Works matching AU Thrasher, Adrian J.


Results: 133
    1

    Catechins and antitumor immunity.

    Published in:
    OncoImmunology, 2013, v. 2, n. 6, p. e24443-1, doi. 10.4161/onci.24443
    By:
    • Santilli, Giorgia;
    • Anderson, John;
    • Thrasher, Adrian J.;
    • Sala, Arturo
    Publication type:
    Article
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    Effective gene therapy with nonintegrating lentiviral vectors.

    Published in:
    Nature Medicine, 2006, v. 12, n. 3, p. 348, doi. 10.1038/nm1365
    By:
    • Yáñez-Muñoz, Rafael J.;
    • Balaggan, Kamaljit S.;
    • MacNeil, Angus;
    • Howe, Steven J.;
    • Schmidt, Manfred;
    • Smith, Alexander J.;
    • Buch, Prateek;
    • MacLaren, Robert E.;
    • Anderson, Patrick N.;
    • Barker, Susie E.;
    • Duran, Yanai;
    • Bartholomae, Cynthia;
    • von Kalle, Christof;
    • Heckenlively, John R.;
    • Kinnon, Christine;
    • Ali, Robin R.;
    • Thrasher, Adrian J.
    Publication type:
    Article
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    A phagocyte dilemma...

    Published in:
    Nature Immunology, 2011, v. 12, n. 3, p. 201, doi. 10.1038/ni0311-201
    By:
    • Thrasher, Adrian J;
    • Segal, Anthony W
    Publication type:
    Article
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    Gene therapy for primary immunodeficiency.

    Published in:
    Human Molecular Genetics, 2019, v. 28, p. R15, doi. 10.1093/hmg/ddz170
    By:
    • Booth, Claire;
    • Romano, Rosa;
    • Roncarolo, Maria Grazia;
    • Thrasher, Adrian J
    Publication type:
    Article
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    Patients with T<sup>+/low</sup> NK<sup>+</sup> IL-2 receptor γ chain deficiency have differentially-impaired cytokine signaling resulting in severe combined immunodeficiency.

    Published in:
    European Journal of Immunology, 2014, v. 44, n. 10, p. 3129, doi. 10.1002/eji.201444689
    By:
    • Fuchs, Sebastian;
    • Rensing‐Ehl, Anne;
    • Erlacher, Miriam;
    • Vraetz, Thomas;
    • Hartjes, Lara;
    • Janda, Ales;
    • Rizzi, Marta;
    • Lorenz, Myriam R.;
    • Gilmour, Kimberly;
    • Saint‐Basile, Geneviève;
    • Roifman, Chaim M.;
    • Cheuk, Steven;
    • Gennery, Andrew;
    • Thrasher, Adrian J.;
    • Fuchs, Ilka;
    • Schwarz, Klaus;
    • Speckmann, Carsten;
    • Ehl, Stephan
    Publication type:
    Article
    20
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    Restoring the natural tropism of AAV2 vectors for human liver.

    Published in:
    Science Translational Medicine, 2020, v. 12, n. 560, p. 1, doi. 10.1126/scitranslmed.aba3312
    By:
    • Cabanes-Creus, Marti;
    • Hallwirth, Claus V.;
    • Westhaus, Adrian;
    • Ng, Boaz H.;
    • Liao, Sophia H.Y.;
    • Zhu, Erhua;
    • Navarro, Renina Gale;
    • Baltazar, Grober;
    • Drouyer, Matthieu;
    • Scott, Suzanne;
    • Logan, Grant J.;
    • Santilli, Giorgia;
    • Bennett, Antonette;
    • Ginn, Samantha L.;
    • McCaughan, Geoff;
    • Thrasher, Adrian J.;
    • Agbandje-McKenna, Mavis;
    • Alexander, Ian E.;
    • Lisowski, Leszek
    Publication type:
    Article
    22

    Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy.

