OpenURL Connection Search

Select item for more details and to access through your institution.

Evaluation of rAAVrh74 gene therapy vector seroprevalence by measurement of total binding antibodies in patients with Duchenne muscular dystrophy.
Published in:
Therapeutic Advances in Neurological Disorders, 2023, p. 1, doi. 10.1177/17562864221149781
By:
- Goedeker, Natalie L.;
- Dharia, Sachi D.;
- Griffin, Danielle A.;
- Coy, Jesantha;
- Truesdale, Todd;
- Parikh, Rajan;
- Whitehouse, Kasen;
- Santra, Sourav;
- Asher, Damon R.;
- Zaidman, Craig M.
Publication type:
Article
Evaluation of rAAVrh74 gene therapy vector seroprevalence by measurement of total binding antibodies in patients with Duchenne muscular dystrophy.
Published in:
Therapeutic Advances in Neurological Disorders, 2023, v. 16, p. 1, doi. 10.1177/17562864221149781
By:
- Goedeker, Natalie L.;
- Dharia, Sachi D.;
- Griffin, Danielle A.;
- Coy, Jesantha;
- Truesdale, Todd;
- Parikh, Rajan;
- Whitehouse, Kasen;
- Santra, Sourav;
- Asher, Damon R.;
- Zaidman, Craig M.
Publication type:
Article
Quantitative Ultrasound Assessment of Duchenne Muscular Dystrophy Using Edge Detection Analysis.
Published in:
Journal of Ultrasound in Medicine, 2016, v. 35, n. 9, p. 1889, doi. 10.7863/ultra.15.04065
By:
- Koppaka, Sisir;
- Shklyar, Irina;
- Rutkove, Seward B.;
- Darras, Basil T.;
- Anthony, Brian W.;
- Zaidman, Craig M.;
- Wu, Jim S.
Publication type:
Article
Quantitative muscle echointensity: A practical approach using ultrasound to evaluate children with suspected neuromuscular disorders.
Published in:
Muscle & Nerve, 2021, v. 64, n. 1, p. 6, doi. 10.1002/mus.27258
By:
- Zaidman, Craig M.;
- Hobson‐Webb, Lisa D.
Publication type:
Article
Laboratory monitoring of nusinersen safety.
Published in:
2021
By:
- Goedeker, Natalie L.;
- Gibbons, Jennifer L.;
- Varadhachary, Arun S.;
- Connolly, Anne M.;
- Zaidman, Craig M.
Publication type:
journal article
The Spinal Muscular Atrophy Health Index: A novel outcome for measuring how a patient feels and functions.
Published in:
2021
By:
- Zizzi, Christine E.;
- Luebbe, Elizabeth;
- Mongiovi, Phillip;
- Hunter, Michael;
- Dilek, Nuran;
- Garland, Connie;
- Ciafaloni, Emma;
- Zaidman, Craig M.;
- Kissel, John T.;
- McDermott, Michael P.;
- Johnson, Nicholas;
- Sansone, Valeria;
- Heatwole, Chad R.
Publication type:
journal article
Pulse oral corticosteroids in pediatric chronic inflammatory demyelinating polyneuropathy.
Published in:
Muscle & Nerve, 2020, v. 62, n. 6, p. 705, doi. 10.1002/mus.27058
By:
- Rogers, Amanda B.;
- Zaidman, Craig M.;
- Connolly, Anne M.
Publication type:
Article
Twice‐weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2019, v. 59, n. 6, p. 650, doi. 10.1002/mus.26441
By:
- Connolly, Anne M.;
- Zaidman, Craig M.;
- Golumbek, Paul T.;
- Cradock, Mary M.;
- Flanigan, Kevin M.;
- Kuntz, Nancy L.;
- Finkel, Richard S.;
- McDonald, Craig M.;
- Iannaccone, Susan T.;
- Anand, Pallavi;
- Siener, Catherine A.;
- Florence, Julaine M.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Johnson, Linda B.;
- Nicorici, Alina;
- Nelson, Leslie L.;
- Mendell, Jerry R.
Publication type:
Article
Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy.
Published in:
2019
By:
- Connolly, Anne M;
- Zaidman, Craig M;
- Golumbek, Paul T;
- Cradock, Mary M;
- Flanigan, Kevin M;
- Kuntz, Nancy L;
- Finkel, Richard S;
- McDonald, Craig M;
- Iannaccone, Susan T;
- Anand, Pallavi;
- Siener, Catherine A;
- Florence, Julaine M;
- Lowes, Linda P;
- Alfano, Lindsay N;
- Johnson, Linda B;
- Nicorici, Alina;
- Nelson, Leslie L;
- Mendell, Jerry R;
- MDA DMD Clinical Research Network
Publication type:
journal article
Reliability of bedside ultrasound of limb and diaphragm muscle thickness in critically ill children.
