Works matching AU Pipe, Steven W.


Results: 45
    1

    A chamber of hope for hemophilia.

    Published in:
    Nature Biotechnology, 2000, v. 18, n. 3, p. 264, doi. 10.1038/73690
    By:
    • Pipe, Steven W.;
    • Kaufman, Randal J.
    Publication type:
    Article
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    Bleeding due to disruption of a cargo-specific ER-to-Golgi transport complex.

    Published in:
    Nature Genetics, 2003, v. 34, n. 2, p. 220, doi. 10.1038/ng1153
    By:
    • Zhang, Bin;
    • Cunningham, Michael A;
    • Nichols, William C;
    • Bernat, John A;
    • Seligsohn, Uri;
    • Pipe, Steven W;
    • McVey, John H;
    • Schulte-Overberg, Ursula;
    • de Bosch, Norma B;
    • Ruiz-Saez, Arlette;
    • White, Gilbert C.;
    • Tuddenham, EGD;
    • Kaufman, Randal J.;
    • Ginsburg, David
    Publication type:
    Article
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    339. FIV Lentiviral Vector Gene Transfer for Hemophilia A.

    Published in:
    Molecular Therapy, 2006, v. 13, p. S129, doi. 10.1016/j.ymthe.2006.08.396
    By:
    • Chikkanna-Gowda, C. P.;
    • Litao Xie;
    • Yubin Kang;
    • Hickey, Melissa A.;
    • Sinn, Patrick L.;
    • Goreham-Voss, Jessica D.;
    • Pipe, Steven W.;
    • McCray, Paul B.
    Publication type:
    Article
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    Operationalising a Haemophilia Gene Editing Lexicon for Practical Use.

    Published in:
    Haemophilia, 2025, v. 31, n. 2, p. 207, doi. 10.1111/hae.15155
    By:
    • McKeown, William;
    • Hermans, Cedric;
    • Unzu, Carmen;
    • Kay, Mark A.;
    • Peyvandi, Flora;
    • Smith, Penni;
    • Miesbach, Wolfgang;
    • Pierce, Glenn F.;
    • Khair, Kate;
    • Valentino, Leonard A.;
    • Pipe, Steven W.;
    • Pillai, Monisha;
    • Jones, Micheala;
    • Delwart, Virginie;
    • Sindhurakar, Anil;
    • Gutstein, David E.;
    • Kessler, Craig M.
    Publication type:
    Article
    20

    A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.

    Published in:
    Haemophilia, 2024, v. 30, n. 6, p. 1272, doi. 10.1111/hae.15108
    By:
    • Hermans, Cedric;
    • Valentino, Leonard A.;
    • Thornburg, Courtney D.;
    • Unzu, Carmen;
    • Kay, Mark A.;
    • Peyvandi, Flora;
    • Smith, Penni;
    • Miesbach, Wolfgang;
    • McKeown, William;
    • Pierce, Glenn F.;
    • Khair, Kate;
    • Pipe, Steven W.;
    • Starcevic, Katarina;
    • Pillai, Monisha;
    • Jones, Micheala;
    • Chiao, Megan;
    • Antonino, Ilia;
    • Kessler, Craig
    Publication type:
    Article
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    Eptacog beta efficacy and safety in the treatment and control of bleeding in paediatric subjects (<12 years) with haemophilia A or B with inhibitors.

    Published in:
    Haemophilia, 2022, v. 28, n. 4, p. 548, doi. 10.1111/hae.14563
    By:
    • Pipe, Steven W.;
    • Hermans, Cédric;
    • Chitlur, Meera;
    • Carcao, Manuel;
    • Castaman, Giancarlo;
    • Davis, Joanna A.;
    • Ducore, Jonathan;
    • Dunn, Amy L.;
    • Escobar, Miguel;
    • Journeycake, Janna;
    • Khan, Osman;
    • Mahlangu, Johnny;
    • Meeks, Shannon L.;
    • Mitha, Ismail Haroon;
    • Négrier, Claude;
    • Nowak‐Göttl, Ulrike;
    • Recht, Michael;
    • Chrisentery‐Singleton, Tammuella;
    • Stasyshyn, Oleksandra;
    • Vilchevska, Kateryna V.
    Publication type:
    Article
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    The effect of emicizumab prophylaxis on long‐term, self‐reported physical health in persons with haemophilia A without factor VIII inhibitors in the HAVEN 3 and HAVEN 4 studies.

    Published in:
    Haemophilia, 2021, v. 27, n. 5, p. 854, doi. 10.1111/hae.14363
    By:
    • Skinner, Mark W.;
    • Négrier, Claude;
    • Paz‐Priel, Ido;
    • Chebon, Sammy;
    • Jiménez‐Yuste, Victor;
    • Callaghan, Michael U.;
    • Lehle, Michaela;
    • Niggli, Markus;
    • Mahlangu, Johnny;
    • Shapiro, Amy;
    • Shima, Midori;
    • Campinha‐Bacote, Avrita;
    • Levy, Gallia G.;
    • Oldenburg, Johannes;
    • von Mackensen, Sylvia;
    • Pipe, Steven W.
    Publication type:
    Article
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    WFH Guidelines for the Management of Hemophilia, 3rd edition.

    Published in:
    Haemophilia, 2020, v. 26, n. 6, p. 1, doi. 10.1111/hae.14046
    By:
    • Srivastava, Alok;
    • Santagostino, Elena;
    • Dougall, Alison;
    • Kitchen, Steve;
    • Sutherland, Megan;
    • Pipe, Steven W.;
    • Carcao, Manuel;
    • Mahlangu, Johnny;
    • Ragni, Margaret V.;
    • Windyga, Jerzy;
    • Llinás, Adolfo;
    • Goddard, Nicholas J.;
    • Mohan, Richa;
    • Poonnoose, Pradeep M.;
    • Feldman, Brian M.;
    • Lewis, Sandra Zelman;
    • Berg, H. Marijke;
    • Pierce, Glenn F.
    Publication type:
    Article
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