Biotechnology, 2010, v. 28, n. 11, p. 1139, doi. 10.1038/nbt1110-1139a
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- Publication type:
- Article
Pfizer stakes a claim in plant cell–made biopharmaceuticals.
- Published in:
- Nature Biotechnology, 2010, v. 28, n. 2, p. 107, doi. 10.1038/nbt0210-107
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- Publication type:
- Article
Neutralizing antibodies to therapeutic enzymes: considerations for testing, prevention and treatment.
- Published in:
- Nature Biotechnology, 2008, v. 26, n. 8, p. 901, doi. 10.1038/nbt.1484
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- Publication type:
- Article
EMEA approves OGS drug rejected by FDA.
- Published in:
- Nature Biotechnology, 2002, v. 20, n. 9, p. 858, doi. 10.1038/nbt0902-858
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- Publication type:
- Article
Interruption in enzyme replacement therapy for gaucher disease.
- Published in:
- British Journal of Haematology, 2001, v. 113, n. 4, p. 1087, doi. 10.1046/j.1365-2141.2001.02821-11.x
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- Publication type:
- Article
Reply to vom dahl et al.
- Published in:
- British Journal of Haematology, 2001, v. 113, n. 4, p. 1086, doi. 10.1046/j.1365-2141.2001.02821-10.x
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- Publication type:
- Article
Withdrawal of enzyme replacement therapy in Gaucher's disease.
- Published in:
- British Journal of Haematology, 2000, v. 110, n. 2, p. 488, doi. 10.1046/j.1365-2141.2000.02177.x
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- Publication type:
- Article
Generation of a Chinese Hamster Ovary Cell Line Producing Recombinant Human Glucocerebrosidase.
- Published in:
- Journal of Biomedicine & Biotechnology, 2012, v. 2012, p. 1, doi. 10.1155/2012/875383
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- Publication type:
- Article
Improvement of life quality measured by Lansky Score after enzymatic replacement therapy in children with Gaucher disease type 1.
- Published in:
- Molecular Genetics & Genomic Medicine, 2018, v. 6, n. 1, p. 27, doi. 10.1002/mgg3.339
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- Publication type:
- Article
PATIENTS WITH GAUCHER DISEASE: RESULTS OF LONG FOLLOW UP.
- Published in:
- Erciyes Medical Journal / Erciyes Tip Dergisi, 2018, v. 40, n. 1, p. S23
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- Publication type:
- Article
Glycosylation and functionality of recombinant ß-glucocerebrosidase from various production systems.
- Published in:
- Bioscience Reports, 2013, v. 33, n. 5, p. 771, doi. 10.1042/BSR20130081
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- Publication type:
- Article
Echocardiographic assessment in children with Gaucher disease receiving enzyme replacement therapy.
- Published in:
- 2012
- By:
- Publication type:
- Letter
Gaucher disease in Iraqi children (Clinical, diagnostic & therapeutic aspects).
- Published in:
- Pakistan Journal of Medical Sciences, 2016, v. 32, n. 2, p. 319, doi. 10.12669/pjms.322.9316
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- Publication type:
- Article
A branch retinal artery occlusion in a patient with Gaucher disease.
- Published in:
- 2012
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- Publication type:
- Report
Target identification: Targeting neuronal loss in Gaucher's disease.
- Published in:
- Nature Reviews Drug Discovery, 2014, v. 13, n. 3, p. 178, doi. 10.1038/nrd4270
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- Publication type:
- Article
Quality of life assessment in adults with type 1 Gaucher disease.
- Published in:
- 1999
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- Publication type:
- journal article
VPRIV.
- Published in:
- Formulary, 2010, v. 45, n. 4, p. 113
- Publication type:
- Article
Discussed Poster Abstracts.
- Published in:
- 2018
- Publication type:
- Abstract
Goal-oriented therapy with miglustat in Gaucher disease.
- Published in:
- Current Medical Research & Opinion, 2009, v. 25, n. 1, p. 23, doi. 10.1185/03007990802576518
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- Publication type:
- Article
Allogeneic Hematopoietic Stem Cell Transplantation for Treatment of Gaucher Disease.
- Published in:
- Pediatric Hematology & Oncology, 2013, v. 30, n. 5, p. 459, doi. 10.3109/08880018.2013.793757
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- Publication type:
- Article
Response to the Letter: Allogeneic Hematopoietic Stem Cell Transplantation for Treatment of Gaucher Disease.
- Published in:
- Pediatric Hematology & Oncology, 2013, v. 30, n. 5, p. 462, doi. 10.3109/08880018.2013.793758
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- Publication type:
- Article
Treatment of severe pulmonary hypertension with inhaled iloprost.
- Published in:
- 2003
- By:
- Publication type:
- Case Study
Pulmonary hypertension developing after alglucerase therapy in two patients with type 1 Gaucher..
