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Dystrophin R16/17 protein therapy restores sarcolemmal nNOS in trans and improves muscle perfusion and function.
- Published in:
- Molecular Medicine, 2019, v. 25, n. 1, p. N.PAG, doi. 10.1186/s10020-019-0101-6
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- Publication type:
- Article
Viral serotype and the transgene sequence influence overlapping adeno-associated viral (AAV) vector-mediated gene transfer in skeletal muscle.
- Published in:
- Journal of Gene Medicine, 2006, v. 8, n. 3, p. 298, doi. 10.1002/jgm.835
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- Publication type:
- Article
Microdystrophin Ameliorates Muscular Dystrophy in the Canine Model of Duchenne Muscular Dystrophy.
- Published in:
- Molecular Therapy, 2013, v. 21, n. 4, p. 750, doi. 10.1038/mt.2012.283
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- Publication type:
- Article
Partial restoration of cardiac function with ΔPDZ nNOS in aged mdx model of Duchenne cardiomyopathy.
- Published in:
- Human Molecular Genetics, 2014, v. 23, n. 12, p. 3189, doi. 10.1093/hmg/ddu029
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- Publication type:
- Article
Dual AAV therapy ameliorates exercise-induced muscle injury and functional ischemia in murine models of Duchenne muscular dystrophy.
- Published in:
- Human Molecular Genetics, 2013, v. 22, n. 18, p. 3720, doi. 10.1093/hmg/ddt224
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- Publication type:
- Article
Exclusive skeletal muscle correction does not modulate dystrophic heart disease in the aged mdx model of Duchenne cardiomyopathy.
- Published in:
- Human Molecular Genetics, 2013, v. 22, n. 13, p. 2634, doi. 10.1093/hmg/ddt112
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- Publication type:
- Article
Sub-physiological sarcoglycan expression contributes to compensatory muscle protection in mdx mice.
- Published in:
- Human Molecular Genetics, 2009, v. 18, n. 7, p. 1209, doi. 10.1093/hmg/ddp015
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- Publication type:
- Article
Full-length dystrophin expression in half of the heart cells ameliorates β-isoproterenol-induced cardiomyopathy in mdx mice.
- Published in:
- Human Molecular Genetics, 2004, v. 13, n. 15, p. 1669, doi. 10.1093/hmg/ddh174
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- Publication type:
- Article
A novel genetic model provides a unique perspective on the relationship between postexercise glycogen concentration and increases in the abundance of key metabolic proteins after acute exercise.
- Published in:
- PLoS ONE, 2024, v. 19, n. 1, p. 1, doi. 10.1371/journal.pone.0295964
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- Publication type:
- Article
AAV-microdystrophin Therapy Improves Cardiac Performance in Aged Female mdx Mice.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 10, p. 1826, doi. 10.1038/mt.2011.154
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- Publication type:
- Article
Evidence for the Failure of Adeno-associated Virus Serotype 5 to Package a Viral Genome ≥8.2 kb.
- Published in:
- Molecular Therapy, 2010, v. 18, n. 1, p. 75, doi. 10.1038/mt.2009.256
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- Publication type:
- Article
Cardiac Expression of a Mini-dystrophin That Normalizes Skeletal Muscle Force Only Partially Restores Heart Function in Aged Mdx Mice.
- Published in:
- Molecular Therapy, 2009, v. 17, n. 2, p. 253, doi. 10.1038/mt.2008.264
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- Publication type:
- Article
A Single Intravenous Injection of Adeno-associated Virus Serotype-9 Leads to Whole Body Skeletal Muscle Transduction in Dogs.
- Published in:
- Molecular Therapy, 2008, v. 16, n. 12, p. 1944, doi. 10.1038/mt.2008.207
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- Publication type:
- Article
A Hybrid Vector System Expands Adeno-associated Viral Vector Packaging Capacity in a Transgene-independent Manner.
- Published in:
- Molecular Therapy, 2008, v. 16, n. 1, p. 124, doi. 10.1038/sj.mt.6300322
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- Publication type:
- Article
Efficient Whole-body Transduction with Trans-splicing Adeno-associated Viral Vectors.
- Published in:
- 2007
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- Publication type:
- Bibliography
Efficient Whole-body Transduction with Trans-splicing Adeno-associated Viral Vectors.
- Published in:
- Molecular Therapy, 2007, v. 15, n. 4, p. 750, doi. 10.1038/sj.mt.6300081
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- Publication type:
- Article
C-Terminal-Truncated Microdystrophin Recruits Dystrobrevin and Syntrophin to the Dystrophin-Associated Glycoprotein Complex and Reduces Muscular Dystrophy in Symptomatic Utrophin/Dystrophin Double-Knockout Mice.
