Found: 17
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Assessment of non-myelotoxic agents as a preparatory regimen for hematopoietic stem cell gene therapy.
- Published in:
- Human Cell, 2025, v. 38, n. 1, p. 1, doi. 10.1007/s13577-024-01130-6
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- Publication type:
- Article
Gene and Cellular Therapies for Leukodystrophies.
- Published in:
- Pharmaceutics, 2023, v. 15, n. 11, p. 2522, doi. 10.3390/pharmaceutics15112522
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- Publication type:
- Article
Gene Augmentation and Editing to Improve TCR Engineered T Cell Therapy against Solid Tumors.
- Published in:
- Vaccines, 2020, v. 8, n. 4, p. 733, doi. 10.3390/vaccines8040733
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- Publication type:
- Article
Correction of Griscelli Syndrome Type 2 causing mutations in the RAB27A gene with CRISPR/Cas9.
- Published in:
- Turkish Journal of Biology, 2024, v. 48, n. 5, p. 290, doi. 10.55730/1300-0152.2705
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- Publication type:
- Article
Strategies to Genetically Modulate Dendritic Cells to Potentiate Anti-Tumor Responses in Hematologic Malignancies.
- Published in:
- Frontiers in Immunology, 2018, p. 1, doi. 10.3389/fimmu.2018.00982
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- Publication type:
- Article
Angiopoietin-Like Protein 3 Promotes Preservation of Stemness during <i>Ex Vivo</i> Expansion of Murine Hematopoietic Stem Cells.
- Published in:
- PLoS ONE, 2014, v. 9, n. 8, p. 1, doi. 10.1371/journal.pone.0105642
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- Publication type:
- Article
Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene.
- Published in:
- Molecular Therapy, 2012, v. 20, n. 10, p. 1968, doi. 10.1038/mt.2012.110
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- Publication type:
- Article
Human post-mortem organotypic brain slice cultures: a tool to study pathomechanisms and test therapies.
- Published in:
- Acta Neuropathologica Communications, 2024, v. 12, n. 1, p. 1, doi. 10.1186/s40478-024-01784-1
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- Publication type:
- Article
Mitochondrial Neurogastrointestinal Encephalomyopathy Caused by Thymidine Phosphorylase Enzyme Deficiency: From Pathogenesis to Emerging Therapeutic Options.
- Published in:
- Frontiers in Cellular Neuroscience, 2017, v. 11, p. 1, doi. 10.3389/fncel.2017.00031
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- Publication type:
- Article
Focal lesions following intracerebral gene therapy for mucopolysaccharidosis IIIA.
- Published in:
- Annals of Clinical & Translational Neurology, 2023, v. 10, n. 6, p. 904, doi. 10.1002/acn3.51772
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- Publication type:
- Article
Transplantation, gene therapy and intestinal pathology in MNGIE patients and mice.
- Published in:
- 2018
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- Publication type:
- journal article
Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-optimized IL2RG Gene and Minimal Pretransplant Conditioning.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 10, p. 1867, doi. 10.1038/mt.2011.127
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- Publication type:
- Article
470. ABCB4 P-Glycoprotein Reduces Infectivity of Lentiviral Particles by Increasing Their Phosphatidylcholine Content.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S182, doi. 10.1016/j.ymthe.2006.08.539
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- Publication type:
- Article
Kupffer Cells and Not Liver Sinusoidal Endothelial Cells Prevent Lentiviral Transduction of Hepatocytes
- Published in:
- Molecular Therapy, 2005, v. 11, n. 1, p. 26, doi. 10.1016/j.ymthe.2004.09.012
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- Publication type:
- Article
Long-term correction of bilirubin UDPglucuronyltransferase deficiency in rats by in utero lentiviral gene transfer
- Published in:
- Molecular Therapy, 2003, v. 8, n. 4, p. 593, doi. 10.1016/S1525-0016(03)00234-X
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- Publication type:
- Article
Gene Therapy Developments for Pompe Disease.
- Published in:
- Biomedicines, 2022, v. 10, n. 2, p. 302, doi. 10.3390/biomedicines10020302
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- Publication type:
- Article
Alteration of viral lipid composition by expression of the phospholipid floppase ABCB4 reduces HIV vector infectivity.
- Published in:
- Retrovirology, 2008, v. 5, p. 1, doi. 10.1186/1742-4690-5-14
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- Publication type:
- Article