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Characterization of patients with Duchenne muscular dystrophy across previously developed health states.
Published in:
PLoS ONE, 2024, v. 19, n. 10, p. 1, doi. 10.1371/journal.pone.0307118
By:
- Muntoni, Francesco;
- Goemans, Nathalie;
- Posner, Nate;
- Signorovitch, James;
- Johnson, Michaela;
- He, Chujun;
- Dorling, Patricia;
- Beaverson, Katherine;
- Alvir, Jose;
- Mahn, Matthias;
- Ward, Susan J.;
- McDonald, Craig M.;
- Mercuri, Eugenio
Publication type:
Article
A presynaptic congenital myasthenic syndrome attributed to a homozygous sequence variant in <italic>LAMA5</italic>.
Published in:
Annals of the New York Academy of Sciences, 2018, v. 1413, n. 1, p. 119, doi. 10.1111/nyas.13585
By:
- Maselli, Ricardo A.;
- Arredondo, Juan;
- Vázquez, Jessica;
- Chong, Jessica X.;
- Bamshad, Michael J.;
- Nickerson, Deborah A.;
- Lara, Marian;
- Ng, Fiona;
- Lo, Victoria Lee;
- Pytel, Peter;
- McDonald, Craig M.
Publication type:
Article
Multi-Omics Identifies Circulating miRNA and Protein Biomarkers for Facioscapulohumeral Dystrophy.
Published in:
Journal of Personalized Medicine, 2020, v. 10, n. 4, p. 236, doi. 10.3390/jpm10040236
By:
- Heier, Christopher R.;
- Zhang, Aiping;
- Nguyen, Nhu Y;
- Tully, Christopher B.;
- Panigrahi, Aswini;
- Gordish-Dressman, Heather;
- Pandey, Sachchida Nand;
- Guglieri, Michela;
- Ryan, Monique M.;
- Clemens, Paula R.;
- Thangarajh, Mathula;
- Webster, Richard;
- Smith, Edward C.;
- Connolly, Anne M.;
- McDonald, Craig M.;
- Karachunski, Peter;
- Tulinius, Mar;
- Harper, Amy;
- Mah, Jean K.;
- Fiorillo, Alyson A.
Publication type:
Article
Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.
Published in:
PLoS ONE, 2024, v. 19, n. 6, p. 1, doi. 10.1371/journal.pone.0304099
By:
- McDonald, Craig M.;
- Signorovitch, James;
- Mercuri, Eugenio;
- Niks, Erik H.;
- Wong, Brenda;
- Fillbrunn, Mirko;
- Sajeev, Gautam;
- Yim, Erica;
- Dieye, Ibrahima;
- Miller, Debra;
- Ward, Susan J.;
- Goemans, Nathalie
Publication type:
Article
Presynaptic congenital myasthenic syndrome with a homozygous sequence variant in LAMA5 combines myopia, facial tics, and failure of neuromuscular transmission.
Published in:
American Journal of Medical Genetics. Part A, 2017, v. 173, n. 8, p. 2240, doi. 10.1002/ajmg.a.38291
By:
- Maselli, Ricardo A.;
- Arredondo, Juan;
- Vázquez, Jessica;
- Chong, Jessica X.;
- Bamshad, Michael J.;
- Nickerson, Deborah A.;
- Lara, Marian;
- Ng, Fiona;
- Lo, Victoria L.;
- Pytel, Peter;
- McDonald, Craig M.
Publication type:
Article
Survival among patients receiving eteplirsen for up to 8 years for the treatment of Duchenne muscular dystrophy and contextualization with natural history controls.
Published in:
Muscle & Nerve, 2024, v. 70, n. 1, p. 60, doi. 10.1002/mus.28075
By:
- Iff, Joel;
- Done, Nicolae;
- Tuttle, Edward;
- Zhong, Yi;
- Wei, Fangzhou;
- Darras, Basil T.;
- McDonald, Craig M.;
- Mercuri, Eugenio;
- Muntoni, Francesco
Publication type:
Article
Treatment effect of idebenone on inspiratory function in patients with Duchenne muscular dystrophy.
