Works by Liu, Yuanjing


Results: 9
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    Variant-selective stereopure oligonucleotides protect against pathologies associated with C9orf72-repeat expansion in preclinical models.

    Published in:
    Nature Communications, 2021, v. 12, n. 1, p. 1, doi. 10.1038/s41467-021-21112-8
    By:
    • Liu, Yuanjing;
    • Dodart, Jean-Cosme;
    • Tran, Helene;
    • Berkovitch, Shaunna;
    • Braun, Maurine;
    • Byrne, Michael;
    • Durbin, Ann F.;
    • Hu, Xiao Shelley;
    • Iwamoto, Naoki;
    • Jang, Hyun Gyung;
    • Kandasamy, Pachamuthu;
    • Liu, Fangjun;
    • Longo, Kenneth;
    • Ruschel, Jörg;
    • Shelke, Juili;
    • Yang, Hailin;
    • Yin, Yuan;
    • Donner, Amy;
    • Zhong, Zhong;
    • Vargeese, Chandra
    Publication type:
    Article
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    O4‐05‐02: THE INVESTIGATIONAL STEREOPURE ANTISENSE OLIGONUCLEOTIDE WVE‐3972‐01 PREFERENTIALLY REDUCES G<sub>4</sub>C<sub>2</sub> REPEAT‐CONTAINING C9ORF72 TRANSCRIPTS: A POTENTIAL THERAPEUTIC APPROACH FOR THE TREATMENT OF FRONTOTEMPORAL DEMENTIA

    Published in:
    Alzheimer's & Dementia: The Journal of the Alzheimer's Association, 2018, v. 14, p. P1411, doi. 10.1016/j.jalz.2018.06.2934
    By:
    • Dodart, Jean-Cosme;
    • Liu, Yuanjing;
    • Tran, Helene;
    • Berkovitch, Shaunna;
    • Byrne, Michael;
    • Durbin, Ann;
    • Iwamoto, Naoki;
    • Jang, Hyun Gyung;
    • Kandasamy, Pachamuthu;
    • Liu, Fangjun;
    • Mohapatra, Susovan;
    • Yang, Hailin;
    • Yin, Yuan;
    • Zhang, Jason;
    • Zhong, Zhong;
    • Vargeese, Chandra;
    • Brown, Robert H.
    Publication type:
    Article
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