Published in:
2019
By:
- Ng, Kay W. P.;
- DIETZ, Alexander R.;
- Johnson, Ryan;
- Shoykhet, Michael;
- Zaidman, Craig M.
Publication type:
journal article
Nerve ultrasound in polyneuropathies.
Published in:
2018
By:
- Telleman, Johan A.;
- Grimm, Alexander;
- Goedee, Stephan;
- Visser, Leo H.;
- Zaidman, Craig M.
Publication type:
journal article
Nerve ultrasound reliability of upper limbs: Effects of examiner training.
Published in:
2018
By:
- Garcia‐Santibanez, Rocio;
- Dietz, Alexander R.;
- Bucelli, Robert C.;
- Zaidman, Craig M.;
- Garcia-Santibanez, Rocio
Publication type:
journal article
Serial diaphragm ultrasound studies in neuralgic amyotrophy with bilateral phrenic neuropathies.
Published in:
2017
By:
- Garcia‐Santibanez, Rocio;
- Zaidman, Craig M.;
- Russell, Tonya;
- Bucelli, Robert C.;
- Garcia-Santibanez, Rocio
Publication type:
journal article
Intramuscular blood flow quantification with power doppler ultrasonography.
Published in:
2016
By:
- Dori, Amir;
- Abbasi, Hiba;
- Zaidman, Craig M.
Publication type:
journal article
Clinical trial readiness in non-ambulatory boys and men with duchenne muscular dystrophy: MDA-DMD network follow-up.
Published in:
2016
By:
- Connolly, Anne M.;
- Florence, Julaine M.;
- Zaidman, Craig M.;
- Golumbek, Paul T.;
- Mendell, Jerry R.;
- Flanigan, Kevin M.;
- Karachunski, Peter I.;
- Day, John W.;
- McDonald, Craig M.;
- Darras, Basil T.;
- Kang, Peter B.;
- Siener, Catherine A.;
- Gadeken, Rebecca K.;
- Anand, Pallavi;
- Schierbecker, Jeanine R.;
- Malkus, Elizabeth C.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Johnson, Linda;
- Nicorici, Alina
Publication type:
journal article
Nerve ultrasound identifies abnormalities in the posterior interosseous nerve in patients with proximal radial neuropathies.
Published in:
2016
By:
- Dietz, Alexander R.;
- Bucelli, Robert C.;
- Pestronk, Alan;
- Zaidman, Craig M.
Publication type:
journal article
Muscle ultrasound quantifies disease progression over time in infants and young boys with duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2015, v. 52, n. 3, p. 334, doi. 10.1002/mus.24609
By:
- Zaidman, Craig M.;
- Malkus, Elizabeth C.;
- Connolly, Anne M.
Publication type:
Article
Electrical impedance myography in Duchenne muscular dystrophy and healthy controls: A multicenter study of reliability and validity.
Published in:
2015
By:
- Zaidman, Craig M.;
- Wang, Lucy L.;
- Connolly, Anne M.;
- Florence, Julaine;
- Wong, Brenda L.;
- Parsons, Julie A.;
- Apkon, Susan;
- Goyal, Namita;
- Williams, Eugene;
- Escolar, Diana;
- Rutkove, Seward B.;
- Bohorquez, Jose L.
Publication type:
journal article
Outcome reliability in non-Ambulatory Boys/Men with duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2015, v. 51, n. 4, p. 522, doi. 10.1002/mus.24346
By:
- Connolly, Anne M.;
- Malkus, Elizabeth C.;
- Mendell, Jerry R.;
- Flanigan, Kevin M.;
- Miller, J. Philip;
- Schierbecker, Jeanine R.;
- Siener, Catherine A.;
- Golumbek, Paul T.;
- Zaidman, Craig M.;
- Mcdonald, Craig M.;
- Johnson, Linda;
- Nicorici, Alina;
- Karachunski, Peter I.;
- Day, John W.;
- Kelecic, Jason M.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Darras, Basil T.;
- Kang, Peter B.;
- Quigley, Janet
Publication type:
Article
Quantitative muscle ultrasound in Duchenne muscular dystrophy: A comparison of techniques.
