Found: 5
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Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD.
- Published in:
- American Journal of Hematology, 2022, v. 97, n. 3, p. E120, doi. 10.1002/ajh.26458
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- Publication type:
- Article
Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patients.
- Published in:
- American Journal of Hematology, 2021, v. 96, n. 8, p. 989, doi. 10.1002/ajh.26234
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- Publication type:
- Article
Findings on Optical Coherence Tomography in Malignant Infantile Osteopetrosis.
- Published in:
- 2022
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- Publication type:
- journal article
Busulfan and subsequent malignancy: An evidence-based risk assessment.
- Published in:
- Pediatric Blood & Cancer, 2024, v. 71, n. 1, p. 1, doi. 10.1002/pbc.30738
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- Publication type:
- Article
Mosaicism in Fanconi anemia: concise review and evaluation of published cases with focus on clinical course of blood count normalization.
- Published in:
- 2020
- By:
- Publication type:
- journal article