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Effective gene therapy for haemophilic mice with pathogenic factor IX antibodies.
Published in:
EMBO Molecular Medicine, 2013, v. 5, n. 11, p. 1698, doi. 10.1002/emmm.201302859
By:
- Markusic, David M.;
- Hoffman, Brad E.;
- Perrin, George Q.;
- Nayak, Sushrusha;
- Wang, Xiaomei;
- LoDuca, Paul A.;
- High, Katherine A.;
- Herzog, Roland W.
Publication type:
Article
GITR engagement preferentially enhances proliferation of functionally competent CD4+CD25+FoxP3+ regulatory T cells.
Published in:
International Immunology, 2010, v. 22, n. 4, p. 259, doi. 10.1093/intimm/dxq001
By:
- Gongxian Liao;
- Nayak, Sushrusha;
- Regueiro, Jose R.;
- Berger, Scott B.;
- Detre, Cynthia;
- Romero, Xavier;
- de Waal Malefyt, Rene;
- Chatila, Talal A.;
- Herzog, Roland W.;
- Terhorst, Cox
Publication type:
Article
Immune Responses and Hypercoagulation in ERT for Pompe Disease Are Mutation and rhGAA Dose Dependent.
Published in:
PLoS ONE, 2014, v. 9, n. 6, p. 1, doi. 10.1371/journal.pone.0098336
By:
- Nayak, Sushrusha;
- Doerfler, Phillip A.;
- Porvasnik, Stacy L.;
- Cloutier, Denise D.;
- Khanna, Richie;
- Valenzano, Ken J.;
- Herzog, Roland W.;
- Byrne, Barry J.
Publication type:
Article
Tolerance Induction to Cytoplasmic β-Galactosidase by Hepatic AAV Gene Transfer - Implications for Antigen Presentation and Immunotoxicity.
Published in:
PLoS ONE, 2009, v. 4, n. 8, p. 1, doi. 10.1371/journal.pone.0006376
By:
- Martino, Ashley T.;
- Nayak, Sushrusha;
- Hoffman, Brad E.;
- Cooper, Mario;
- Liao, Gongxian;
- Markusic, David M.;
- Byrne, Barry J.;
- Terhorst, Cox;
- Herzog, Roland W.
Publication type:
Article
Sustained Correction of Motoneuron Histopathology Following Intramuscular Delivery of AAV in Pompe Mice.
Published in:
Molecular Therapy, 2014, v. 22, n. 4, p. 702, doi. 10.1038/mt.2013.282
By:
- ElMallah, Mai K;
- Falk, Darin J;
- Nayak, Sushrusha;
- Federico, Roland A;
- Sandhu, Milapjit S;
- Poirier, Amy;
- Byrne, Barry J;
- Fuller, David D
Publication type:
Article
Impact of the Underlying Mutation and the Route of Vector Administration on Immune Responses to Factor IX in Gene Therapy for Hemophilia B.
Published in:
Molecular Therapy, 2009, v. 17, n. 10, p. 1733, doi. 10.1038/mt.2009.159
By:
- Cao, Ou;
- Hoffman, Brad E.;
- Moghimi, Babak;
- Nayak, Sushrusha;
- Cooper, Mario;
- Zhou, Shangzhen;
- Ertl, Hildegund C. J.;
- High, Katherine A.;
- Herzog, Roland W.
Publication type:
Article
Pompe disease gene therapy.
Published in:
Human Molecular Genetics, 2011, v. 20, n. R1, p. R61, doi. 10.1093/hmg/ddr174
By:
- Byrne, Barry J.;
- Falk, Darin J.;
- Pacak, Christina A.;
- Nayak, Sushrusha;
- Herzog, Roland W.;
- Elder, Melissa E.;
- Collins, Shelley W.;
- Conlon, Thomas J.;
- Clement, Nathalie;
- Cleaver, Brian D.;
- Cloutier, Denise A.;
- Porvasnik, Stacy L.;
- Islam, Saleem;
- Elmallah, Mai K.;
- Martin, Anatole;
- Smith, Barbara K.;
- Fuller, David D.;
- Lawson, Lee Ann;
- Mah, Cathryn S.
Publication type:
Article

Found: 7

Effective gene therapy for haemophilic mice with pathogenic factor IX antibodies.

GITR engagement preferentially enhances proliferation of functionally competent CD4+CD25+FoxP3+ regulatory T cells.

Immune Responses and Hypercoagulation in ERT for Pompe Disease Are Mutation and rhGAA Dose Dependent.

Tolerance Induction to Cytoplasmic β-Galactosidase by Hepatic AAV Gene Transfer - Implications for Antigen Presentation and Immunotoxicity.

Sustained Correction of Motoneuron Histopathology Following Intramuscular Delivery of AAV in Pompe Mice.

Impact of the Underlying Mutation and the Route of Vector Administration on Immune Responses to Factor IX in Gene Therapy for Hemophilia B.

Pompe disease gene therapy.