Found: 2
Select item for more details and to access through your institution.
Somatic CAG expansion in Huntington's disease is dependent on the MLH3 endonuclease domain, which can be excluded via splice redirection.
- Published in:
- Nucleic Acids Research, 2021, v. 49, n. 7, p. 3907, doi. 10.1093/nar/gkab152
- By:
- Publication type:
- Article
Splice modulators target PMS1 to reduce somatic expansion of the Huntington's disease-associated CAG repeat.
- Published in:
- Nature Communications, 2024, v. 15, n. 1, p. 1, doi. 10.1038/s41467-024-47485-0
- By:
- Publication type:
- Article