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Human mesenchymal stem cells (hMSCs) expressing truncated soluble vascular endothelial growth factor receptor (tsFlk-1) following lentiviral-mediated gene transfer inhibit growth of Burkitt's lymphoma in a murine model.
- Published in:
- Journal of Gene Medicine, 2006, v. 8, n. 3, p. 253, doi. 10.1002/jgm.840
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- Publication type:
- Article
Modification of a Constitutive to Glucose-Responsive Liver-Specific Promoter Resulted in Increased Efficacy of Adeno-Associated Virus Serotype 8-Insulin Gene Therapy of Diabetic Mice.
- Published in:
- Cells (2073-4409), 2020, v. 9, n. 11, p. 2474, doi. 10.3390/cells9112474
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- Publication type:
- Article
Therapeutic expression of human clotting factors IX and X following adeno-associated viral vector-mediated intrauterine gene transfer in early-gestation fetal macaques.
- Published in:
- FASEB Journal, 2019, v. 33, n. 3, p. 3954, doi. 10.1096/fj.201801391R
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- Article
AAV Vector Biology in Primates: Finding the Missing Link?
- Published in:
- 2011
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- Publication type:
- Editorial
Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 11, p. 1950, doi. 10.1038/mt.2011.107
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- Publication type:
- Article
Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins.
- Published in:
- Molecular Therapy, 2011, v. 19, n. 5, p. 876, doi. 10.1038/mt.2010.274
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- Publication type:
- Article
490. Successful Readministration of AAV8 Following Administration of Nondepleting CD4 Antibody at the Time of Vector Administration.
- Published in:
- Molecular Therapy, 2006, v. 13, p. S190, doi. 10.1016/j.ymthe.2006.08.560
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- Publication type:
- Article
711. Treatment of Acute Myeloid Leukemia by rAAV 8 Vector Mediated Human Interferon-β Gene Transfer
- Published in:
- 2005
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- Publication type:
- Abstract
118. Self-Complementary AAV Vectors Pseudotyped with Either Serotype 5 or 8 Capsids Give Therapeutic Human Factor IX Levels at Significantly Reduced Doses in Non-Human Primates
- Published in:
- 2005
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- Publication type:
- Abstract
Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models
- Published in:
- Molecular Therapy, 2005, v. 11, n. 6, p. 875, doi. 10.1016/j.ymthe.2004.12.022
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- Publication type:
- Article
Careful Decoy Receptor Titering is Required to Inhibit Tumor Angiogenesis While Avoiding Adversely Altering VEGF Bioavailability
- Published in:
- Molecular Therapy, 2005, v. 11, n. 2, p. 300, doi. 10.1016/j.ymthe.2004.09.014
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- Publication type:
- Article
Comparison of Various Envelope Proteins for Their Ability to Pseudotype Lentiviral Vectors and Transduce Primitive Hematopoietic Cells from Human Blood
- Published in:
- Molecular Therapy, 2002, v. 5, n. 3, p. 242, doi. 10.1006/mthe.2002.0549
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- Publication type:
- Article
The Role of Histone Demethylase KDM4B in Myc Signaling in Neuroblastoma.
- Published in:
- JNCI: Journal of the National Cancer Institute, 2015, v. 107, n. 6, p. 1, doi. 10.1093/jnci/djv080
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- Publication type:
- Article
The role of histone demethylase KDM4B in Myc signaling in neuroblastoma.
- Published in:
- 2015
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- Publication type:
- journal article
An introduction to induced pluripotent stem cells.
- Published in:
- British Journal of Haematology, 2010, v. 151, n. 1, p. 16, doi. 10.1111/j.1365-2141.2010.08296.x
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- Publication type:
- Article
Exogenous TERC alone can enhance proliferative potential, telomerase activity and telomere length in lymphocytes from dyskeratosis congenita patients.
- Published in:
- British Journal of Haematology, 2009, v. 144, n. 5, p. 771, doi. 10.1111/j.1365-2141.2008.07516.x
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- Publication type:
- Article
A review of gene therapy for haematological disorders.
- Published in:
- British Journal of Haematology, 2005, v. 128, n. 1, p. 3, doi. 10.1111/j.1365-2141.2004.05231.x
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- Publication type:
- Article
A Systematic Evaluation of Integration Free Reprogramming Methods for Deriving Clinically Relevant Patient Specific Induced Pluripotent Stem (iPS) Cells.
- Published in:
- PLoS ONE, 2013, v. 8, n. 11, p. 1, doi. 10.1371/journal.pone.0081622
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- Publication type:
- Article
Transient B Cell Depletion or Improved Transgene Expression by Codon Optimization Promote Tolerance to Factor VIII in Gene Therapy.
- Published in:
- PLoS ONE, 2012, v. 7, n. 5, p. 1, doi. 10.1371/journal.pone.0037671
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- Publication type:
- Article
Haemophilia, the journey in search of a cure. 1960–2020.
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- British Journal of Haematology, 2020, v. 191, n. 4, p. 573, doi. 10.1111/bjh.17155
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- Publication type:
- Article
Ibrutinib enhances the efficacy of ROR1 bispecific T cell engager mediated cytotoxicity in chronic lymphocytic leukaemia.
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- British Journal of Haematology, 2019, v. 186, n. 2, p. 380, doi. 10.1111/bjh.15911
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- Publication type:
- Article
Recent advances in developing specific therapies for haemophilia.
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- British Journal of Haematology, 2018, v. 181, n. 2, p. 161, doi. 10.1111/bjh.15084
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- Publication type:
- Article
Developments in the treatment of hemophilia B: focus on emerging gene therapy.
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- Application of Clinical Genetics, 2013, v. 6, p. 91, doi. 10.2147/TACG.S31928
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- Publication type:
- Article
Efficient gene transfer into human umbilical vein endothelial cells allows functional analysis of the human tissue factor gene promoter.
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- British Journal of Haematology, 1994, v. 88, n. 1, p. 122, doi. 10.1111/j.1365-2141.1994.tb04987.x
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- Publication type:
- Article