Found: 11
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Genetic modifiers of ambulation in the cooperative international Neuromuscular research group Duchenne natural history study.
- Published in:
- Annals of Neurology, 2015, v. 77, n. 4, p. 684, doi. 10.1002/ana.24370
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- Publication type:
- Article
Correction to: Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015–2022): 2022 interim analysis.
- Published in:
- 2023
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- Publication type:
- Correction Notice
Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015–2022): 2022 interim analysis.
- Published in:
- Journal of Neurology, 2023, v. 270, n. 8, p. 3896, doi. 10.1007/s00415-023-11687-1
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- Publication type:
- Article
Serum pharmacodynamic biomarkers for chronic corticosteroid treatment of children.
- Published in:
- Scientific Reports, 2016, p. 31727, doi. 10.1038/srep31727
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- Publication type:
- Article
Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial.
- Published in:
- JAMA Neurology, 2020, v. 77, n. 8, p. 982, doi. 10.1001/jamaneurol.2020.1264
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- Publication type:
- Article
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study.
- Published in:
- 2020
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- Publication type:
- journal article
Rare Disease Clinical Trials: Strategies Learned from Duchenne Muscular Dystrophy: Approaches sponsors, CROs, and investigators can take from the DMD experience.
- Published in:
- Applied Clinical Trials, 2022, v. 31, n. 10, p. 18
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- Publication type:
- Article
The CINRG Becker Natural History Study: Baseline characteristics.
- Published in:
- 2020
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- Publication type:
- journal article
Cooperative international neuromuscular research group duchenne natural history study demonstrates insufficient diagnosis and treatment of cardiomyopathy in duchenne muscular dystrophy.
- Published in:
- Muscle & Nerve, 2014, v. 50, n. 2, p. 250, doi. 10.1002/mus.24163
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- Publication type:
- Article
Correction: Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study.
- Published in:
- 2016
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- Publication type:
- Correction Notice
Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study.
- Published in:
- PLoS ONE, 2016, v. 11, n. 4, p. 1, doi. 10.1371/journal.pone.0153461
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- Publication type:
- Article