- Published in:
- Molecular Therapy, 2006, v. 14, n. 1, p. 79, doi. 10.1016/j.ymthe.2006.01.007
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- Publication type:
- Article
911. C-Terminal Truncated Microdystrophin Recruits Dystrobrevin and Syntrophin to the Dystrophin-Associated Glycoprotein Complex and Reduces Muscular Dystrophy in Symptomatic Utrophin/Dystrophin Double Knock-Out Mice.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S351, doi. 10.1016/j.ymthe.2006.08.1001
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- Publication type:
- Article
740. A Novel Hybrid System Efficiently Expands AAV Packaging Capacity.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S286, doi. 10.1016/j.ymthe.2006.08.822
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- Publication type:
- Article
793. Efficient Expression of the 6 kb Mini-Dystrophin Gene by Trans-Splicing Adeno-Associated Viral (AAV) Vector Restores the Entire Dystrophin-Associated Glycoprotein Complex and Reduces Contraction-Induced Damage in the Mdx Mouse Model of Duchenne Muscular Dystrophy
- Published in:
- 2005
- By:
- Publication type:
- Abstract
688. Adno-Associated Virus (AAV)-Mediated Catalase Overexpression Protects the Extensor Digitorum Longous Muscle from Contraction-Induced Injury
- Published in:
- 2005
- By:
- Publication type:
- Abstract
515. Overlapping Adeno-Associated Viral (AAV) Vector Mediated Gene Transfer Is Dependent on Viral Serotype and the Transgene Sequence in Skeletal Muscle
- Published in:
- 2005
- By:
- Publication type:
- Abstract
Adeno-Associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury
- Published in:
- Molecular Therapy, 2005, v. 11, n. 2, p. 245, doi. 10.1016/j.ymthe.2004.09.013
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- Publication type:
- Article
Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors.
- Published in:
- Nature Biotechnology, 2005, v. 23, n. 11, p. 1435, doi. 10.1038/nbt1153
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- Publication type:
- Article
Characterization of 65 Epitope-Specific Dystrophin Monoclonal Antibodies in Canine and Murine Models of Duchenne Muscular Dystrophy by Immunostaining and Western Blot.
- Published in:
- PLoS ONE, 2014, v. 9, n. 2, p. 1, doi. 10.1371/journal.pone.0088280
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- Publication type:
- Article
Marginal Level Dystrophin Expression Improves Clinical Outcome in a Strain of Dystrophin/Utrophin Double Knockout Mice.
- Published in:
- PLoS ONE, 2010, v. 5, n. 12, p. 1, doi. 10.1371/journal.pone.0015286
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- Publication type:
- Article
Ectopic Catalase Expression in Mitochondria by Adeno- Associated Virus Enhances Exercise Performance in Mice.
- Published in:
- PLoS ONE, 2009, v. 4, n. 8, p. 1, doi. 10.1371/journal.pone.0006673
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- Publication type:
- Article
Nitrosative stress elicited by nNOSµ delocalization inhibits muscle force in dystrophin-null mice.
- Published in:
- Journal of Pathology, 2011, v. 223, n. 1, p. 88, doi. 10.1002/path.2799
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- Publication type:
- Article
SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice.
- Published in:
- 2011
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- Publication type:
- journal article
Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models.
- Published in:
- Nature Communications, 2021, v. 12, n. 1, p. 1, doi. 10.1038/s41467-021-26830-7
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- Publication type:
- Article
Dystrophin R16/17-syntrophin PDZ fusion protein restores sarcolemmal nNOSμ.
- Published in:
- Skeletal Muscle, 2018, v. 8, n. 1, p. N.PAG, doi. 10.1186/s13395-018-0182-x
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- Publication type:
- Article
Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.
- Published in:
- Journal of Clinical Investigation, 2009, v. 119, n. 3, p. 624, doi. 10.1172/JCI36612
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- Publication type:
- Article
A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation.
- Published in:
- Nature Medicine, 2000, v. 6, n. 5, p. 595, doi. 10.1038/75080
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- Publication type:
- Article
Dwarf Open Reading Frame (DWORF) Gene Therapy Ameliorated Duchenne Muscular Dystrophy Cardiomyopathy in Aged mdx Mice.
- Published in:
- Journal of the American Heart Association, 2023, v. 12, n. 3, p. 1, doi. 10.1161/JAHA.122.027480
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- Publication type:
- Article
Proteomic analysis identifies key differences in the cardiac interactomes of dystrophin and micro-dystrophin.
- Published in:
- Human Molecular Genetics, 2021, v. 30, n. 14, p. 1321, doi. 10.1093/hmg/ddab133
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- Publication type:
- Article
Dystrophin contains multiple independent membrane-binding domains.
- Published in:
- Human Molecular Genetics, 2016, v. 25, n. 17, p. 3647, doi. 10.1093/hmg/ddw210
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- Publication type:
- Article
Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype.
- Published in:
- Human Molecular Genetics, 2016, v. 25, n. 13, p. 2633, doi. 10.1093/hmg/ddw123
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- Publication type:
- Article
Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus.
- Published in:
- Human Molecular Genetics, 2015, v. 24, n. 20, p. 5880, doi. 10.1093/hmg/ddv310
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- Publication type:
- Article
Gender influences cardiac function in the mdx model of duchenne cardiomyopathy.
- Published in:
- Muscle & Nerve, 2010, v. 42, n. 4, p. 600, doi. 10.1002/mus.21763
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- Publication type:
- Article
Catalase overexpression does not impair extensor digitorum longus muscle function in normal mice.
- Published in:
- Muscle & Nerve, 2007, v. 36, n. 6, p. 833, doi. 10.1002/mus.20874
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- Publication type:
- Article