Published in:
Pediatric Pulmonology, 2017, v. 52, n. 4, p. 508, doi. 10.1002/ppul.23547
By:
- Buyse, Gunnar M.;
- Voit, Thomas;
- Schara, Ulrike;
- Straathof, Chiara S.M.;
- D'Angelo, Maria Grazia;
- Bernert, Günther;
- Cuisset, Jean-Marie;
- Finkel, Richard S.;
- Goemans, Nathalie;
- Rummey, Christian;
- Leinonen, Mika;
- Mayer, Oscar H.;
- Spagnolo, Paolo;
- Meier, Thomas;
- McDonald, Craig M.
Publication type:
Article
Quality-of-Life Measures in Children With Neurological Conditions: Pediatric Neuro-QOL.
Published in:
Neurorehabilitation & Neural Repair, 2012, v. 26, n. 1, p. 36, doi. 10.1177/1545968311412054
By:
- Lai, Jin-Shei;
- Nowinski, Cindy;
- Victorson, David;
- Bode, Rita;
- Podrabsky, Tracy;
- McKinney, Natalie;
- Straube, Don;
- Holmes, Gregory L.;
- McDonald, Craig M.;
- Henricson, Erik;
- Abresch, R. Ted;
- Moy, Claudia S.;
- Cella, David
Publication type:
Article
Delays in pulmonary decline in eteplirsen-treated patients with Duchenne muscular dystrophy.
Published in:
2022
By:
- Iff, Joel;
- Gerrits, Charles;
- Zhong, Yi;
- Tuttle, Edward;
- Birk, Erica;
- Zheng, Yeya;
- Paul, Xander;
- Henricson, Erik K.;
- McDonald, Craig M.;
- CINRG-DNHS Investigators
Publication type:
journal article
Evaluating longitudinal therapy effects via the North Star Ambulatory Assessment.
Published in:
Muscle & Nerve, 2021, v. 64, n. 5, p. 614, doi. 10.1002/mus.27396
By:
- McDonald, Craig M.;
- Wei, Lee‐Jen;
- Flanigan, Kevin M.;
- Elfring, Gary;
- Trifillis, Panayiota;
- Muntoni, Francesco
Publication type:
Article
(-)-Epicatechin induces mitochondrial biogenesis and markers of muscle regeneration in adults with Becker muscular dystrophy.
Published in:
2021
By:
- McDonald, Craig M.;
- Ramirez‐Sanchez, Israel;
- Oskarsson, Björn;
- Joyce, Nanette;
- Aguilar, Candace;
- Nicorici, Alina;
- Dayan, Jonathan;
- Goude, Erica;
- Abresch, R. Ted;
- Villarreal, Francisco;
- Ceballos, Guillermo;
- Perkins, Guy;
- Dugar, Sundeep;
- Schreiner, George;
- Henricson, Erik K.;
- Ramirez-Sanchez, Israel
Publication type:
journal article
The CINRG Becker Natural History Study: Baseline characteristics.
Published in:
2020
By:
- Clemens, Paula R.;
- Niizawa, Gabriela;
- Feng, Jia;
- Florence, Julaine;
- DʼAlessandro, Andrea Smith;
- Morgenroth, Lauren P.;
- Gorni, Ksenija;
- Guglieri, Michela;
- Connolly, Anne;
- Wicklund, Matthew;
- Bertorini, Tulio;
- Mah, Jean K.;
- Thangarajh, Mathula;
- Smith, Edward;
- Kuntz, Nancy;
- McDonald, Craig M.;
- Henricson, Erik K.;
- Upadhyayula, Saila;
- Byrne, Barry;
- Manousakis, Georgios
Publication type:
journal article
The care of patients with Duchenne, Becker, and other muscular dystrophies in the COVID-19 pandemic.
Published in:
2020
By:
- Veerapandiyan, Aravindhan;
- Wagner, Kathryn R.;
- Apkon, Susan;
- McDonald, Craig M.;
- Mathews, Katherine D.;
- Parsons, Julie A.;
- Wong, Brenda L.;
- Eichinger, Katy;
- Shieh, Perry B.;
- Butterfield, Russell J.;
- Rao, Vamshi K.;
- Smith, Edward C.;
- Proud, Crystal M.;
- Connolly, Anne M.;
- Ciafaloni, Emma
Publication type:
journal article
Conference report on contractures in musculoskeletal and neurological conditions.