- Published in:
- Annals of Internal Medicine, 1996, v. 125, n. 11, p. 901, doi. 10.7326/0003-4819-125-11-199612010-00005
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- Publication type:
- Article
Enzyme therapy in type 1 Gaucher disease: Comparative efficacy of mannose-terminated...
- Published in:
- Annals of Internal Medicine, 1995, v. 122, n. 1, p. 33, doi. 10.7326/0003-4819-122-1-199501010-00005
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- Publication type:
- Article
Therapeutic potential of resveratrol for the treatment of type III Gaucher disease.
- Published in:
- Neurology Asia, 2015, v. 20, n. 1, p. 43
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- Publication type:
- Article
TYPE 2 GAUCHER DISEASE: ONSET AND EVOLUTION - CASE REPORT.
- Published in:
- Romanian Journal of Pediatrics / Revista Romana de Pediatrie, 2015, v. 64, n. 3, p. 293, doi. 10.37897/rjp.2015.3.12
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- Publication type:
- Article
How we manage Gaucher Disease in the era of choices.
- Published in:
- British Journal of Haematology, 2018, v. 182, n. 4, p. 467, doi. 10.1111/bjh.15402
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- Publication type:
- Article
Abundant Hepatic Gaucher-Like Cells Following Chemotherapy and Bone Marrow Transplantation for Hematologic Malignancy: Report of Two Cases.
- Published in:
- International Journal of Surgical Pathology, 2013, v. 21, n. 1, p. 89, doi. 10.1177/1066896912456081
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- Publication type:
- Article
Partial splenic embolization in a child with Gaucher disease, massive splenomegaly and severe thrombocytopenia.
- Published in:
- Pediatric Radiology, 2009, v. 39, n. 9, p. 1006, doi. 10.1007/s00247-009-1303-9
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- Publication type:
- Article
Splenic nodules in paediatric Gaucher disease treated by enzyme replacement therapy.
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- Pediatric Radiology, 2008, v. 38, n. 6, p. 657, doi. 10.1007/s00247-008-0811-3
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- Publication type:
- Article
The natural history of Gaucher disease type 1 in 31 patients over a median of 15 years: a retrospective study.
- Published in:
- Internal Medicine Journal, 2024, v. 54, n. 10, p. 1661, doi. 10.1111/imj.16503
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- Publication type:
- Article
IMMUNOGLOBULIN HEAVY CHAIN GENE REARRANGEMENTS IN PATIENTS WITH GAUCHER DISEASE.
- Published in:
- Journal of Medical Biochemistry, 2018, v. 37, n. 3, p. 307, doi. 10.1515/jomb-2017-0061
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- Publication type:
- Article
Achievement of Therapeutic Goals with Low-Dose Imiglucerase in Gaucher Disease: A Single-Center Experience.
- Published in:
- Advances in Hematology, 2013, p. 1, doi. 10.1155/2013/151506
- By:
- Publication type:
- Article
Pharmacokinetics of Novel Plant Cell-Expressed Taliglucerase Alfa in Adult and Pediatric Patients with Gaucher Disease.
- Published in:
- PLoS ONE, 2015, v. 10, n. 6, p. 1, doi. 10.1371/journal.pone.0128986
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- Publication type:
- Article
Miglustat: withdrawal by manufacturer.
- Published in:
- WHO Drug Information, 2008, v. 22, n. 1, p. 21
- Publication type:
- Article
Novel Therapies.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2014, v. 12, n. 1, p. 26
- Publication type:
- Article
Novel Therapies.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2013, v. 11, n. 4, p. 122
- Publication type:
- Article
Taliglucerase alfa leads to favorable bone marrow responses in patients with type I Gaucher disease.
- Published in:
- 2013
- By:
- Publication type:
- Opinion
Velaglucerase alfa enzyme replacement therapy compared with imiglucerase in patients with Gaucher disease.
- Published in:
- 2013
- By:
- Publication type:
- Opinion
Altered innate function of plasmacytoid dendritic cells restored by enzyme replacement therapy in Gaucher disease.
- Published in:
- 2013
- By:
- Publication type:
- Opinion
Successful desensitization to imiglucerase of an adult patient diagnosed with type I Gaucher disease.
- Published in:
- 2013
- By:
- Publication type:
- Opinion
Gauchers disease - a reappraisal of hematopoietic stem cell transplantation.
- Published in:
- 2013
- By:
- Publication type:
- Opinion
Evaluation of miglustat as maintenance therapy after enzyme therapy on adults with stable type 1 Gaucher disease: a prospective, open-label non-inferiority study.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2013, v. 11, n. 2, p. 49
- By:
- Publication type:
- Article
Miscellaneous.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2013, v. 11, n. 1, p. 31
- Publication type:
- Article
Novel Therapies.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2013, v. 11, n. 1, p. 27
- Publication type:
- Article
Clinical Manifestations.
- Published in:
- Current Medical Literature: Lysosomal Storage Disease, 2013, v. 11, n. 1, p. 20
- Publication type:
- Article