OpenURL Connection Search

Select item for more details and to access through your institution.

Health-Related Quality of Life and Emotional Distress Among Mothers of Sons With Muscular Dystrophy as Compared to Sex- and Age Group–Matched Controls.
Published in:
Journal of Child Neurology, 2021, v. 36, n. 3, p. 177, doi. 10.1177/0883073820962927
By:
- Jackson, Jamie L.;
- Korth, Christina X.;
- Leslie, Carine E.;
- Cotto, Jennifer;
- Mah, May Ling;
- Hor, Kan;
- Cripe, Linda;
- Al-Zaidy, Samiah;
- Camino, Eric M.;
- Church, Kathleen;
- Lehman, Kelly J.;
- Shay, Victoria;
- Mendell, Jerry R.
Publication type:
Article
Long‐term safety and functional outcomes of delandistrogene moxeparvovec gene therapy in patients with Duchenne muscular dystrophy: A phase 1/2a nonrandomized trial.
Published in:
Muscle & Nerve, 2024, v. 69, n. 1, p. 93, doi. 10.1002/mus.27955
By:
- Mendell, Jerry R.;
- Sahenk, Zarife;
- Lehman, Kelly J.;
- Lowes, Linda P.;
- Reash, Natalie F.;
- Iammarino, Megan A.;
- Alfano, Lindsay N.;
- Lewis, Sarah;
- Church, Kathleen;
- Shell, Richard;
- Potter, Rachael A.;
- Griffin, Danielle A.;
- Hogan, Mark;
- Wang, Shufang;
- Mason, Stefanie;
- Darton, Eddie;
- Rodino‐Klapac, Louise R.
Publication type:
Article
Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy.
Published in:
JAMA Neurology, 2021, v. 78, n. 7, p. 834, doi. 10.1001/jamaneurol.2021.1272
By:
- Mendell, Jerry R.;
- Al-Zaidy, Samiah A.;
- Lehman, Kelly J.;
- McColly, Markus;
- Lowes, Linda P.;
- Alfano, Lindsay N.;
- Reash, Natalie F.;
- Iammarino, Megan A.;
- Church, Kathleen R.;
- Kleyn, Aaron;
- Meriggioli, Matthew N.;
- Shell, Richard
Publication type:
Article
Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study SRP‐9001‐103 (ENDEAVOR).
Published in:
Annals of Neurology, 2023, v. 94, n. 5, p. 955, doi. 10.1002/ana.26755
By:
- Zaidman, Craig M.;
- Proud, Crystal M.;
- McDonald, Craig M.;
- Lehman, Kelly J.;
- Goedeker, Natalie L.;
- Mason, Stefanie;
- Murphy, Alexander P.;
- Guridi, Maitea;
- Wang, Shufang;
- Reid, Carol;
- Darton, Eddie;
- Wandel, Christoph;
- Lewis, Sarah;
- Malhotra, Jyoti;
- Griffin, Danielle A.;
- Potter, Rachael A.;
- Rodino‐Klapac, Louise R.;
- Mendell, Jerry R.
Publication type:
Article

Found: 4

Health-Related Quality of Life and Emotional Distress Among Mothers of Sons With Muscular Dystrophy as Compared to Sex- and Age Group–Matched Controls.

Long‐term safety and functional outcomes of delandistrogene moxeparvovec gene therapy in patients with Duchenne muscular dystrophy: A phase 1/2a nonrandomized trial.

Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy.

Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study SRP‐9001‐103 (ENDEAVOR).