Published in:
2020
By:
- Nuckolls, Glen H.;
- Kinnett, Kathi;
- Dayanidhi, Sudarshan;
- Domenighetti, Andrea A.;
- Duong, Tina;
- Hathout, Yetrib;
- Lawlor, Michael W.;
- Lee, Sabrina S. M.;
- Magnusson, S. Peter;
- McDonald, Craig M.;
- McNally, Elizabeth M.;
- Miller, Natalie F.;
- Olwin, Bradley B.;
- Raghavan, Preeti;
- Roberts, Thomas J.;
- Rutkove, Seward B.;
- Sarwark, John F.;
- Senesac, Claudia R.;
- Vogel, Leslie F.;
- Walter, Glenn A.
Publication type:
journal article
Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta-analysis of disease progression rates in recent multicenter clinical trials.
Published in:
2020
By:
- McDonald, Craig M.;
- Sajeev, Gautam;
- Yao, Zhiwen;
- McDonnell, Erin;
- Elfring, Gary;
- Souza, Marcio;
- Peltz, Stuart W.;
- Darras, Basil T.;
- Shieh, Perry B.;
- Cox, David A.;
- Landry, John;
- Signorovitch, James;
- ACT DMD Study Group and the Tadalafil DMD Study Group
Publication type:
journal article
Twice‐weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2019, v. 59, n. 6, p. 650, doi. 10.1002/mus.26441
By:
- Connolly, Anne M.;
- Zaidman, Craig M.;
- Golumbek, Paul T.;
- Cradock, Mary M.;
- Flanigan, Kevin M.;
- Kuntz, Nancy L.;
- Finkel, Richard S.;
- McDonald, Craig M.;
- Iannaccone, Susan T.;
- Anand, Pallavi;
- Siener, Catherine A.;
- Florence, Julaine M.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Johnson, Linda B.;
- Nicorici, Alina;
- Nelson, Leslie L.;
- Mendell, Jerry R.
Publication type:
Article
Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy.
Published in:
2019
By:
- Connolly, Anne M;
- Zaidman, Craig M;
- Golumbek, Paul T;
- Cradock, Mary M;
- Flanigan, Kevin M;
- Kuntz, Nancy L;
- Finkel, Richard S;
- McDonald, Craig M;
- Iannaccone, Susan T;
- Anand, Pallavi;
- Siener, Catherine A;
- Florence, Julaine M;
- Lowes, Linda P;
- Alfano, Lindsay N;
- Johnson, Linda B;
- Nicorici, Alina;
- Nelson, Leslie L;
- Mendell, Jerry R;
- MDA DMD Clinical Research Network
Publication type:
journal article
Timed function tests have withstood the test of time as clinically meaningful and responsive endpoints in duchenne muscular dystrophy.
Published in:
2018
By:
- McDonald, Craig M.
Publication type:
Editorial
Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial.
Published in:
2018
By:
- Shieh, Perry B.;
- Mcintosh, Joseph;
- Jin, Fengbin;
- Souza, Marcio;
- Elfring, Gary;
- Narayanan, Siva;
- Trifillis, Panayiota;
- Peltz, Stuart W.;
- Mcdonald, Craig M.;
- Darras, Basil T.;
- AND THE ACT DMD STUDY GROUP;
- THE ACT DMD STUDY GROUP
Publication type:
journal article
Mexiletine for muscle cramps in amyotrophic lateral sclerosis: A randomized, double-blind crossover trial.
Published in:
2018
By:
- Oskarsson, Björn;
- Moore, Dan;
- Mozaffar, Tahseen;
- Ravits, John;
- Wiedau‐Pazos, Martina;
- Parziale, Nicholas;
- Joyce, Nanette C.;
- Mandeville, Ross;
- Goyal, Namita;
- Cudkowicz, Merit E.;
- Weiss, Michael;
- Miller, Robert G.;
- McDonald, Craig M.;
- Wiedau-Pazos, Martina
Publication type:
journal article
Longitudinal community walking activity in Duchenne muscular dystrophy.
