Works by Wasserstein, M.


Results: 9
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    PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL.

    Published in:
    HemaSphere, 2022, v. 6, p. 2183, doi. 10.1097/01.HS9.0000852080.43506.a5
    By:
    • Villarrubia, J.;
    • Wasserstein, M.;
    • Barbato, A.;
    • Gallagher, R. C.;
    • Giugliani, R.;
    • Guelbert, N. B.;
    • Hennermann, J. B.;
    • Hollak, C.;
    • Ikezoe, T.;
    • Lachmann, R.;
    • Lidove, O.;
    • Mabe, P.;
    • Mengel, E.;
    • Scarpa, M.;
    • Senates, E.;
    • Tchan, M.;
    • Thurberg, B. L.;
    • Yarramaneni, A.;
    • Rawlings, A. M.;
    • Kim, Y.
    Publication type:
    Article
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    Automated extraction of functional biomarkers of verbal and ambulatory ability from multi-institutional clinical notes using large language models.

    Published in:
    Journal of Neurodevelopmental Disorders, 2025, v. 17, n. 1, p. 1, doi. 10.1186/s11689-025-09612-w
    By:
    • Kaster, Levi;
    • Hillis, Ethan;
    • Oh, Inez Y.;
    • Aravamuthan, Bhooma R.;
    • Lanzotti, Virginia C.;
    • Vickstrom, Casey R.;
    • Wasserstein, M;
    • Chopra, M;
    • Sahin, M;
    • Wangler, M;
    • Schultz, B;
    • Izumi, K;
    • Bergner, S;
    • Gropman, A;
    • Smith-Hicks, C;
    • Abbeduto, L;
    • Hazlett, H;
    • Doherty, D;
    • German, K;
    • DaWalt, L
    Publication type:
    Article
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