Published in:
Muscle & Nerve, 2015, v. 51, n. 2, p. 207, doi. 10.1002/mus.24296
By:
- Shklyar, Irina;
- Geisbush, Tom R.;
- Mijialovic, Aleksandar S.;
- Pasternak, Amy;
- Darras, Basil T.;
- Wu, Jim S.;
- Rutkove, Seward B.;
- Zaidman, Craig M.
Publication type:
Article
Nerve size in chronic inflammatory demyelinating neuropathy varies with disease activity and therapy response over time: A retrospective ultrasound study.
Published in:
Muscle & Nerve, 2014, v. 50, n. 5, p. 733, doi. 10.1002/mus.24227
By:
- Zaidman, Craig M.;
- Pestronk, Alan
Publication type:
Article
Minimal training is required to reliably perform quantitative ultrasound of muscle.
Published in:
Muscle & Nerve, 2014, v. 50, n. 1, p. 124, doi. 10.1002/mus.24117
By:
- Zaidman, Craig m.;
- WU, JIM S.;
- Wilder, Sarah;
- Darras, Basil T.;
- Rutkove, Seward B.
Publication type:
Article
Coenzyme Q10 deficiency in children: Frequent type 2C muscle fibers with normal morphology.
Published in:
2013
By:
- Sommerville, R Brian;
- Zaidman, Craig M;
- Pestronk, Alan
Publication type:
Journal Article
Coenzyme Q<sub>10</sub> deficiency in children: Frequent type 2C muscle fibers with normal morphology.
Published in:
Muscle & Nerve, 2013, v. 48, n. 5, p. 722, doi. 10.1002/mus.23837
By:
- Sommerville, R. Brian;
- Zaidman, Craig M.;
- Pestronk, Alan
Publication type:
Article
Newborn brachial plexus palsy: Evaluation of severity using quantitative ultrasound of muscle.
Published in:
Muscle & Nerve, 2013, v. 47, n. 2, p. 246, doi. 10.1002/mus.23518
By:
- Zaidman, Craig M.;
- Holland, Mark R.;
- Noetzel, Michael J.;
- Park, Tae Sung;
- Pestronk, Alan
Publication type:
Article
Qualitative and quantitative skeletal muscle ultrasound in late-onset acid maltase deficiency.
Published in:
Muscle & Nerve, 2011, v. 44, n. 3, p. 418, doi. 10.1002/mus.22088
By:
- Zaidman, Craig M.;
- Malkus, Elizabeth C.;
- Siener, Catherine;
- Florence, Julaine;
- Pestronk, Alan;
- Al-Lozi, Muhammad
Publication type:
Article
Peripheral nerve size in normals and patients with polyneuropathy: An ultrasound study.
Published in:
Muscle & Nerve, 2009, v. 40, n. 6, p. 960, doi. 10.1002/mus.21431
By:
- Zaidman, Craig M.;
- Al-Lozi, Mohammed;
- Pestronk, Alan
Publication type:
Article
Calibrated quantitative ultrasound imaging of skeletal muscle using backscatter analysis.
Published in:
Muscle & Nerve, 2008, v. 38, n. 1, p. 893, doi. 10.1002/mus.21052
By:
- Zaidman, Craig M.;
- Holland, Mark R.;
- Anderson, Christian C.;
- Pestronk, Alan
Publication type:
Article
Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial.
Published in:
JAMA Neurology, 2020, v. 77, n. 8, p. 982, doi. 10.1001/jamaneurol.2020.1264
By:
- Clemens, Paula R.;
- Rao, Vamshi K.;
- Connolly, Anne M.;
- Harper, Amy D.;
- Mah, Jean K.;
- Smith, Edward C.;
- McDonald, Craig M.;
- Zaidman, Craig M.;
- Morgenroth, Lauren P.;
- Osaki, Hironori;
- Satou, Youhei;
- Yamashita, Taishi;
- Hoffman, Eric P.
Publication type:
Article
Medical management of muscle weakness in Duchenne muscular dystrophy.
Published in:
PLoS ONE, 2020, v. 15, n. 10, p. 1, doi. 10.1371/journal.pone.0240687
By:
- Rivera, Sarah R.;
- Jhamb, Sumit K.;
- Abdel-Hamid, Hoda Z.;
- Acsadi, Gyula;
- Brandsema, John;
- Ciafaloni, Emma;
- Darras, Basil T.;
- Iannaccone, Susan T.;
- Konersman, Chamindra G.;
- Kuntz, Nancy L.;
- McDonald, Craig M.;
- Parsons, Julie A.;
- Tesi Rocha, Carolina;
- Zaidman, Craig M.;
- Butterfield, Russell J.;
- Connolly, Anne M.;
- Mathews, Katherine D.