Published in:
2018
By:
- Fowler, Eileen G.;
- Staudt, Loretta A.;
- Heberer, Kent R.;
- Sienko, Susan E.;
- Buckon, Cathleen E.;
- Bagley, Anita M.;
- Sussman, Michael D.;
- McDonald, Craig M.
Publication type:
journal article
In memoriam: William M. Fowler Jr, MD.
Published in:
2017
By:
- McDonald, Craig M.;
- Carter, Gregory T.
Publication type:
journal article
Clinical trial readiness in non-ambulatory boys and men with duchenne muscular dystrophy: MDA-DMD network follow-up.
Published in:
2016
By:
- Connolly, Anne M.;
- Florence, Julaine M.;
- Zaidman, Craig M.;
- Golumbek, Paul T.;
- Mendell, Jerry R.;
- Flanigan, Kevin M.;
- Karachunski, Peter I.;
- Day, John W.;
- McDonald, Craig M.;
- Darras, Basil T.;
- Kang, Peter B.;
- Siener, Catherine A.;
- Gadeken, Rebecca K.;
- Anand, Pallavi;
- Schierbecker, Jeanine R.;
- Malkus, Elizabeth C.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Johnson, Linda;
- Nicorici, Alina
Publication type:
journal article
Reachable workspace and performance of upper limb (PUL) in duchenne muscular dystrophy.
Published in:
2016
By:
- Han, Jay J.;
- de Bie, Evan;
- Nicorici, Alina;
- Abresch, Richard T.;
- Anthonisen, Colleen;
- Bajcsy, Ruzena;
- Kurillo, Gregorij;
- Mcdonald, Craig M.
Publication type:
journal article
Outcome reliability in non-Ambulatory Boys/Men with duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2015, v. 51, n. 4, p. 522, doi. 10.1002/mus.24346
By:
- Connolly, Anne M.;
- Malkus, Elizabeth C.;
- Mendell, Jerry R.;
- Flanigan, Kevin M.;
- Miller, J. Philip;
- Schierbecker, Jeanine R.;
- Siener, Catherine A.;
- Golumbek, Paul T.;
- Zaidman, Craig M.;
- Mcdonald, Craig M.;
- Johnson, Linda;
- Nicorici, Alina;
- Karachunski, Peter I.;
- Day, John W.;
- Kelecic, Jason M.;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Darras, Basil T.;
- Kang, Peter B.;
- Quigley, Janet
Publication type:
Article
THE 6-minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study.
Published in:
Muscle & Nerve, 2013, v. 48, n. 3, p. 343, doi. 10.1002/mus.23902
By:
- Mcdonald, Craig M.;
- Henricson, Erik K.;
- Abresch, R. Ted;
- Florence, Julaine M.;
- Eagle, Michelle;
- Gappmaier, Eduard;
- Glanzman, Allan M.;
- Spiegel, Robert;
- Barth, Jay;
- Elfring, Gary;
- Reha, Allen;
- Peltz, Stuart
Publication type:
Article
The cooperative international neuromuscular research group Duchenne natural history study--a longitudinal investigation in the era of glucocorticoid therapy: design of protocol and the methods used.
Published in:
2013
By:
- McDonald, Craig M;
- Henricson, Erik K;
- Abresch, R Ted;
- Han, Jay J;
- Escolar, Diana M;
- Florence, Julaine M;
- Duong, Tina;
- Arrieta, Adrienne;
- Clemens, Paula R;
- Hoffman, Eric P;
- Cnaan, Avital;
- Cinrg Investigators
Publication type:
journal article
The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: Reliability, concurrent validity, and minimal clinically important differences from a multicenter study.
Published in:
Muscle & Nerve, 2013, v. 48, n. 3, p. 357, doi. 10.1002/mus.23905
By:
- McDonald, Craig M.;
- Henricson, Erik K.;
- Abresch, R. Ted;
- Florence, Julaine;
- Eagle, Michelle;
- Gappmaier, Eduard;
- Glanzman, Allan M.;
- Spiegel, Robert;
- Barth, Jay;
- Elfring, Gary;
- Reha, Allen;
- Peltz, Stuart W.
Publication type:
Article
Why short stature is beneficial in duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2013, v. 48, n. 3, p. 336, doi. 10.1002/mus.23793
By:
- Bodor, Marko;
- Mcdonald, Craig M.
