Found: 7
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In vitro metabolism, reaction phenotyping, enzyme kinetics, CYP inhibition and induction potential of ataluren.
- Published in:
- Pharmacology Research & Perspectives, 2020, v. 8, n. 2, p. 1, doi. 10.1002/prp2.576
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- Article
An internal open reading frame triggers nonsense-mediated decay of the yeast SPT10 mRNA.
- Published in:
- EMBO Journal, 1999, v. 18, n. 21, p. 6134, doi. 10.1093/emboj/18.21.6134
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- Article
PTC124 targets genetic disorders caused by nonsense mutations.
- Published in:
- Nature, 2007, v. 447, n. 7140, p. 87, doi. 10.1038/nature05756
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- Article
Corrigendum to: Pharmacologically-induced mouse model of adult spinal muscular atrophy to evaluate effectiveness of therapeutics after disease onset.
- Published in:
- Human Molecular Genetics, 2021, v. 30, n. 9, p. 843, doi. 10.1093/hmg/ddaa247
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- Article
Pharmacokinetics, pharmacodynamics, and efficacy of a small-molecule SMN2 splicing modifier in mouse models of spinal muscular atrophy.
- Published in:
- Human Molecular Genetics, 2016, v. 25, n. 10, p. 1885, doi. 10.1093/hmg/ddw062
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- Article
Pharmacologically induced mouse model of adult spinal muscular atrophy to evaluate effectiveness of therapeutics after disease onset.
- Published in:
- Human Molecular Genetics, 2016, v. 25, n. 5, p. 964, doi. 10.1093/hmg/ddv629
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- Publication type:
- Article
The minor gentamicin complex component, X2, is a potent premature stop codon readthrough molecule with therapeutic potential.
- Published in:
- PLoS ONE, 2018, v. 13, n. 10, p. 1, doi. 10.1371/journal.pone.0206158
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- Article