Publication type:
Article
Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy.
Published in:
Journal of Neuromuscular Diseases, 2024, v. 11, n. 3, p. 687, doi. 10.3233/JND-230185
By:
- Zaidman, Craig M.;
- Goedeker, Natalie L.;
- Aqul, Amal A.;
- Butterfield, Russell J.;
- Connolly, Anne M.;
- Crystal, Ronald G.;
- Godwin, Kara E.;
- Hor, Kan N.;
- Mathews, Katherine D.;
- Proud, Crystal M.;
- Kula Smyth, Elizabeth;
- Veerapandiyan, Aravindhan;
- Watkins, Paul B.;
- Mendell, Jerry R.
Publication type:
Article
Pamrevlumab, a Fully Human Monoclonal Antibody Targeting Connective Tissue Growth Factor, for Non-Ambulatory Patients with Duchenne Muscular Dystrophy.
Published in:
Journal of Neuromuscular Diseases, 2023, v. 10, n. 4, p. 685, doi. 10.3233/JND-230019
By:
- Connolly, Anne M.;
- Zaidman, Craig M.;
- Brandsema, John F.;
- Phan, Han C.;
- Tian, Cuixia;
- Zhang, Xueping;
- Li, Jack;
- Eisner, Mark D.;
- Carrier, Ewa
Publication type:
Article
Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy: Results From the Phase 2, Open-Label, 4-Year Extension Study.
Published in:
Journal of Neuromuscular Diseases, 2023, v. 10, n. 3, p. 439, doi. 10.3233/JND-221656
By:
- Clemens, Paula R.;
- Rao, Vamshi K.;
- Connolly, Anne M.;
- Harper, Amy D.;
- Mah, Jean K.;
- McDonald, Craig M.;
- Smith, Edward C.;
- Zaidman, Craig M.;
- Nakagawa, Tomoyuki;
- Hoffman, Eric P.
Publication type:
Article
Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG).
Published in:
Journal of Neuromuscular Diseases, 2023, v. 10, n. 3, p. 389, doi. 10.3233/JND-221560
By:
- Finkel, Richard S.;
- Darras, Basil T.;
- Mendell, Jerry R.;
- Day, John W.;
- Kuntz, Nancy L.;
- Connolly, Anne M.;
- Zaidman, Craig M.;
- Crawford, Thomas O.;
- Butterfield, Russell J.;
- Shieh, Perry B.;
- Tennekoon, Gihan;
- Brandsema, John F.;
- Iannaccone, Susan T.;
- Shoffner, John;
- Kavanagh, Sarah;
- Macek, Thomas A.;
- Tauscher-Wisniewski, Sitra
Publication type:
Article
Long-Term Functional Efficacy and Safety of Viltolarsen in Patients with Duchenne Muscular Dystrophy.
Published in:
Journal of Neuromuscular Diseases, 2022, v. 9, n. 4, p. 493, doi. 10.3233/JND-220811
By:
- Clemens, Paula R.;
- Rao, Vamshi K.;
- Connolly, Anne M.;
- Harper, Amy D.;
- Mah, Jean K.;
- McDonald, Craig M.;
- Smith, Edward C.;
- Zaidman, Craig M.;
- Nakagawa, Tomoyuki;
- Hoffman, Eric P.
Publication type:
Article
Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study SRP‐9001‐103 (ENDEAVOR).
Published in:
Annals of Neurology, 2023, v. 94, n. 5, p. 955, doi. 10.1002/ana.26755
By:
- Zaidman, Craig M.;
- Proud, Crystal M.;
- McDonald, Craig M.;
- Lehman, Kelly J.;
- Goedeker, Natalie L.;
- Mason, Stefanie;
- Murphy, Alexander P.;
- Guridi, Maitea;
- Wang, Shufang;
- Reid, Carol;
- Darton, Eddie;
- Wandel, Christoph;
- Lewis, Sarah;
- Malhotra, Jyoti;
- Griffin, Danielle A.;
- Potter, Rachael A.;
- Rodino‐Klapac, Louise R.;
- Mendell, Jerry R.
Publication type:
Article
Quantitative muscle ultrasound detects disease progression in Duchenne muscular dystrophy.
Published in:
2017
By:
- Zaidman, Craig M.;
- Wu, Jim S.;
- Kapur, Kush;
- Pasternak, Amy;
- Madabusi, Lavanya;
- Yim, Sung;
- Pacheck, Adam;
- Szelag, Heather;
- Harrington, Tim;
- Darras, Basil T.;
- Rutkove, Seward B.