Publication type:
Article
The cooperative international neuromuscular research group duchenne natural history study-a longitudinal investigation in the era of glucocorticoid therapy: Design of protocol and the methods used.
Published in:
Muscle & Nerve, 2013, v. 48, n. 1, p. 32, doi. 10.1002/mus.23807
By:
- McDonald, Craig M.;
- Henricson, Erik K.;
- Abresch, R. Ted;
- Han, Jay J.;
- Escolar, Diana M.;
- Florence, Julaine M.;
- Duong, Tina;
- Arrieta, Adrienne;
- Clemens, Paula R.;
- Hoffman, Eric P.;
- Cnaan, Avital
Publication type:
Article
The cooperative international neuromuscular research group Duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures
Published in:
Muscle & Nerve, 2013, v. 48, n. 1, p. 55, doi. 10.1002/mus.23808
By:
- Henricson, Erik K.;
- Abresch, R. Ted;
- Cnaan, Avital;
- Hu, Fengming;
- Duong, Tina;
- Arrieta, Adrienne;
- Han, Jay;
- Escolar, Diana M.;
- Florence, Julaine M.;
- Clemens, Paula R.;
- Hoffman, Eric P.;
- McDonald, Craig M.
Publication type:
Article
Corticosteroids and duchenne muscular dystrophy: Does earlier treatment really matter?
Published in:
Muscle & Nerve, 2012, v. 45, n. 6, p. 777, doi. 10.1002/mus.23304
By:
- Mcdonald, Craig M.;
- Han, Jay J.;
- Mah, Jean K.;
- Carter, Gregory T.
Publication type:
Article
The 6-minute walk test in Duchenne/Becker muscular dystrophy: Longitudinal observations.
Published in:
Muscle & Nerve, 2010, v. 42, n. 6, p. 966, doi. 10.1002/mus.21808
By:
- MCDonald, Craig M.;
- Henricson, Erik K.;
- Han, Jay J.;
- Abresch, R. Ted;
- Nicorici, Alina;
- Atkinson, Leone;
- Elfring, Gary L.;
- Reha, Allen;
- Miller, Langdon L.
Publication type:
Article
The 6-minute walk test as a new outcome measure in Duchenne muscular dystrophy.
Published in:
Muscle & Nerve, 2010, v. 41, n. 4, p. 500, doi. 10.1002/mus.21544
By:
- McDonald, Craig M.;
- Henricson, Erik K.;
- Han, Jay J.;
- Abresch, R. Ted;
- Nicorici, Alina;
- Elfring, Gary L.;
- Atkinson, Leone;
- Reha, Allen;
- Hirawat, Samit;
- Miller, Langdon L.
Publication type:
Article
Assessment of regional body composition with dual-energy X-ray absorptiometry in Duchenne muscular dystrophy: Correlation of regional lean mass and quantitative strength.
Published in:
Muscle & Nerve, 2009, v. 39, n. 5, p. 647, doi. 10.1002/mus.21212
By:
- Skalsky, Andrew J.;
- Han, Jay J.;
- Abresch, Richard T.;
- Shin, Chris S.;
- McDonald, Craig M.
Publication type:
Article
Challenges in drug development for muscle disease: A stakeholders' meeting.
Published in:
Muscle & Nerve, 2007, v. 35, n. 1, p. 8, doi. 10.1002/mus.20686
By:
- Mendell, Jerry R.;
- Csimma, Cristina;
- McDonald, Craig M.;
- Escolar, Diana M.;
- Janis, Scott;
- Porter, John D.;
- Hesterlee, Sharon E.;
- Howell, R. Rodney
Publication type:
Article
Magnetic resonance imaging of denervated muscle: comparison to electromyography.
Published in:
2000
By:
- McDonald, Craig M.;
- Carter, Gregory T.;
- Fritz, Russell C.;
- Anderson, Mark W.;
- Abresch, Richard T.;
- Kilmer, David D.;
- McDonald, C M;
- Carter, G T;
- Fritz, R C;
- Anderson, M W;
- Abresch, R T;
- Kilmer, D D
Publication type:
journal article
Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary.