    Published in:
    2007
    By:
    • Deichmann, Annette;
    • Hacein-Bey-Abina, Salima;
    • Schmidt, Manfred;
    • Garrigue, Alexandrine;
    • Brugman, Martijn H.;
    • Jingqiong Hu;
    • Glimm, Hanno;
    • Gyapay, Gabor;
    • Prum, Bernard;
    • Fraser, Christopher C.;
    • Fischer, Nicolas;
    • Schwarzwaelder, Kerstin;
    • Siegler, Maria-Luise;
    • de Ridder, Dick;
    • Pike-Overzet, Karin;
    • Howe, Steven J.;
    • Thrasher, Adrian J.;
    • Wagemaker, Gerard;
    • Abel, Ulrich;
    • Staal, Frank J. T.
    Publication type:
    journal article
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    Lentiviral vectors can be used for full-length dystrophin gene therapy.

    Published in:
    Scientific Reports, 2017, p. 44775, doi. 10.1038/srep44775
    By:
    • Counsell, John R.;
    • Asgarian, Zeinab;
    • Meng, Jinhong;
    • Ferrer, Veronica;
    • Vink, Conrad A.;
    • Howe, Steven J.;
    • Waddington, Simon N.;
    • Thrasher, Adrian J.;
    • Muntoni, Francesco;
    • Morgan, Jennifer E.;
    • Danos, Olivier
    Publication type:
    Article
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    WASP-mediated regulation of anti-inflammatory macrophages is IL-10 dependent and is critical for intestinal homeostasis.

    Published in:
    Nature Communications, 2018, v. 9, n. 1, p. 1, doi. 10.1038/s41467-018-03670-6
    By:
    • Biswas, Amlan;
    • Shouval, Dror S.;
    • Griffith, Alexandra;
    • Goettel, Jeremy A.;
    • Field, Michael;
    • Yu Hui Kang;
    • Konnikova, Liza;
    • Janssen, Erin;
    • Redhu, Naresh Singh;
    • Thrasher, Adrian J.;
    • Chatila, Talal;
    • Kuchroo, Vijay K.;
    • Geha, Raif S.;
    • Notarangelo, Luigi D.;
    • Sung-Yun Pai;
    • Horwitz, Bruce H.;
    • Snapper, Scott B.
    Publication type:
    Article
    28

    Out of harm's way.

    Published in:
    2011
    By:
    • Williams, David A.;
    • Thrasher, Adrian J.
    Publication type:
    Opinion
    29

    RISC control for gene therapy.

    Published in:
    Nature Biotechnology, 2006, v. 24, n. 6, p. 661, doi. 10.1038/nbt0606-661
    By:
    • Qasim, Waseem;
    • Thrasher, Adrian J.
    Publication type:
    Article
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    The cytoplasm of living cells behaves as a poroelastic material.

    Published in:
    Nature Materials, 2013, v. 12, n. 3, p. 253, doi. 10.1038/nmat3517
    By:
    • Moeendarbary, Emad;
    • Valon, Léo;
    • Fritzsche, Marco;
    • Harris, Andrew R.;
    • Moulding, Dale A.;
    • Thrasher, Adrian J.;
    • Stride, Eleanor;
    • Mahadevan, L.;
    • Charras, Guillaume T.
    Publication type:
    Article
    40

    FOXP3+ Tregs require WASP to restrain Th2-mediated food allergy.

    Published in:
    2016
    By:
    • Lexmond, Willem S.;
    • Goettel, Jeremy A.;
    • Lyons, Jonathan J.;
    • Jacobse, Justin;
    • Deken, Marion M.;
    • Lawrence, Monica G.;
    • DiMaggio, Thomas H.;
    • Kotlarz, Daniel;
    • Garabedian, Elizabeth;
    • Sackstein, Paul;
    • Nelson, Celeste C.;
    • Jones, Nina;
    • Stone, Kelly D.;
    • Candotti, Fabio;
    • Rings, Edmond H. H. M.;
    • Thrasher, Adrian J.;
    • Milner, Joshua D.;
    • Snapper, Scott B.;
    • Fiebiger, Edda
    Publication type:
    journal article
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    Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency.

