Found: 26
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scAAVIL-1ra dosing trial in a large animal model and validation of long-term expression with repeat administration for osteoarthritis therapy.
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- Gene Therapy, 2015, v. 22, n. 7, p. 536, doi. 10.1038/gt.2015.21
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- Article
Efficient transduction of vascular smooth muscle cells with a translational AAV2.5 vector: a new perspective for in-stent restenosis gene therapy.
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- Gene Therapy, 2013, v. 20, n. 9, p. 901, doi. 10.1038/gt.2013.13
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- Article
Three-dimensional multipotent progenitor cell aggregates for expansion, osteogenic differentiation and 'in vivo' tracing with AAV vector serotype 6.
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- Gene Therapy, 2013, v. 20, n. 2, p. 158, doi. 10.1038/gt.2012.16
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- Article
Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs.
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- Gene Therapy, 2013, v. 20, n. 1, p. 35, doi. 10.1038/gt.2011.211
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- Article
Preclinical safety evaluation of subretinal AAV2.sFlt-1 in non-human primates.
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- Gene Therapy, 2012, v. 19, n. 10, p. 999, doi. 10.1038/gt.2011.169
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- Article
Robust spinal motor neuron transduction following intrathecal delivery of AAV9 in pigs.
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- Gene Therapy, 2012, v. 19, n. 8, p. 852, doi. 10.1038/gt.2011.130
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- Article
Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia.
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- Gene Therapy, 2012, v. 19, n. 3, p. 288, doi. 10.1038/gt.2011.90
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- Article
The influence of epileptic neuropathology and prior peripheral immunity on CNS transduction by rAAV2 and rAAV5.
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- Gene Therapy, 2011, v. 18, n. 10, p. 961, doi. 10.1038/gt.2011.49
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- Article
Self-complementary AAV mediates gene targeting and enhances endonuclease delivery for double-strand break repair.
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- Gene Therapy, 2010, v. 17, n. 9, p. 1175, doi. 10.1038/gt.2010.65
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- Article
Delivering multiple gene products in the brain from a single adeno-associated virus vector.
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- Gene Therapy, 2009, v. 16, n. 11, p. 1314, doi. 10.1038/gt.2009.106
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Gene therapy for cardiomyocytes, a heart beat away.
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- Gene Therapy, 2009, v. 16, n. 6, p. 707, doi. 10.1038/gt.2009.40
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- Article
A small regulatory element from chromosome 19 enhances liver-specific gene expression.
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- Gene Therapy, 2009, v. 16, n. 1, p. 43, doi. 10.1038/gt.2008.134
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- Article
Bioluminescent virion shells: new tools for quantitation of AAV vector dynamics in cells and live animals.
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- Gene Therapy, 2008, v. 15, n. 24, p. 1618, doi. 10.1038/gt.2008.127
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- Article
Adeno-associated virus-mediated expression and constitutive secretion of NPY or NPY13-36 suppresses seizure activity in vivo.
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- Gene Therapy, 2007, v. 14, n. 21, p. 1534, doi. 10.1038/sj.gt.3303013
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- Article
Heart Failure: A Silver bullet to treat heart failure.
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- Gene Therapy, 2006, v. 13, n. 13, p. 997, doi. 10.1038/sj.gt.3302747
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- Article
Adeno-associated virus-mediated gene transfer of the heart/muscle adenine nucleotide translocator (ANT) in mouse.
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- Gene Therapy, 2005, v. 12, n. 7, p. 570, doi. 10.1038/sj.gt.3302443
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- Article
Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo.
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- Gene Therapy, 2003, v. 10, n. 26, p. 2112, doi. 10.1038/sj.gt.3302134
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- Article
Vector biophysics: Crystal-clear view.
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- Gene Therapy, 2002, v. 9, n. 21, p. 1413, doi. 10.1038/sj.gt.3301884
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- Article
Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis.
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- Gene Therapy, 2001, v. 8, n. 16, p. 1248, doi. 10.1038/sj.gt.3301514
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- Article
AAV vectors: is clinical success on the horizon?
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- Gene Therapy, 2000, v. 7, n. 1, p. 24, doi. 10.1038/sj.gt.3301109
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- Article
Titration of AAV-2 particles via a novel capsid ELISA: packaging of genomes can limit production of recombinant AAV-2.
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- Gene Therapy, 1999, v. 6, n. 7, p. 1322, doi. 10.1038/sj.gt.3300946
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- Article
Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield.
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- Gene Therapy, 1999, v. 6, n. 6, p. 973, doi. 10.1038/sj.gt.3300938
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- Article
Inducible long-term gene expression in brain with adeno-associated virus gene transfer.
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- Gene Therapy, 1998, v. 5, n. 12, p. 1604, doi. 10.1038/sj.gt.3300782
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- Article
In vivo expression of therapeutic human genes for dopamine production in the caudates of MPTP-treated monkeys using an AAV vector.
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- Gene Therapy, 1998, v. 5, n. 6, p. 820, doi. 10.1038/sj.gt.3300650
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- Article
Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia.
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- Gene Therapy, 1998, v. 5, n. 1, p. 40, doi. 10.1038/sj.gt.3300548
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- Article
Immune responses to AAV in a phase I study for Canavan disease.
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- Journal of Gene Medicine, 2006, v. 8, n. 5, p. 577, doi. 10.1002/jgm.885
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- Article