Works matching DE "ANIMAL models of lysosomal storage diseases"
Results: 2
Preclinical Dose-Finding Study With a Liver-Tropic, Recombinant AAV-2/8 Vector in the Mouse Model of Galactosialidosis.
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- Molecular Therapy, 2012, v. 20, n. 2, p. 267, doi. 10.1038/mt.2011.227
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- Article
Central nervous system pathology in preclinical MPS IIIB dogs reveals progressive changes in clinically relevant brain regions.
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- Scientific Reports, 2020, v. 10, n. 1, p. N.PAG, doi. 10.1038/s41598-020-77032-y
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- Article