    Published in:
    Molecular Therapy, 2014, v. 22, n. 3, p. 607, doi. 10.1038/mt.2013.265
    By:
    • Carbonaro, Denise A;
    • Zhang, Lin;
    • Jin, Xiangyang;
    • Montiel-Equihua, Claudia;
    • Geiger, Sabine;
    • Carmo, Marlene;
    • Cooper, Aaron;
    • Fairbanks, Lynette;
    • Kaufman, Michael L;
    • Sebire, Neil J;
    • Hollis, Roger P;
    • Blundell, Michael P;
    • Senadheera, Shantha;
    • Fu, Pei-Yu;
    • Sahaghian, Arineh;
    • Chan, Rebecca Y;
    • Wang, Xiaoyan;
    • Cornetta, Kenneth;
    • Thrasher, Adrian J;
    • Kohn, Donald B
    Publication type:
    Article
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    Valproic Acid Confers Functional Pluripotency to Human Amniotic Fluid Stem Cells in a Transgene-free Approach.

    Published in:
    Molecular Therapy, 2012, v. 20, n. 10, p. 1953, doi. 10.1038/mt.2012.117
    By:
    • Moschidou, Dafni;
    • Mukherjee, Sayandip;
    • Blundell, Michael P;
    • Drews, Katharina;
    • Jones, Gemma N;
    • Abdulrazzak, Hassan;
    • Nowakowska, Beata;
    • Phoolchund, Anju;
    • Lay, Kenneth;
    • Ramasamy, T Selvee;
    • Cananzi, Mara;
    • Nettersheim, Daniel;
    • Sullivan, Mark;
    • Frost, Jennifer;
    • Moore, Gudrun;
    • Vermeesch, Joris R;
    • Fisk, Nicholas M;
    • Thrasher, Adrian J;
    • Atala, Anthony;
    • Adjaye, James
    Publication type:
    Article
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    The β-Globin Locus Control Region in Combination With the EF1α Short Promoter Allows Enhanced Lentiviral Vector-mediated Erythroid Gene Expression With Conserved Multilineage Activity.

    Published in:
    Molecular Therapy, 2012, v. 20, n. 7, p. 1400, doi. 10.1038/mt.2012.50
    By:
    • Montiel-Equihua, Claudia A;
    • Zhang, Lin;
    • Knight, Sean;
    • Saadeh, Heba;
    • Scholz, Simone;
    • Carmo, Marlene;
    • Alonso-Ferrero, Maria E;
    • Blundell, Michael P;
    • Monkeviciute, Aiste;
    • Schulz, Reiner;
    • Collins, Mary;
    • Takeuchi, Yasuhiro;
    • Schmidt, Manfred;
    • Fairbanks, Lynette;
    • Antoniou, Michael;
    • Thrasher, Adrian J;
    • Gaspar, H Bobby
    Publication type:
    Article
    50

    Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-optimized IL2RG Gene and Minimal Pretransplant Conditioning.

    Published in:
    Molecular Therapy, 2011, v. 19, n. 10, p. 1867, doi. 10.1038/mt.2011.127
    By:
    • Huston, Marshall W;
    • van Til, Niek P;
    • Visser, Trudi P;
    • Arshad, Shazia;
    • Brugman, Martijn H;
    • Cattoglio, Claudia;
    • Nowrouzi, Ali;
    • Li, Yuedan;
    • Schambach, Axel;
    • Schmidt, Manfred;
    • Baum, Christopher;
    • von Kalle, Christof;
    • Mavilio, Fulvio;
    • Zhang, Fang;
    • Blundell, Mike P;
    • Thrasher, Adrian J;
    • Verstegen, Monique MA;
    • Wagemaker, Gerard
    Publication type:
    Article