Published in:
2017
By:
- Finder, Jonathan;
- Mayer, Oscar Henry;
- Sheehan, Daniel;
- Sawnani, Hemant;
- Abresch, R. Ted;
- Benditt, Joshua;
- Birnkrant, David J.;
- Duong, Tina;
- Henricson, Erik;
- Kinnett, Kathi;
- McDonald, Craig M.;
- Connolly, Anne M.
Publication type:
journal article
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial.
Published in:
JAMA Network Open, 2022, v. 5, n. 1, p. e2144178, doi. 10.1001/jamanetworkopen.2021.44178
By:
- Mah, Jean K.;
- Clemens, Paula R.;
- Guglieri, Michela;
- Smith, Edward C.;
- Finkel, Richard S.;
- Tulinius, Mar;
- Nevo, Yoram;
- Ryan, Monique M.;
- Webster, Richard;
- Castro, Diana;
- Kuntz, Nancy L.;
- McDonald, Craig M.;
- Damsker, Jesse M.;
- Schwartz, Benjamin D.;
- Mengle-Gaw, Laurel J.;
- Jackowski, Stefan;
- Stimpson, Georgia;
- Ridout, Deborah A.;
- Ayyar-Gupta, Vandana;
- Baranello, Giovanni
Publication type:
Article
Assessing the value of delandistrogene moxeparvovec (SRP-9001) gene therapy in patients with Duchenne muscular dystrophy in the United States.
Published in:
Journal of Market Access & Health Policy, 2023, v. 11, n. 1, p. 1, doi. 10.1080/20016689.2023.2216518
By:
- Klimchak, Alexa C.;
- Sedita, Lauren E.;
- Rodino-Klapac, Louise R.;
- Mendell, Jerry R.;
- McDonald, Craig M.;
- Gooch, Katherine L.;
- Malone, Daniel C.
Publication type:
Article
Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
Published in:
JAMA Neurology, 2022, v. 79, n. 10, p. 1005, doi. 10.1001/jamaneurol.2022.2480
By:
- Guglieri, Michela;
- Clemens, Paula R.;
- Perlman, Seth J.;
- Smith, Edward C.;
- Horrocks, Iain;
- Finkel, Richard S.;
- Mah, Jean K.;
- Deconinck, Nicolas;
- Goemans, Nathalie;
- Haberlova, Jana;
- Straub, Volker;
- Mengle-Gaw, Laurel J.;
- Schwartz, Benjamin D.;
- Harper, Amy D.;
- Shieh, Perry B.;
- De Waele, Liesbeth;
- Castro, Diana;
- Yang, Michelle L.;
- Ryan, Monique M.;
- McDonald, Craig M.
Publication type:
Article
Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial.
Published in:
JAMA Neurology, 2020, v. 77, n. 8, p. 982, doi. 10.1001/jamaneurol.2020.1264
By:
- Clemens, Paula R.;
- Rao, Vamshi K.;
- Connolly, Anne M.;
- Harper, Amy D.;
- Mah, Jean K.;
- Smith, Edward C.;
- McDonald, Craig M.;
- Zaidman, Craig M.;
- Morgenroth, Lauren P.;
- Osaki, Hironori;
- Satou, Youhei;
- Yamashita, Taishi;
- Hoffman, Eric P.
Publication type:
Article
Can Quantitative Muscle Strength and Functional Motor Ability Differentiate the Influence of Age and Corticosteroids in Ambulatory Boys with Duchenne Muscular Dystrophy?
Published in:
PLoS Currents, 2016, p. 1, doi. 10.1371/currents.md.1ced64dff945f8958221fddcd4ee60b0
By:
- Buckon, Cathleen;
- Sienko, Susan;
- Bagley, Anita;
- Sison-Williamson, Mitell;
- Fowler, Eileen;
- Staudt, Loretta;
- McDonald, Craig M.;
- Sussman, Michael
Publication type:
Article
Prednisone and Deflazacort in Duchenne Muscular Dystrophy: Do They Play a Different Role in Child Behavior and Perceived Quality of Life?
