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  • Mucopolysaccharidosis VII in Brazil: natural history and clinical findings.

    Published in:
    2021
    By:
    • Giugliani, Roberto;
    • Barth, Anneliese Lopes;
    • Dumas, Melissa Rossi Calvão;
    • da Silva Franco, José Francisco;
    • de Rosso Giuliani, Liane;
    • Grangeiro, Carlos Henrique Paiva;
    • Horovitz, Dafne Dain Gandelman;
    • Kim, Chong Ae;
    • de Araújo Leão, Emilia Katiane Embiruçu;
    • de Medeiros, Paula Frassinetti Vasconcelos;
    • Miguel, Diego Santana Chaves Geraldo;
    • Moreira, Maria Espírito Santo Almeida;
    • dos Santos, Helena Maria Guimarães Pimentel;
    • da Silva, Luiz Carlos Santana;
    • da Silva, Luiz Roberto;
    • de Souza, Isabel Neves;
    • Nalin, Tatiele;
    • Garcia, Daniel
    Publication type:
    journal article