Found: 7
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Improvements in Walking Distance during Nusinersen Treatment – A Prospective 3-year SMArtCARE Registry Study.
- Published in:
- Journal of Neuromuscular Diseases, 2023, v. 10, n. 1, p. 29, doi. 10.3233/JND-221600
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- Publication type:
- Article
De-duplicating patient records from three independent data sources reveals the incidence of rare neuromuscular disorders in Germany.
- Published in:
- 2019
- By:
- Publication type:
- journal article
SMArtCARE - A platform to collect real-life outcome data of patients with spinal muscular atrophy.
- Published in:
- 2019
- By:
- Publication type:
- journal article
Effect of nusinersen on motor, respiratory and bulbar function in early-onset spinal muscular atrophy.
- Published in:
- Brain: A Journal of Neurology, 2023, v. 146, n. 2, p. 668, doi. 10.1093/brain/awac252
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- Publication type:
- Article
EURO-NMD registry: federated FAIR infrastructure, innovative technologies and concepts of a patient-centred registry for rare neuromuscular disorders.
- Published in:
- Orphanet Journal of Rare Diseases, 2024, v. 19, n. 1, p. 1, doi. 10.1186/s13023-024-03059-3
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- Publication type:
- Article
The TREAT-NMD care and trial site registry: an online registry to facilitate clinical research for neuromuscular diseases.
- Published in:
- Orphanet Journal of Rare Diseases, 2013, v. 8, n. 1, p. 1, doi. 10.1186/1750-1172-8-171
- By:
- Publication type:
- Article
Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study.
- Published in:
- 2022
- By:
- Publication type:
- journal article