Published in:
PLoS Currents, 2016, p. 331, doi. 10.1371/currents.md.7628d9c014bfa29f821a5cd19723bbaa
By:
- Sienko, Susan;
- Buckon, Cathleen;
- Fowler, Eileen;
- Bagley, Anita;
- Staudt, Loretta;
- Sison-Williamson, Mitell;
- Zebracki, Kathy;
- McDonald, Craig M.;
- Sussman, Michael
Publication type:
Article
The 6-Minute Walk Test and Person-Reported Outcomes in Boys with Duchenne Muscular Dystrophy and Typically Developing Controls: Longitudinal Comparisons and Clinically-Meaningful Changes Over One Year.
Published in:
PLoS Currents, 2013, p. 678, doi. 10.1371/currents.md.9e17658b007eb79fcd6f723089f79e06
By:
- Henricson, Erik;
- Abresch, Richard;
- Han, Jay J.;
- Nicorici, Alina;
- Keller, Erica Goude;
- de Bie, Evan;
- McDonald, Craig M.
Publication type:
Article
A Randomized, Double-Blind Trial of Lisinopril and Losartan for the Treatment of Cardiomyopathy in Duchenne Muscular Dystrophy.
Published in:
PLoS Currents, 2013, p. 72, doi. 10.1371/currents.md.2cc69a1dae4be7dfe2bcb420024ea865
By:
- Allen, Hugh D.;
- Flanigan, Kevin M;
- Thrush, Philip T.;
- Dvorchik, Igor;
- Yin, Han;
- Canter, Charles;
- Connolly, Anne M.;
- Parrish, Mark;
- McDonald, Craig M.;
- Braunlin, Elizabeth;
- Colan, Steven D.;
- Day, John;
- Darras, Basil;
- Mendell, Jerry R.
Publication type:
Article
Percent-Predicted 6-Minute Walk Distance in Duchenne Muscular Dystrophy to Account for Maturational Influences.
Published in:
PLoS Currents, 2012, p. 388, doi. 10.1371/currents.RRN1297
By:
- Henricson, Erik;
- Abresch, Richard;
- Han, Jay J.;
- Nicorici, Alina;
- Keller, Erica Goude;
- Elfring, Gary;
- Reha, Allen;
- Barth, Jay;
- McDonald, Craig M.
Publication type:
Article
Influence of β<sub>1</sub> Adrenergic Receptor Genotype on Longitudinal Measures of Left Ventricular Ejection Fraction and Responsiveness to ß-Blocker Therapy in Patients With Duchenne Muscular Dystrophy.
Published in:
Clinical Medicine Insights: Cardiology, 2022, v. 16, p. 1, doi. 10.1177/11795468221116838
By:
- Kelley, Eli F;
- Cross, Troy J;
- McDonald, Craig M;
- Investigators, CINRG;
- Hoffman, Eric P;
- Spurney, Christopher F;
- Bello, Luca
Publication type:
Article
Influence of β<sub>1</sub> Adrenergic Receptor Genotype on Longitudinal Measures of Left Ventricular Ejection Fraction and Responsiveness to ß-Blocker Therapy in Patients With Duchenne Muscular Dystrophy.
Published in:
Clinical Medicine Insights: Cardiology, 2022, v. 16, p. 1, doi. 10.1177/11795468221116838
By:
- Kelley, Eli F.;
- Cross, Troy J.;
- McDonald, Craig M.;
- Hoffman, Eric P.;
- Spurney, Christopher F.;
- Bello, Luca
Publication type:
Article
Medical management of muscle weakness in Duchenne muscular dystrophy.
Published in:
PLoS ONE, 2020, v. 15, n. 10, p. 1, doi. 10.1371/journal.pone.0240687
By:
- Rivera, Sarah R.;
- Jhamb, Sumit K.;
- Abdel-Hamid, Hoda Z.;
- Acsadi, Gyula;
- Brandsema, John;
- Ciafaloni, Emma;
- Darras, Basil T.;
- Iannaccone, Susan T.;
- Konersman, Chamindra G.;
- Kuntz, Nancy L.;
- McDonald, Craig M.;
- Parsons, Julie A.;
- Tesi Rocha, Carolina;
- Zaidman, Craig M.;
- Butterfield, Russell J.;
- Connolly, Anne M.;
- Mathews, Katherine D.
Publication type:
Article

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