Works by Perrone, Daniela


Results: 29
    1

    Exon skipping-mediated dystrophin reading frame restoration for small mutations.

    Published in:
    Human Mutation, 2009, v. 30, n. 11, p. 1527, doi. 10.1002/humu.21092
    By:
    • Spitali, Pietro;
    • Rimessi, Paola;
    • Fabris, Marina;
    • Perrone, Daniela;
    • Falzarano, Sofia;
    • Bovolenta, Matteo;
    • Trabanelli, Cecilia;
    • Mari, Lara;
    • Bassi, Elena;
    • Tuffery, Sylvie;
    • Gualandi, Francesca;
    • Maraldi, Nadir M.;
    • Sabatelli-Giraud, Patrizia;
    • Medici, Alessandro;
    • Merlini, Luciano;
    • Ferlini, Alessandra
    Publication type:
    Article
    2

    A New Drug Delivery System Based on Tauroursodeoxycholic Acid and PEDOT.

    Published in:
    Chemistry - A European Journal, 2019, v. 25, n. 9, p. 2322, doi. 10.1002/chem.201805285
    By:
    • Carli, Stefano;
    • Fioravanti, Giulia;
    • Armirotti, Andrea;
    • Ciarpella, Francesca;
    • Prato, Mirko;
    • Ottonello, Giuliana;
    • Salerno, Marco;
    • Scarpellini, Alice;
    • Perrone, Daniela;
    • Marchesi, Elena;
    • Ricci, Davide;
    • Fadiga, Luciano
    Publication type:
    Article
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    Biodistribution and Molecular Studies on Orally Administered Nanoparticle-AON Complexes Encapsulated with Alginate Aiming at Inducing Dystrophin Rescue in mdx Mice.

    Published in:
    BioMed Research International, 2013, v. 2013, p. 1, doi. 10.1155/2013/527418
    By:
    • Falzarano, Maria Sofia;
    • Passarelli, Chiara;
    • Bassi, Elena;
    • Fabris, Marina;
    • Perrone, Daniela;
    • Sabatelli, Patrizia;
    • Maraldi, Nadir M.;
    • Donà, Silvia;
    • Selvatici, Rita;
    • Bonaldo, Paolo;
    • Sparnacci, Katia;
    • Laus, Michele;
    • Braghetta, Paola;
    • Rimessi, Paola;
    • Ferlini, Alessandra
    Publication type:
    Article
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    Persistent Dystrophin Protein Restoration 90 Days after a Course of Intraperitoneally Administered Naked 2′ OMePS AON and ZM2 NP-AON Complexes in mdx Mice.

    Published in:
    Journal of Biomedicine & Biotechnology, 2012, v. 2012, p. 1, doi. 10.1155/2012/897076
    By:
    • Bassi, Elena;
    • Falzarano, Sofia;
    • Fabris, Marina;
    • Gualandi, Francesca;
    • Merlini, Luciano;
    • Vattemi, Gaetano;
    • Perrone, Daniela;
    • Marchesi, Elena;
    • Sabatelli, Patrizia;
    • Sparnacci, Katia;
    • Laus, Michele;
    • Bonaldo, Paolo;
    • Rimessi, Paola;
    • Braghetta, Paola;
    • Ferlini, Alessandra
    Publication type:
    Article
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    Cationic PMMA Nanoparticles Bind and Deliver Antisense Oligoribonucleotides Allowing Restoration of Dystrophin Expression in the mdx Mouse.

    Published in:
    Molecular Therapy, 2009, v. 17, n. 5, p. 820, doi. 10.1038/mt.2009.8
    By:
    • Rimessi, Paola;
    • Sabatelli, Patrizia;
    • Fabris, Marina;
    • Braghetta, Paola;
    • Bassi, Elena;
    • Spitali, Pietro;
    • Vattemi, Gaetano;
    • Tomelleri, Giuliano;
    • Mari, Lara;
    • Perrone, Daniela;
    • Medici, Alessandro;
    • Neri, Marcella;
    • Bovolenta, Matteo;
    • Martoni, Elena;
    • Maraldi, Nadir M.;
    • Gualandi, Francesca;
    • Merlini, Luciano;
    • Ballestri, Marco;
    • Tondelli, Luisa;
    • Sparnacci, Katia
    Publication type:
    Article
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