Publication type:
journal article
Electrical impedance myography for assessment of Duchenne muscular dystrophy.
Published in:
2017
By:
- Rutkove, Seward B.;
- Kapur, Kush;
- Zaidman, Craig M.;
- Wu, Jim S.;
- Pasternak, Amy;
- Madabusi, Lavanya;
- Yim, Sung;
- Pacheck, Adam;
- Szelag, Heather;
- Harrington, Tim;
- Darras, Basil T.
Publication type:
journal article
Immune-mediated myositis following gene therapy for Duchenne muscular dystrophy: a case report.
Published in:
Journal of Neurology, 2024, v. 271, n. 8, p. 5659, doi. 10.1007/s00415-024-12431-z
By:
- Iannaccone, Susan T.;
- Cai, Chunyu;
- Rhem, Brittney;
- Batley, Kaitlin;
- Rajaram, Veena;
- Greenberg, Benjamin M.;
- Dharia, Sachi;
- Zaidman, Craig M.
Publication type:
Article
CANOMAD and other chronic ataxic neuropathies with disialosyl antibodies (CANDA).
Published in:
Journal of Neurology, 2018, v. 265, n. 6, p. 1402, doi. 10.1007/s00415-018-8853-4
By:
- Garcia-Santibanez, Rocio;
- Zaidman, Craig M.;
- Sommerville, R. Brian;
- Lopate, Glenn;
- Weihl, Conrad C.;
- Pestronk, Alan;
- Bucelli, Robert C.
Publication type:
Article
Ultrasound of inherited vs. acquired demyelinating polyneuropathies.
Published in:
Journal of Neurology, 2013, v. 260, n. 12, p. 3115, doi. 10.1007/s00415-013-7123-8
By:
- Zaidman, Craig M.;
- Harms, Matthew B.;
- Pestronk, Alan
Publication type:
Article
Newborn Screening for Spinal Muscular Atrophy: Variations in Practice and Early Management of Infants with Spinal Muscular Atrophy in the United States.
Published in:
International Journal of Neonatal Screening (IJNS), 2024, v. 10, n. 3, p. 58, doi. 10.3390/ijns10030058
By:
- Zaidman, Craig M.;
- Crockett, Cameron D.;
- Wedge, Ethan;
- Tabatabai, Grace;
- Goedeker, Natalie
Publication type:
Article
The Use of Nerve Transfers to Restore Upper Extremity Function in Cervical Spinal Cord Injury.
Published in:
2018
By:
- Fox, Ida K.;
- Novak, Christine B.;
- Krauss, Emily M.;
- Hoben, Gwendolyn M.;
- Zaidman, Craig M.;
- Ruvinskaya, Rimma;
- Juknis, Neringa;
- Winter, Anke C.;
- Mackinnon, Susan E.
Publication type:
journal article
Childhood Graves Disease Masquerading as Myasthenia Gravis.
Published in:
Journal of Child Neurology, 2013, v. 28, n. 10, p. 1309, doi. 10.1177/0883073812457460
By:
- Perlman, Seth J.;
- Zaidman, Craig M.
Publication type:
Article
Intron mutations and early transcription termination in Duchenne and Becker muscular dystrophy.
Published in:
Human Mutation, 2022, v. 43, n. 4, p. 511, doi. 10.1002/humu.24343
By:
- Waldrop, Megan A.;
- Moore, Steven A.;
- Mathews, Katherine D.;
- Darbro, Benjamin W.;
- Medne, Livja;
- Finkel, Richard;
- Connolly, Anne M.;
- Crawford, Thomas O.;
- Drachman, Daniel;
- Wein, Nicolas;
- Habib, Ali A.;
- Krzesniak‐Swinarska, Monika A.;
- Zaidman, Craig M.;
- Collins, James J.;
- Jokela, Manu;
- Udd, Bjarne;
- Day, John W.;
- Ortiz‐Guerrero, Gloria;
- Statland, Jeff;
- Butterfield, Russell J.
Publication type:
Article
Muscle atrophy in mechanically-ventilated critically ill children.
Published in:
PLoS ONE, 2018, v. 13, n. 12, p. 1, doi. 10.1371/journal.pone.0207720
By:
- Johnson, Ryan W.;
- Ng, Kay W. P.;
- Dietz, Alexander R.;
- Hartman, Mary E.;
- Baty, Jack D.;
- Hasan, Nausheen;
- Zaidman, Craig M.;
- Shoykhet, Michael
Publication type:
Article

Found: 46